Literature DB >> 26077850

High diagnostic yield of clinical exome sequencing in Middle Eastern patients with Mendelian disorders.

Tarunashree Yavarna1, Nader Al-Dewik, Mariam Al-Mureikhi, Rehab Ali, Fatma Al-Mesaifri, Laila Mahmoud, Noora Shahbeck, Shenela Lakhani, Mariam AlMulla, Zafar Nawaz, Patrik Vitazka, Fowzan S Alkuraya, Tawfeg Ben-Omran.   

Abstract

Clinical exome sequencing (CES) has become an increasingly popular diagnostic tool in patients with heterogeneous genetic disorders, especially in those with neurocognitive phenotypes. Utility of CES in consanguineous populations has not yet been determined on a large scale. A clinical cohort of 149 probands from Qatar with suspected Mendelian, mainly neurocognitive phenotypes, underwent CES from July 2012 to June 2014. Intellectual disability and global developmental delay were the most common clinical presentations but our cohort displayed other phenotypes, such as epilepsy, dysmorphism, microcephaly and other structural brain anomalies and autism. A pathogenic or likely pathogenic mutation, including pathogenic CNVs, was identified in 89 probands for a diagnostic yield of 60%. Consanguinity and positive family history predicted a higher diagnostic yield. In 5% (7/149) of cases, CES implicated novel candidate disease genes (MANF, GJA9, GLG1, COL15A1, SLC35F5, MAGE4, NEUROG1). CES uncovered two coexisting genetic disorders in 4% (6/149) and actionable incidental findings in 2% (3/149) of cases. Average time to diagnosis was reduced from 27 to 5 months. CES, which already has the highest diagnostic yield among all available diagnostic tools in the setting of Mendelian disorders, appears to be particularly helpful diagnostically in the highly consanguineous Middle Eastern population.

Entities:  

Mesh:

Year:  2015        PMID: 26077850     DOI: 10.1007/s00439-015-1575-0

Source DB:  PubMed          Journal:  Hum Genet        ISSN: 0340-6717            Impact factor:   4.132


  74 in total

1.  Identification of 28 novel mutations in the Bardet-Biedl syndrome genes: the burden of private mutations in an extensively heterogeneous disease.

Authors:  Jean Muller; C Stoetzel; M C Vincent; C C Leitch; V Laurier; J M Danse; S Hellé; V Marion; V Bennouna-Greene; S Vicaire; A Megarbane; J Kaplan; V Drouin-Garraud; M Hamdani; S Sigaudy; C Francannet; J Roume; P Bitoun; A Goldenberg; N Philip; S Odent; J Green; M Cossée; E E Davis; N Katsanis; D Bonneau; A Verloes; O Poch; J L Mandel; H Dollfus
Journal:  Hum Genet       Date:  2010-02-23       Impact factor: 4.132

2.  Molecular basis of lipoamide dehydrogenase deficiency in Ashkenazi Jews.

Authors:  A Shaag; A Saada; I Berger; H Mandel; A Joseph; A Feigenbaum; O N Elpeleg
Journal:  Am J Med Genet       Date:  1999-01-15

3.  Molecular profiling of synaptic vesicle docking sites reveals novel proteins but few differences between glutamatergic and GABAergic synapses.

Authors:  Janina Boyken; Mads Grønborg; Dietmar Riedel; Henning Urlaub; Reinhard Jahn; John Jia En Chua
Journal:  Neuron       Date:  2013-04-24       Impact factor: 17.173

4.  Antenatal presentation of Bardet-Biedl syndrome may mimic Meckel syndrome.

Authors:  Houda Karmous-Benailly; Jelena Martinovic; Marie-Claire Gubler; Yoann Sirot; Laure Clech; Catherine Ozilou; Joëlle Auge; Nora Brahimi; Heather Etchevers; Eric Detrait; Chantal Esculpavit; Sophie Audollent; Géraldine Goudefroye; Marie Gonzales; Julia Tantau; Philippe Loget; Madeleine Joubert; Dominique Gaillard; Corinne Jeanne-Pasquier; Anne-Lise Delezoide; Marie-Odile Peter; Ghislaine Plessis; Brigitte Simon-Bouy; Hélène Dollfus; Martine Le Merrer; Arnold Munnich; Férechté Encha-Razavi; Michel Vekemans; Tania Attié-Bitach
Journal:  Am J Hum Genet       Date:  2005-01-21       Impact factor: 11.025

5.  FORGE Canada Consortium: outcomes of a 2-year national rare-disease gene-discovery project.

Authors:  Chandree L Beaulieu; Jacek Majewski; Jeremy Schwartzentruber; Mark E Samuels; Bridget A Fernandez; Francois P Bernier; Michael Brudno; Bartha Knoppers; Janet Marcadier; David Dyment; Shelin Adam; Dennis E Bulman; Steve J M Jones; Denise Avard; Minh Thu Nguyen; Francois Rousseau; Christian Marshall; Richard F Wintle; Yaoqing Shen; Stephen W Scherer; Jan M Friedman; Jacques L Michaud; Kym M Boycott
Journal:  Am J Hum Genet       Date:  2014-06-05       Impact factor: 11.025

6.  Compendium of cardiac channel mutations in 541 consecutive unrelated patients referred for long QT syndrome genetic testing.

Authors:  David J Tester; Melissa L Will; Carla M Haglund; Michael J Ackerman
Journal:  Heart Rhythm       Date:  2005-05       Impact factor: 6.343

7.  Collagen XIV is important for growth and structural integrity of the myocardium.

Authors:  Ge Tao; Agata K Levay; Jacqueline D Peacock; Danielle J Huk; Sarah N Both; Nicole H Purcell; Jose R Pinto; Maarten L Galantowicz; Manuel Koch; Pamela A Lucchesi; David E Birk; Joy Lincoln
Journal:  J Mol Cell Cardiol       Date:  2012-08-11       Impact factor: 5.000

8.  Practices and policies of clinical exome sequencing providers: analysis and implications.

Authors:  Seema M Jamal; Joon-Ho Yu; Jessica X Chong; Karin M Dent; Jessie H Conta; Holly K Tabor; Michael J Bamshad
Journal:  Am J Med Genet A       Date:  2013-05       Impact factor: 2.802

9.  Characterization of the deleted in autism 1 protein family: implications for studying cognitive disorders.

Authors:  Azhari Aziz; Sean P Harrop; Naomi E Bishop
Journal:  PLoS One       Date:  2011-01-19       Impact factor: 3.240

10.  The Human Gene Mutation Database: 2008 update.

Authors:  Peter D Stenson; Matthew Mort; Edward V Ball; Katy Howells; Andrew D Phillips; Nick St Thomas; David N Cooper
Journal:  Genome Med       Date:  2009-01-22       Impact factor: 11.117

View more
  82 in total

Review 1.  Mesencephalic astrocyte-derived neurotrophic factor (MANF), a new player in endoplasmic reticulum diseases: structure, biology, and therapeutic roles.

Authors:  Yeawon Kim; Sun-Ji Park; Ying Maggie Chen
Journal:  Transl Res       Date:  2017-06-29       Impact factor: 7.012

2.  Warsaw breakage syndrome: Further clinical and genetic delineation.

Authors:  Ebba Alkhunaizi; Ranad Shaheen; Sanjay Kumar Bharti; Ann M Joseph-George; Karen Chong; Ghada M H Abdel-Salam; Mohammed Alowain; Susan I Blaser; Blake C Papsin; Mohammed Butt; Mais Hashem; Nicole Martin; Ruth Godoy; Robert M Brosh; Fowzan S Alkuraya; David Chitayat
Journal:  Am J Med Genet A       Date:  2018-09-14       Impact factor: 2.802

3.  De novo GRIN variants in NMDA receptor M2 channel pore-forming loop are associated with neurological diseases.

Authors:  Jia Li; Jin Zhang; Weiting Tang; Ruth K Mizu; Hirofumi Kusumoto; Wenshu XiangWei; Yuchen Xu; Wenjuan Chen; Johansen B Amin; Chun Hu; Varun Kannan; Stephanie R Keller; William R Wilcox; Johannes R Lemke; Scott J Myers; Sharon A Swanger; Lonnie P Wollmuth; Slavé Petrovski; Stephen F Traynelis; Hongjie Yuan
Journal:  Hum Mutat       Date:  2019-09-10       Impact factor: 4.878

4.  Comprehensive genetic analysis of 57 families with clinically suspected Cornelia de Lange syndrome.

Authors:  Hiromi Aoi; Takeshi Mizuguchi; José Ricard Ceroni; Veronica Eun Hue Kim; Isabel Furquim; Rachel S Honjo; Takuma Iwaki; Toshifumi Suzuki; Futoshi Sekiguchi; Yuri Uchiyama; Yoshiteru Azuma; Kohei Hamanaka; Eriko Koshimizu; Satoko Miyatake; Satomi Mitsuhashi; Atsushi Takata; Noriko Miyake; Satoru Takeda; Atsuo Itakura; Débora R Bertola; Chong Ae Kim; Naomichi Matsumoto
Journal:  J Hum Genet       Date:  2019-07-23       Impact factor: 3.172

5.  The Clinical Sequencing Evidence-Generating Research Consortium: Integrating Genomic Sequencing in Diverse and Medically Underserved Populations.

Authors:  Laura M Amendola; Jonathan S Berg; Carol R Horowitz; Frank Angelo; Jeannette T Bensen; Barbara B Biesecker; Leslie G Biesecker; Gregory M Cooper; Kelly East; Kelly Filipski; Stephanie M Fullerton; Bruce D Gelb; Katrina A B Goddard; Benyam Hailu; Ragan Hart; Kristen Hassmiller-Lich; Galen Joseph; Eimear E Kenny; Barbara A Koenig; Sara Knight; Pui-Yan Kwok; Katie L Lewis; Amy L McGuire; Mary E Norton; Jeffrey Ou; Donald W Parsons; Bradford C Powell; Neil Risch; Mimsie Robinson; Christine Rini; Sarah Scollon; Anne M Slavotinek; David L Veenstra; Melissa P Wasserstein; Benjamin S Wilfond; Lucia A Hindorff; Sharon E Plon; Gail P Jarvik
Journal:  Am J Hum Genet       Date:  2018-09-06       Impact factor: 11.025

Review 6.  Discovery of mutations for Mendelian disorders.

Authors:  Fowzan S Alkuraya
Journal:  Hum Genet       Date:  2016-04-11       Impact factor: 4.132

7.  Potential Role of Genomic Sequencing in the Early Diagnosis of Treatable Genetic Conditions.

Authors:  Hengameh Zahed; Teresa N Sparks; Ben Li; Adnan Alsadah; Joseph T C Shieh
Journal:  J Pediatr       Date:  2017-10       Impact factor: 4.406

8.  Pancreatic β-cell protection from inflammatory stress by the endoplasmic reticulum proteins thrombospondin 1 and mesencephalic astrocyte-derived neutrotrophic factor (MANF).

Authors:  Daniel A Cunha; Monia Cito; Fabio Arturo Grieco; Cristina Cosentino; Tatiana Danilova; Laurence Ladrière; Maria Lindahl; Andrii Domanskyi; Marco Bugliani; Piero Marchetti; Décio L Eizirik; Miriam Cnop
Journal:  J Biol Chem       Date:  2017-07-11       Impact factor: 5.157

9.  De Novo Mutations and Rare Variants Occurring in NMDA Receptors.

Authors:  Wenshu XiangWei; Yuwu Jiang; Hongjie Yuan
Journal:  Curr Opin Physiol       Date:  2017-12-27

Review 10.  A Clinician's perspective on clinical exome sequencing.

Authors:  Anne H O'Donnell-Luria; David T Miller
Journal:  Hum Genet       Date:  2016-04-28       Impact factor: 4.132

View more

北京卡尤迪生物科技股份有限公司 © 2022-2023.