Literature DB >> 30571344

Probing the Virtual Proteome to Identify Novel Disease Biomarkers.

Jonathan D Mosley1, Mark D Benson2,3, J Gustav Smith4, Olle Melander4, Debby Ngo5, Christian M Shaffer1, Jane F Ferguson1, Matthew S Herzig3, Catherine A McCarty6, Christopher G Chute7, Gail P Jarvik8, Adam S Gordon8, Melody R Palmer8, David R Crosslin9, Eric B Larson8,10, David S Carrell10, Iftikhar J Kullo11, Jennifer A Pacheco12, Peggy L Peissig13, Murray H Brilliant14, Terrie E Kitchner14, James G Linneman13, Bahram Namjou15, Marc S Williams16, Marylyn D Ritchie17, Kenneth M Borthwick18, Krzysztof Kiryluk19, Frank D Mentch20, Patrick M Sleiman20, Elizabeth W Karlson21, Shefali S Verma22, Yineng Zhu23, Ramachandran S Vasan24, Qiong Yang23, Josh C Denny1,25, Dan M Roden25,26, Robert E Gerszten3, Thomas J Wang1.   

Abstract

BACKGROUND: Proteomic approaches allow measurement of thousands of proteins in a single specimen, which can accelerate biomarker discovery. However, applying these technologies to massive biobanks is not currently feasible because of the practical barriers and costs of implementing such assays at scale. To overcome these challenges, we used a "virtual proteomic" approach, linking genetically predicted protein levels to clinical diagnoses in >40 000 individuals.
METHODS: We used genome-wide association data from the Framingham Heart Study (n=759) to construct genetic predictors for 1129 plasma protein levels. We validated the genetic predictors for 268 proteins and used them to compute predicted protein levels in 41 288 genotyped individuals in the Electronic Medical Records and Genomics (eMERGE) cohort. We tested associations for each predicted protein with 1128 clinical phenotypes. Lead associations were validated with directly measured protein levels and either low-density lipoprotein cholesterol or subclinical atherosclerosis in the MDCS (Malmö Diet and Cancer Study; n=651).
RESULTS: In the virtual proteomic analysis in eMERGE, 55 proteins were associated with 89 distinct diagnoses at a false discovery rate q<0.1. Among these, 13 associations involved lipid (n=7) or atherosclerosis (n=6) phenotypes. We tested each association for validation in MDCS using directly measured protein levels. At Bonferroni-adjusted significance thresholds, levels of apolipoprotein E isoforms were associated with hyperlipidemia, and circulating C-type lectin domain family 1 member B and platelet-derived growth factor receptor-β predicted subclinical atherosclerosis. Odds ratios for carotid atherosclerosis were 1.31 (95% CI, 1.08-1.58; P=0.006) per 1-SD increment in C-type lectin domain family 1 member B and 0.79 (0.66-0.94; P=0.008) per 1-SD increment in platelet-derived growth factor receptor-β.
CONCLUSIONS: We demonstrate a biomarker discovery paradigm to identify candidate biomarkers of cardiovascular and other diseases.

Entities:  

Keywords:  atherosclerosis; biomarkers; electronic health records; proteomics

Mesh:

Substances:

Year:  2018        PMID: 30571344      PMCID: PMC8833190          DOI: 10.1161/CIRCULATIONAHA.118.036063

Source DB:  PubMed          Journal:  Circulation        ISSN: 0009-7322            Impact factor:   29.690


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