Literature DB >> 32462720

World Federation of Hemophilia Gene Therapy Registry.

Barbara A Konkle1, Donna Coffin2, Glenn F Pierce2, Cary Clark3, Lindsey George4,5, Alfonso Iorio6, Johnny Mahlangu3,7, Mayss Naccache2, Brian O'Mahony8,9, Flora Peyvandi3,10, Steve Pipe11,12, Adrian Quartel13, Eileen K Sawyer14, Mark W Skinner15, Bartholomew Tortella16, Crystal Watson17, Ian Winburn18.   

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Year:  2020        PMID： 32462720      PMCID： PMC8944922          DOI： 10.1111/hae.14015

Source DB:  PubMed          Journal:  Haemophilia        ISSN： 1351-8216            Impact factor:   4.287


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  12 in total

Review 1.  Clinical advances in gene therapy updates on clinical trials of gene therapy in haemophilia.

Authors:  Flora Peyvandi; Isabella Garagiola
Journal:  Haemophilia       Date:  2019-07-08       Impact factor: 4.287

2.  Characterization of the human factor VIII gene.

Authors:  J Gitschier; W I Wood; T M Goralka; K L Wion; E Y Chen; D H Eaton; G A Vehar; D J Capon; R M Lawn
Journal:  Nature       Date:  1984 Nov 22-28       Impact factor: 49.962

3.  Molecular cloning of a cDNA encoding human antihaemophilic factor.

Authors:  J J Toole; J L Knopf; J M Wozney; L A Sultzman; J L Buecker; D D Pittman; R J Kaufman; E Brown; C Shoemaker; E C Orr
Journal:  Nature       Date:  1984 Nov 22-28       Impact factor: 49.962

Review 4.  Past, present and future of haemophilia gene therapy: From vectors and transgenes to known and unknown outcomes.

Authors:  G F Pierce; A Iorio
Journal:  Haemophilia       Date:  2018-05       Impact factor: 4.287

Review 5.  Gene therapy for hemophilia.

Authors:  Amit C Nathwani
Journal:  Hematology Am Soc Hematol Educ Program       Date:  2019-12-06

Review 6.  The 1st WFH Gene Therapy Round Table: Understanding the landscape and challenges of gene therapy for haemophilia around the world.

Authors:  Glenn F Pierce; Donna Coffin
Journal:  Haemophilia       Date:  2019-01-03       Impact factor: 4.287

7.  Expression of active human factor VIII from recombinant DNA clones.

Authors:  W I Wood; D J Capon; C C Simonsen; D L Eaton; J Gitschier; B Keyt; P H Seeburg; D H Smith; P Hollingshead; K L Wion; E Delwart; E G Tuddenham; G A Vehar; R M Lawn
Journal:  Nature       Date:  1984 Nov 22-28       Impact factor: 49.962

8.  Molecular cloning of the gene for human anti-haemophilic factor IX.

Authors:  K H Choo; K G Gould; D J Rees; G G Brownlee
Journal:  Nature       Date:  1982-09-09       Impact factor: 49.962

9.  The gene structure of human anti-haemophilic factor IX.

Authors:  D S Anson; K H Choo; D J Rees; F Giannelli; K Gould; J A Huddleston; G G Brownlee
Journal:  EMBO J       Date:  1984-05       Impact factor: 11.598

10.  Long-term safety and efficacy of factor IX gene therapy in hemophilia B.

Authors:  Amit C Nathwani; Ulreke M Reiss; Edward G D Tuddenham; Cecilia Rosales; Pratima Chowdary; Jenny McIntosh; Marco Della Peruta; Elsa Lheriteau; Nishal Patel; Deepak Raj; Anne Riddell; Jun Pie; Savita Rangarajan; David Bevan; Michael Recht; Yu-Min Shen; Kathleen G Halka; Etiena Basner-Tschakarjan; Federico Mingozzi; Katherine A High; James Allay; Mark A Kay; Catherine Y C Ng; Junfang Zhou; Maria Cancio; Christopher L Morton; John T Gray; Deokumar Srivastava; Arthur W Nienhuis; Andrew M Davidoff
Journal:  N Engl J Med       Date:  2014-11-20       Impact factor: 176.079
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  4 in total

Review 1.  Hemophilia Gene Therapy: Approaching the First Licensed Product.

Authors:  Paul Batty; David Lillicrap
Journal:  Hemasphere       Date:  2021-02-10

Review 2.  Reinforcing Collaboration and Harmonization to Unlock the Potentials of Advanced Therapy Medical Products: Future Efforts Are Awaited From Manufacturers and Decision-Makers.

Authors:  Tingting Qiu; Shuyao Liang; Yitong Wang; Claude Dussart; Borislav Borissov; Mondher Toumi
Journal:  Front Public Health       Date:  2021-11-25

Review 3.  International consensus recommendations on the management of people with haemophilia B.

Authors:  Daniel P Hart; Davide Matino; Jan Astermark; Gerard Dolan; Roseline d'Oiron; Cédric Hermans; Victor Jiménez-Yuste; Adriana Linares; Tadashi Matsushita; Simon McRae; Margareth C Ozelo; Sean Platton; Darrel Stafford; Robert F Sidonio; Andreas Tiede
Journal:  Ther Adv Hematol       Date:  2022-04-02

Review 4.  Gene therapy: Practical aspects of implementation.

Authors:  Steven W Pipe; K Rajender Reddy; Pratima Chowdary
Journal:  Haemophilia       Date:  2022-05       Impact factor: 4.263
  4 in total

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