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11 in total

1. Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy.

Authors: Dhruv S Kazi; Brandon K Bellows; Suzanne J Baron; Changyu Shen; David J Cohen; John A Spertus; Robert W Yeh; Suzanne V Arnold; Brett W Sperry; Mathew S Maurer; Sanjiv J Shah
Journal: Circulation Date: 2020-02-12 Impact factor: 29.690

2. The Evaluation of Orphan Drugs by the German Joint Federal Committee-An Eight-Year Review.

Authors: Sandra Schulz; Anna Marie Passon; Matthias Perleth; Michael Kulig; Nina Paschke; Katja Matthias
Journal: Dtsch Arztebl Int Date: 2020-12-11 Impact factor: 5.594

3. Cost effectiveness of caplacizumab in acquired thrombotic thrombocytopenic purpura.

Authors: George Goshua; Pranay Sinha; Jeanne E Hendrickson; Christopher Tormey; Pavan K Bendapudi; Alfred Ian Lee
Journal: Blood Date: 2021-02-18 Impact factor: 22.113

4. Estimating the size of the United States market for new antibiotics with activity against carbapenem-resistant Enterobacteriaceae.

Authors: Cornelius J Clancy; M Hong Nguyen
Journal: Antimicrob Agents Chemother Date: 2019-10-07 Impact factor: 5.191

5. Rarely mentioned: how we arrived at the quantitative definition of a rare disease.

Authors: Clyde Partin
Journal: Proc (Bayl Univ Med Cent) Date: 2022-03-28

6. Spending For Orphan Indications Among Top-Selling Orphan Drugs Approved To Treat Common Diseases.

Authors: Kao-Ping Chua; Lauren E Kimmel; Rena M Conti
Journal: Health Aff (Millwood) Date: 2021-03 Impact factor: 6.301

7. Response by Kazi et al to Letter Regarding Article, "Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy".

Authors: Dhruv S Kazi; Brandon K Bellows; John A Spertus; Suzanne J Baron; Changyu Shen; David J Cohen; Robert W Yeh; Suzanne V Arnold; Brett W Sperry; Mathew S Maurer; Sanjiv J Shah
Journal: Circulation Date: 2020-10-12 Impact factor: 39.918

8. Effects of socio-economic factors on research over systemic sclerosis: an analysis based on long time series of bibliometric data.

Authors: Wei Guo; Zeyu Zhou; Yinhe Liang; Chuanhui Xu; Lin Zeng; Zhiyong Dong; Rong Mu
Journal: Orphanet J Rare Dis Date: 2021-12-20 Impact factor: 4.123

Review 9. The Price of Progress: Cost, Access, and Adoption of Novel Cardiovascular Drugs in Clinical Practice.

Authors: Merilyn S Varghese; Chia-Liang Liu; Dhruv S Kazi
Journal: Curr Cardiol Rep Date: 2021-10-01 Impact factor: 2.931

10. Therapeutic Value Assessments of Novel Medicines in the US and Europe, 2018-2019.

Authors: Kerstin N Vokinger; Thomas J Hwang; Camille E G Glaus; Aaron S Kesselheim
Journal: JAMA Netw Open Date: 2022-04-01