Literature DB >> 28977313

NEWBORN SCREENING FOR SEVERE COMBINED IMMUNODEFICIENCIES USING TRECS AND KRECS: SECOND PILOT STUDY IN BRAZIL.

Marilia Pyles P Kanegae1, Lucila Akune Barreiros1, Jusley Lira Sousa1, Marco Antônio S Brito1, Edgar Borges de Oliveira1, Lara Pereira Soares2, Juliana Themudo L Mazzucchelli3, Débora Quiorato Fernandes4, Sonia Marchezi Hadachi5, Silvia Maia Holanda6, Flavia Alice T M Guimarães7, Maura Aparecida P V V Boacnin8, Marley Aparecida L Pereira9, Joaquina Maria C Bueno2, Anete Sevciovic Grumach10, Regina Sumiko W Di Gesu11, Amélia Miyashiro N Dos Santos3, Newton Bellesi12, Beatriz T Costa-Carvalho3, Antonio Condino-Neto1.   

Abstract

OBJECTIVE: To validate the quantification of T-cell receptor excision circles (TRECs) and kappa-deleting recombination excision circles (KRECs) by real-time polymerase chain reaction (qRT-PCR) for newborn screening of primary immunodeficiencies with defects in T and/or B cells in Brazil.
METHODS: Blood samples from newborns and controls were collected on filter paper. DNA was extracted and TRECs, and KRECs were quantified by a duplex real-time PCR. The cutoff values were determined by receiver operating characteristic curve analysis using SPSS software (IBM®, Armonk, NY, USA).
RESULTS: Around 6,881 samples from newborns were collected and TRECs and KRECs were quantified. The TRECs values ranged between 1 and 1,006 TRECs/µL, with mean and median of 160 and 139 TRECs/µL, respectively. Three samples from patients with severe combined immunodeficiency (SCID) showed TRECs below 4/µL and a patient with DiGeorge syndrome showed undetectable TRECs. KRECs values ranged from 10 to 1,097 KRECs/µL, with mean and median of 130 and 108 KRECs/µL. Four patients with agammaglobulinemia had results below 4 KRECs/µL. The cutoff values were 15 TRECs/µL and 14 KRECs/µL and were established according to the receiver operating characteristic curve analysis, with 100% sensitivity for SCID and agammaglobulinemia detection, respectively.
CONCLUSIONS: Quantification of TRECs and KRECs was able to diagnose children with T- and/or B-cell lymphopenia in our study, which validated the technique in Brazil and enabled us to implement the newborn screening program for SCID and agammaglobulinemia.

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Year:  2017        PMID: 28977313      PMCID: PMC5417806          DOI: 10.1590/1984-0462/;2017;35;1;00013

Source DB:  PubMed          Journal:  Rev Paul Pediatr        ISSN: 0103-0582


  21 in total

1.  Implementing routine testing for severe combined immunodeficiency within Wisconsin's newborn screening program.

Authors:  Mei Wang Baker; Ronald H Laessig; Murray L Katcher; John M Routes; William J Grossman; James Verbsky; Daniel F Kurtycz; Charles D Brokopp
Journal:  Public Health Rep       Date:  2010 May-Jun       Impact factor: 2.792

2.  Laboratory technology for population-based screening for severe combined immunodeficiency in neonates: the winner is T-cell receptor excision circles.

Authors:  Jennifer M Puck
Journal:  J Allergy Clin Immunol       Date:  2012-01-29       Impact factor: 10.793

Review 3.  History and current status of newborn screening for severe combined immunodeficiency.

Authors:  Antonia Kwan; Jennifer M Puck
Journal:  Semin Perinatol       Date:  2015-04-30       Impact factor: 3.300

4.  Fiscal implications of newborn screening in the diagnosis of severe combined immunodeficiency.

Authors:  Catherine Kubiak; Soma Jyonouchi; Caroline Kuo; Maria Garcia-Lloret; Morna J Dorsey; John Sleasman; Arthur S Zbrozek; Elena E Perez
Journal:  J Allergy Clin Immunol Pract       Date:  2014-08-28

5.  Newborn screening for severe combined immunodeficiency in 11 screening programs in the United States.

Authors:  Antonia Kwan; Roshini S Abraham; Robert Currier; Amy Brower; Karen Andruszewski; Jordan K Abbott; Mei Baker; Mark Ballow; Louis E Bartoshesky; Francisco A Bonilla; Charles Brokopp; Edward Brooks; Michele Caggana; Jocelyn Celestin; Joseph A Church; Anne Marie Comeau; James A Connelly; Morton J Cowan; Charlotte Cunningham-Rundles; Trivikram Dasu; Nina Dave; Maria T De La Morena; Ulrich Duffner; Chin-To Fong; Lisa Forbes; Debra Freedenberg; Erwin W Gelfand; Jaime E Hale; I Celine Hanson; Beverly N Hay; Diana Hu; Anthony Infante; Daisy Johnson; Neena Kapoor; Denise M Kay; Donald B Kohn; Rachel Lee; Heather Lehman; Zhili Lin; Fred Lorey; Aly Abdel-Mageed; Adrienne Manning; Sean McGhee; Theodore B Moore; Stanley J Naides; Luigi D Notarangelo; Jordan S Orange; Sung-Yun Pai; Matthew Porteus; Ray Rodriguez; Neil Romberg; John Routes; Mary Ruehle; Arye Rubenstein; Carlos A Saavedra-Matiz; Ginger Scott; Patricia M Scott; Elizabeth Secord; Christine Seroogy; William T Shearer; Subhadra Siegel; Stacy K Silvers; E Richard Stiehm; Robert W Sugerman; John L Sullivan; Susan Tanksley; Millard L Tierce; James Verbsky; Beth Vogel; Rosalyn Walker; Kelly Walkovich; Jolan E Walter; Richard L Wasserman; Michael S Watson; Geoffrey A Weinberg; Leonard B Weiner; Heather Wood; Anne B Yates; Jennifer M Puck; Vincent R Bonagura
Journal:  JAMA       Date:  2014-08-20       Impact factor: 56.272

6.  Neonatal screening for severe combined immunodeficiency in Brazil.

Authors:  Marilia Pyles Patto Kanegae; Lucila Akune Barreiros; Juliana Themudo Lessa Mazzucchelli; Sonia Marchezi Hadachi; Laura Maria de Figueiredo Ferreira Guilhoto; Ana Lúcia Acquesta; Isabel Rugue Genov; Silvia Maia Holanda; Regina Sumiko Watanabe Di Gesu; Ana Lucia Goulart; Amélia Miyashiro Nunes Dos Santos; Newton Bellesi; Beatriz Tavares Costa-Carvalho; Antonio Condino-Neto
Journal:  J Pediatr (Rio J)       Date:  2016-05-18       Impact factor: 2.197

7.  Development of a routine newborn screening protocol for severe combined immunodeficiency.

Authors:  Mei W Baker; William J Grossman; Ronald H Laessig; Gary L Hoffman; Charles D Brokopp; Daniel F Kurtycz; Michael F Cogley; Thomas J Litsheim; Murray L Katcher; John M Routes
Journal:  J Allergy Clin Immunol       Date:  2009-05-31       Impact factor: 10.793

8.  Challenges of newborn severe combined immunodeficiency screening among premature infants.

Authors:  Claire E Ward; Alan P Baptist
Journal:  Pediatrics       Date:  2013-03-04       Impact factor: 7.124

Review 9.  TREC Based Newborn Screening for Severe Combined Immunodeficiency Disease: A Systematic Review.

Authors:  Jet van der Spek; Rolf H H Groenwold; Mirjam van der Burg; Joris M van Montfrans
Journal:  J Clin Immunol       Date:  2015-04-17       Impact factor: 8.317

Review 10.  Splice-correction strategies for treatment of X-linked agammaglobulinemia.

Authors:  Burcu Bestas; Janne J Turunen; K Emelie M Blomberg; Qing Wang; Robert Månsson; Samir El Andaloussi; Anna Berglöf; C I Edvard Smith
Journal:  Curr Allergy Asthma Rep       Date:  2015-03       Impact factor: 4.806

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3.  SCID and Other Inborn Errors of Immunity with Low TRECs - the Brazilian Experience.

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Journal:  J Clin Immunol       Date:  2022-05-03       Impact factor: 8.542

4.  A Novel Homozygous JAK3 Mutation Leading to T-B+NK- SCID in Two Brazilian Patients.

Authors:  Lucila A Barreiros; Gesmar R S Segundo; Anete S Grumach; Pérsio Roxo-Júnior; Troy R Torgerson; Hans D Ochs; Antonio Condino-Neto
Journal:  Front Pediatr       Date:  2018-08-20       Impact factor: 3.418

5.  IN TIME: THE VALUE AND GLOBAL IMPLICATIONSOF NEWBORN SCREENING FORSEVERE COMBINED IMMUNODEFICIENCY.

Authors:  Cristina Meehan; Carmem Bonfim; Joseph F Dasso; Beatriz Tavares Costa-Carvalho; Antonio Condino-Neto; Jolan Walter
Journal:  Rev Paul Pediatr       Date:  2018 Oct-Dec

6.  Multiplex PCR-Based Newborn Screening for Severe T and B-Cell Lymphopenia: The first Pilot Study in Turkey.

Authors:  Seyhan Kutlug; Medine Karadag Alpaslan; Gonca Hancioglu; Sariye Elif Ozyazici Ozkan; Didem Cemile Yesilirmak; Hasan Bulut; Canan Aygun; Gonul Ogur; Alisan Yildiran
Journal:  Sisli Etfal Hastan Tip Bul       Date:  2021-01-12

7.  Newborn screening for severe combined immunodeficiency: The results of the first pilot TREC and KREC study in Ukraine with involving of 10,350 neonates.

Authors:  Oksana Boyarchuk; Nataliia Yarema; Volodymyr Kravets; Oleksandra Shulhai; Ivanna Shymanska; Iryna Chornomydz; Tetyana Hariyan; Liubov Volianska; Maria Kinash; Halyna Makukh
Journal:  Front Immunol       Date:  2022-09-15       Impact factor: 8.786

8.  Newborn Screening for SCID and Other Severe Primary Immunodeficiency in the Polish-German Transborder Area: Experience From the First 14 Months of Collaboration.

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Journal:  Front Immunol       Date:  2020-10-16       Impact factor: 7.561

9.  Parents' Perspectives and Societal Acceptance of Implementation of Newborn Screening for SCID in the Netherlands.

Authors:  Maartje Blom; Robbert G M Bredius; Marleen E Jansen; Gert Weijman; Evelien A Kemper; Clementien L Vermont; Iris H I M Hollink; Willem A Dik; Joris M van Montfrans; Mariëlle E van Gijn; Stefanie S Henriet; Koen J van Aerde; Wouter Koole; Arjan C Lankester; Eugènie H B M Dekkers; Peter C J I Schielen; Martine C de Vries; Lidewij Henneman; Mirjam van der Burg
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