Literature DB >> 27041689

Metastatic neuroblastoma in infants: are survival rates excellent only within the stringent framework of clinical trials?

A Di Cataldo1, A Agodi2, J Balaguer3, A Garaventa4, M Barchitta2, V Segura5, M Bianchi6, V Castel5, A Castellano7, S Cesaro8, J M Couselo9, O Cruz10, P D'Angelo11, B De Bernardi4, J Donat12, N G de Andoin13, M I Hernandez14, M La Spina1, M Lillo15, R Lopez-Almaraz16, R Luksch17, S Mastrangelo18, E Mateos19, J Molina20, C Moscheo17, R Mura21, F Porta22, G Russo1, A Tondo23, M Torrent24, S Vetrella25, J A Villegas26, E Viscardi27, G A Zanazzo28, A Cañete5.   

Abstract

INTRODUCTION: SIOPEN INES protocol yielded excellent 5-year survival rates for MYCN-non-amplified metastatic neuroblastoma. Patients deemed ineligible due to lack or delay of MYCN status or late registration were treated, but not included in the study. Our goal was to analyse survival at 10 years among the whole population.
MATERIALS AND METHODS: Italian and Spanish metastatic INES patients' data are reported. SPSS 20.0 was used for statistical analysis.
RESULTS: Among 98 infants, 27 had events and 19 died, while 79 were disease free. Five- and 10-year event-free survival (EFS) were 73 and 70 %, and overall survival (OS) was 81 and 74 %, respectively. MYCN status was significant for EFS, but not for OS in multivariate analysis.
CONCLUSIONS: The survival rates of patients who complied with all the inclusion criteria for INES trials are higher compared to those that included also not registered patients. Five-year EFS and OS for INES 99.2 were 87.8 and 95.7 %, while our stage 4s population obtained 78 and 87 %. Concerning 99.3, 5-year EFS and OS were 86.7 and 95.6 %, while for stage 4 we registered 61 and 68 %. MYCN amplification had a strong impact on prognosis and therefore we consider it unacceptable that many patients were not studied for MYCN and probably inadequately treated. Ten-year survival rates were shown to decrease: EFS from 73 to 70 % and OS from 81 to 74 %, indicating a risk of late events, particularly in stage 4s. Population-based registries like European ENCCA WP 11-task 11 will possibly clarify these data.

Entities:  

Keywords:  Eligibility; Infant; Metastatic; Neuroblastoma; Survival

Mesh:

Substances:

Year:  2016        PMID: 27041689     DOI: 10.1007/s12094-016-1505-1

Source DB:  PubMed          Journal:  Clin Transl Oncol        ISSN: 1699-048X            Impact factor:   3.405


  10 in total

1.  Improved survival of children with neuroblastoma between 1979 and 2005: a report of the Italian Neuroblastoma Registry.

Authors:  Riccardo Haupt; Alberto Garaventa; Claudio Gambini; Stefano Parodi; Giuliana Cangemi; Fiorina Casale; Elisabetta Viscardi; Maurizio Bianchi; Arcangelo Prete; Alessandro Jenkner; Roberto Luksch; Andrea Di Cataldo; Claudio Favre; Paolo D'Angelo; Giulio Andrea Zanazzo; Giampaolo Arcamone; Gian Carlo Izzi; Anna Rita Gigliotti; Guido Pastore; Bruno De Bernardi
Journal:  J Clin Oncol       Date:  2010-03-29       Impact factor: 44.544

2.  Hepatomegaly in neuroblastoma stage 4s: criteria for treatment of the vulnerable neonate.

Authors:  L L Hsu; A E Evans; G J D'Angio
Journal:  Med Pediatr Oncol       Date:  1996-12

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Journal:  Cancer       Date:  1999-07-15       Impact factor: 6.860

4.  Poor survival for infants with MYCN-amplified metastatic neuroblastoma despite intensified treatment: the International Society of Paediatric Oncology European Neuroblastoma Experience.

Authors:  Adela Canete; Mary Gerrard; Hervé Rubie; Victoria Castel; Andrea Di Cataldo; Caroline Munzer; Ruth Ladenstein; Bénédicte Brichard; José D Bermúdez; Jerôme Couturier; Bruno de Bernardi; Andrew J Pearson; Jean Michon
Journal:  J Clin Oncol       Date:  2009-01-26       Impact factor: 44.544

5.  Excellent outcome with reduced treatment for infants with disseminated neuroblastoma without MYCN gene amplification.

Authors:  Bruno De Bernardi; Mary Gerrard; Luca Boni; Hervé Rubie; Adela Cañete; Andrea Di Cataldo; Victoria Castel; Ana Forjaz de Lacerda; Ruth Ladenstein; Ellen Ruud; Benédicte Brichard; Jerome Couturier; Caroline Ellershaw; Caroline Munzer; Paolo Bruzzi; Jean Michon; Andrew D J Pearson
Journal:  J Clin Oncol       Date:  2009-01-26       Impact factor: 44.544

6.  The International Neuroblastoma Risk Group (INRG) classification system: an INRG Task Force report.

Authors:  Susan L Cohn; Andrew D J Pearson; Wendy B London; Tom Monclair; Peter F Ambros; Garrett M Brodeur; Andreas Faldum; Barbara Hero; Tomoko Iehara; David Machin; Veronique Mosseri; Thorsten Simon; Alberto Garaventa; Victoria Castel; Katherine K Matthay
Journal:  J Clin Oncol       Date:  2008-12-01       Impact factor: 44.544

7.  Neuroblastoma in the newborn. A study of the Italian Neuroblastoma Registry.

Authors:  Anna Rita Gigliotti; Andrea Di Cataldo; Stefania Sorrentino; Stefano Parodi; Antonino Rizzo; Piero Buffa; Claudio Granata; Angela Rita Sementa; Anna Maria Fagnani; Massimo Provenzi; Arcangelo Prete; Carmelita D'Ippolito; Anna Clerico; Aurora Castellano; Gian Paolo Tonini; Massimo Conte; Alberto Garaventa; Bruno De Bernardi
Journal:  Eur J Cancer       Date:  2009-09-18       Impact factor: 9.162

Review 8.  Revisions of the international criteria for neuroblastoma diagnosis, staging, and response to treatment.

Authors:  G M Brodeur; J Pritchard; F Berthold; N L Carlsen; V Castel; R P Castelberry; B De Bernardi; A E Evans; M Favrot; F Hedborg
Journal:  J Clin Oncol       Date:  1993-08       Impact factor: 44.544

9.  Diagnostic and prognostic markers in infants with disseminated neuroblastoma: a retrospective analysis from the Italian Cooperative Group for Neuroblastoma.

Authors:  Andrea Di Cataldo; Daniela Dau; Massimo Conte; Stefano Parodi; Bruno De Bernardi; Maria Giuliano; Andrea Pession; Elisabetta Viscardi; Roberto Luksch; Aurora Castellano; Gregoria Bertuna; Riccardo Haupt
Journal:  Med Sci Monit       Date:  2009-01

10.  Treatment of localised resectable neuroblastoma. Results of the LNESG1 study by the SIOP Europe Neuroblastoma Group.

Authors:  B De Bernardi; V Mosseri; H Rubie; V Castel; A Foot; R Ladenstein; G Laureys; M Beck-Popovic; A F de Lacerda; A D J Pearson; J De Kraker; P F Ambros; Y de Rycke; M Conte; P Bruzzi; J Michon
Journal:  Br J Cancer       Date:  2008-09-02       Impact factor: 7.640

  10 in total
  4 in total

1.  Treatment and survival of childhood neuroblastoma: Evidence from a population-based study in the United States.

Authors:  Diarmuid Coughlan; Matthew Gianferante; Charles F Lynch; Jennifer L Stevens; Linda C Harlan
Journal:  Pediatr Hematol Oncol       Date:  2017-10-17       Impact factor: 1.969

2.  miR-15a-5p, miR-15b-5p, and miR-16-5p inhibit tumor progression by directly targeting MYCN in neuroblastoma.

Authors:  Srinivas Chava; C Patrick Reynolds; Anup S Pathania; Santhi Gorantla; Larisa Y Poluektova; Don W Coulter; Subash C Gupta; Manoj K Pandey; Kishore B Challagundla
Journal:  Mol Oncol       Date:  2019-11-29       Impact factor: 6.603

Review 3.  Mechanisms, Characteristics, and Treatment of Neuropathic Pain and Peripheral Neuropathy Associated with Dinutuximab in Neuroblastoma Patients.

Authors:  Stefano Mastrangelo; Serena Rivetti; Silvia Triarico; Alberto Romano; Giorgio Attinà; Palma Maurizi; Antonio Ruggiero
Journal:  Int J Mol Sci       Date:  2021-11-23       Impact factor: 5.923

4.  Amino Acids Regulate Cisplatin Insensitivity in Neuroblastoma.

Authors:  Venugopal Gunda; Anup S Pathania; Srinivas Chava; Philip Prathipati; Nagendra K Chaturvedi; Don W Coulter; Manoj K Pandey; Donald L Durden; Kishore B Challagundla
Journal:  Cancers (Basel)       Date:  2020-09-10       Impact factor: 6.639

  4 in total

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