Literature DB >> 27029608

In vivo gene therapy potentials of CRISPR-Cas9.

H-Y Xue1, X Zhang2, Y Wang3, L Xiaojie3, W-J Dai4, Y Xu5.   

Abstract

Mesh:

Year:  2016        PMID: 27029608     DOI: 10.1038/gt.2016.25

Source DB:  PubMed          Journal:  Gene Ther        ISSN: 0969-7128            Impact factor:   5.250


× No keyword cloud information.
  26 in total

1.  Genome-wide binding of the CRISPR endonuclease Cas9 in mammalian cells.

Authors:  Xuebing Wu; David A Scott; Andrea J Kriz; Anthony C Chiu; Patrick D Hsu; Daniel B Dadon; Albert W Cheng; Alexandro E Trevino; Silvana Konermann; Sidi Chen; Rudolf Jaenisch; Feng Zhang; Phillip A Sharp
Journal:  Nat Biotechnol       Date:  2014-04-20       Impact factor: 54.908

2.  Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA.

Authors:  Chengzu Long; John R McAnally; John M Shelton; Alex A Mireault; Rhonda Bassel-Duby; Eric N Olson
Journal:  Science       Date:  2014-08-14       Impact factor: 47.728

3.  Efficient genome modification by CRISPR-Cas9 nickase with minimal off-target effects.

Authors:  Bin Shen; Wensheng Zhang; Jun Zhang; Jiankui Zhou; Jianying Wang; Li Chen; Lu Wang; Alex Hodgkins; Vivek Iyer; Xingxu Huang; William C Skarnes
Journal:  Nat Methods       Date:  2014-03-02       Impact factor: 28.547

4.  In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.

Authors:  Christopher E Nelson; Chady H Hakim; David G Ousterout; Pratiksha I Thakore; Eirik A Moreb; Ruth M Castellanos Rivera; Sarina Madhavan; Xiufang Pan; F Ann Ran; Winston X Yan; Aravind Asokan; Feng Zhang; Dongsheng Duan; Charles A Gersbach
Journal:  Science       Date:  2015-12-31       Impact factor: 47.728

5.  Seamless modification of wild-type induced pluripotent stem cells to the natural CCR5Δ32 mutation confers resistance to HIV infection.

Authors:  Lin Ye; Jiaming Wang; Ashley I Beyer; Fernando Teque; Thomas J Cradick; Zhongxia Qi; Judy C Chang; Gang Bao; Marcus O Muench; Jingwei Yu; Jay A Levy; Yuet Wai Kan
Journal:  Proc Natl Acad Sci U S A       Date:  2014-06-09       Impact factor: 11.205

6.  Increasing the efficiency of homology-directed repair for CRISPR-Cas9-induced precise gene editing in mammalian cells.

Authors:  Van Trung Chu; Timm Weber; Benedikt Wefers; Wolfgang Wurst; Sandrine Sander; Klaus Rajewsky; Ralf Kühn
Journal:  Nat Biotechnol       Date:  2015-03-24       Impact factor: 54.908

7.  Increasing the efficiency of precise genome editing with CRISPR-Cas9 by inhibition of nonhomologous end joining.

Authors:  Takeshi Maruyama; Stephanie K Dougan; Matthias C Truttmann; Angelina M Bilate; Jessica R Ingram; Hidde L Ploegh
Journal:  Nat Biotechnol       Date:  2015-03-23       Impact factor: 54.908

8.  Improving CRISPR-Cas nuclease specificity using truncated guide RNAs.

Authors:  Yanfang Fu; Jeffry D Sander; Deepak Reyon; Vincent M Cascio; J Keith Joung
Journal:  Nat Biotechnol       Date:  2014-01-26       Impact factor: 54.908

9.  A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice.

Authors:  Yang Yang; Lili Wang; Peter Bell; Deirdre McMenamin; Zhenning He; John White; Hongwei Yu; Chenyu Xu; Hiroki Morizono; Kiran Musunuru; Mark L Batshaw; James M Wilson
Journal:  Nat Biotechnol       Date:  2016-02-01       Impact factor: 54.908

10.  Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo.

Authors:  Hao Yin; Chun-Qing Song; Joseph R Dorkin; Lihua J Zhu; Yingxiang Li; Qiongqiong Wu; Angela Park; Junghoon Yang; Sneha Suresh; Aizhan Bizhanova; Ankit Gupta; Mehmet F Bolukbasi; Stephen Walsh; Roman L Bogorad; Guangping Gao; Zhiping Weng; Yizhou Dong; Victor Koteliansky; Scot A Wolfe; Robert Langer; Wen Xue; Daniel G Anderson
Journal:  Nat Biotechnol       Date:  2016-02-01       Impact factor: 54.908

View more
  10 in total

Review 1.  Control of gene editing by manipulation of DNA repair mechanisms.

Authors:  Eric Danner; Sanum Bashir; Saniye Yumlu; Wolfgang Wurst; Benedikt Wefers; Ralf Kühn
Journal:  Mamm Genome       Date:  2017-04-03       Impact factor: 2.957

2.  Structurally modulated codelivery of siRNA and Argonaute 2 for enhanced RNA interference.

Authors:  Jiahe Li; Connie Wu; Wade Wang; Yanpu He; Elad Elkayam; Leemor Joshua-Tor; Paula T Hammond
Journal:  Proc Natl Acad Sci U S A       Date:  2018-02-05       Impact factor: 11.205

3.  Gene-specific MicroRNA antagonism protects against HIV Tat and TGF-β-mediated suppression of CFTR mRNA and function.

Authors:  R K Dutta; S Chinnapaiyan; M J Santiago; I Rahman; H J Unwalla
Journal:  Biomed Pharmacother       Date:  2021-08-27       Impact factor: 7.419

Review 4.  Gene Delivery in Neuro-Oncology.

Authors:  Karan Dixit; Priya Kumthekar
Journal:  Curr Oncol Rep       Date:  2017-09-02       Impact factor: 5.075

5.  Deep mutational scanning of S. pyogenes Cas9 reveals important functional domains.

Authors:  Jeffrey M Spencer; Xiaoliu Zhang
Journal:  Sci Rep       Date:  2017-12-04       Impact factor: 4.379

Review 6.  Therapeutic gene editing: delivery and regulatory perspectives.

Authors:  Gayong Shim; Dongyoon Kim; Gyu Thae Park; Hyerim Jin; Soo-Kyung Suh; Yu-Kyoung Oh
Journal:  Acta Pharmacol Sin       Date:  2017-04-10       Impact factor: 6.150

Review 7.  Glioblastoma: new therapeutic strategies to address cellular and genomic complexity.

Authors:  Xue Cai; Michael E Sughrue
Journal:  Oncotarget       Date:  2017-12-20

8.  Antibody-targeted chromatin enables effective intracellular delivery and functionality of CRISPR/Cas9 expression plasmids.

Authors:  Tobias Killian; Annette Buntz; Teresa Herlet; Heike Seul; Olaf Mundigl; Gernot Längst; Ulrich Brinkmann
Journal:  Nucleic Acids Res       Date:  2019-06-04       Impact factor: 16.971

9.  Stimulation of homologous recombination in plants expressing heterologous recombinases.

Authors:  Abdellah Barakate; Ewan Keir; Helena Oakey; Claire Halpin
Journal:  BMC Plant Biol       Date:  2020-07-16       Impact factor: 4.215

Review 10.  Tissue Engineering and Regenerative Medicine: Achievements, Future, and Sustainability in Asia.

Authors:  Fengxuan Han; Jiayuan Wang; Luguang Ding; Yuanbin Hu; Wenquan Li; Zhangqin Yuan; Qianping Guo; Caihong Zhu; Li Yu; Huan Wang; Zhongliang Zhao; Luanluan Jia; Jiaying Li; Yingkang Yu; Weidong Zhang; Genglei Chu; Song Chen; Bin Li
Journal:  Front Bioeng Biotechnol       Date:  2020-03-24
  10 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.