Literature DB >> 25938534

Long-term effects of retinal gene therapy in childhood blindness.

Alan F Wright1.   

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Year:  2015        PMID: 25938534     DOI: 10.1056/NEJMe1503419

Source DB:  PubMed          Journal:  N Engl J Med        ISSN: 0028-4793            Impact factor:   91.245


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  13 in total

1.  Success against blindness encourages gene therapy researchers.

Authors:  Heidi Ledford
Journal:  Nature       Date:  2015-10-22       Impact factor: 49.962

2.  Bench-to-Bedside; Clinical and Translational Research; Personalized Medicine; Precision Medicine-What's in a Name?

Authors:  Arthur M Feldman
Journal:  Clin Transl Sci       Date:  2015-06       Impact factor: 4.689

3.  Reprogramming metabolism by targeting sirtuin 6 attenuates retinal degeneration.

Authors:  Lijuan Zhang; Jianhai Du; Sally Justus; Chun-Wei Hsu; Luis Bonet-Ponce; Wen-Hsuan Wu; Yi-Ting Tsai; Wei-Pu Wu; Yading Jia; Jimmy K Duong; Vinit B Mahajan; Chyuan-Sheng Lin; Shuang Wang; James B Hurley; Stephen H Tsang
Journal:  J Clin Invest       Date:  2016-11-14       Impact factor: 14.808

4.  Multimodal Imaging of Central Retinal Disease Progression in a 2-Year Mean Follow-up of Retinitis Pigmentosa.

Authors:  Tharikarn Sujirakul; Michael K Lin; Jimmy Duong; Ying Wei; Sara Lopez-Pintado; Stephen H Tsang
Journal:  Am J Ophthalmol       Date:  2015-07-09       Impact factor: 5.258

5.  CRISPR genome surgery in a novel humanized model for autosomal dominant retinitis pigmentosa.

Authors:  Wen-Hsuan Wu; Yi-Ting Tsai; I-Wen Huang; Chia-Hua Cheng; Chun-Wei Hsu; Xuan Cui; Joseph Ryu; Peter M J Quinn; Salvatore Marco Caruso; Chyuang-Sheng Lin; Stephen H Tsang
Journal:  Mol Ther       Date:  2022-02-10       Impact factor: 12.910

6.  Optimization of Retinal Gene Therapy for X-Linked Retinitis Pigmentosa Due to RPGR Mutations.

Authors:  William A Beltran; Artur V Cideciyan; Shannon E Boye; Guo-Jie Ye; Simone Iwabe; Valerie L Dufour; Luis Felipe Marinho; Malgorzata Swider; Mychajlo S Kosyk; Jin Sha; Sanford L Boye; James J Peterson; C Douglas Witherspoon; John J Alexander; Gui-Shuang Ying; Mark S Shearman; Jeffrey D Chulay; William W Hauswirth; Paul D Gamlin; Samuel G Jacobson; Gustavo D Aguirre
Journal:  Mol Ther       Date:  2017-05-27       Impact factor: 11.454

7.  Halting progressive neurodegeneration in advanced retinitis pigmentosa.

Authors:  Susanne F Koch; Yi-Ting Tsai; Jimmy K Duong; Wen-Hsuan Wu; Chun-Wei Hsu; Wei-Pu Wu; Luis Bonet-Ponce; Chyuan-Sheng Lin; Stephen H Tsang
Journal:  J Clin Invest       Date:  2015-08-24       Impact factor: 14.808

Review 8.  Gene therapy returns to centre stage.

Authors:  Luigi Naldini
Journal:  Nature       Date:  2015-10-15       Impact factor: 49.962

9.  Retinal Remodeling: Concerns, Emerging Remedies and Future Prospects.

Authors:  Vidhyasankar Krishnamoorthy; Pitchaiah Cherukuri; Deepak Poria; Manvi Goel; Sushma Dagar; Narender K Dhingra
Journal:  Front Cell Neurosci       Date:  2016-02-17       Impact factor: 5.505

Review 10.  Genetic manipulation for inherited neurodegenerative diseases: myth or reality?

Authors:  Patrick Yu-Wai-Man
Journal:  Br J Ophthalmol       Date:  2016-03-21       Impact factor: 4.638

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