Literature DB >> 26490597

Success against blindness encourages gene therapy researchers.

Heidi Ledford.   

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Year:  2015        PMID： 26490597     DOI： 10.1038/526487a

Source DB:  PubMed          Journal:  Nature        ISSN： 0028-0836            Impact factor:   49.962


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  6 in total

1.  Improvement and decline in vision with gene therapy in childhood blindness.

Authors:  Samuel G Jacobson; Artur V Cideciyan; Alejandro J Roman; Alexander Sumaroka; Sharon B Schwartz; Elise Heon; William W Hauswirth
Journal:  N Engl J Med       Date:  2015-05-03       Impact factor: 91.245

2.  Successful arrest of photoreceptor and vision loss expands the therapeutic window of retinal gene therapy to later stages of disease.

Authors:  William A Beltran; Artur V Cideciyan; Simone Iwabe; Malgorzata Swider; Mychajlo S Kosyk; Kendra McDaid; Inna Martynyuk; Gui-Shuang Ying; James Shaffer; Wen-Tao Deng; Sanford L Boye; Alfred S Lewin; William W Hauswirth; Samuel G Jacobson; Gustavo D Aguirre
Journal:  Proc Natl Acad Sci U S A       Date:  2015-10-12       Impact factor: 11.205

3.  Effect of gene therapy on visual function in Leber's congenital amaurosis.

Authors:  James W B Bainbridge; Alexander J Smith; Susie S Barker; Scott Robbie; Robert Henderson; Kamaljit Balaggan; Ananth Viswanathan; Graham E Holder; Andrew Stockman; Nick Tyler; Simon Petersen-Jones; Shomi S Bhattacharya; Adrian J Thrasher; Fred W Fitzke; Barrie J Carter; Gary S Rubin; Anthony T Moore; Robin R Ali
Journal:  N Engl J Med       Date:  2008-04-27       Impact factor: 91.245

4.  Safety and efficacy of gene transfer for Leber's congenital amaurosis.

Authors:  Albert M Maguire; Francesca Simonelli; Eric A Pierce; Edward N Pugh; Federico Mingozzi; Jeannette Bennicelli; Sandro Banfi; Kathleen A Marshall; Francesco Testa; Enrico M Surace; Settimio Rossi; Arkady Lyubarsky; Valder R Arruda; Barbara Konkle; Edwin Stone; Junwei Sun; Jonathan Jacobs; Lou Dell'Osso; Richard Hertle; Jian-xing Ma; T Michael Redmond; Xiaosong Zhu; Bernd Hauck; Olga Zelenaia; Kenneth S Shindler; Maureen G Maguire; J Fraser Wright; Nicholas J Volpe; Jennifer Wellman McDonnell; Alberto Auricchio; Katherine A High; Jean Bennett
Journal:  N Engl J Med       Date:  2008-04-27       Impact factor: 91.245

5.  Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial.

Authors:  William W Hauswirth; Tomas S Aleman; Shalesh Kaushal; Artur V Cideciyan; Sharon B Schwartz; Lili Wang; Thomas J Conlon; Sanford L Boye; Terence R Flotte; Barry J Byrne; Samuel G Jacobson
Journal:  Hum Gene Ther       Date:  2008-10       Impact factor: 5.695

6.  Long-term effects of retinal gene therapy in childhood blindness.

Authors:  Alan F Wright
Journal:  N Engl J Med       Date:  2015-05-04       Impact factor: 91.245
  6 in total
  3 in total

1.  Structure-guided evolution of antigenically distinct adeno-associated virus variants for immune evasion.

Authors:  Longping Victor Tse; Kelli A Klinc; Victoria J Madigan; Ruth M Castellanos Rivera; Lindsey F Wells; L Patrick Havlik; J Kennon Smith; Mavis Agbandje-McKenna; Aravind Asokan
Journal:  Proc Natl Acad Sci U S A       Date:  2017-05-30       Impact factor: 11.205

2.  Dystrophin Gene Replacement and Gene Repair Therapy for Duchenne Muscular Dystrophy in 2016: An Interview.

Authors:  Dongsheng Duan
Journal:  Hum Gene Ther Clin Dev       Date:  2016-03       Impact factor: 5.032

Review 3.  Metabolic and Redox Signaling of the Nucleoredoxin-Like-1 Gene for the Treatment of Genetic Retinal Diseases.

Authors:  Emmanuelle Clérin; Myriam Marussig; José-Alain Sahel; Thierry Léveillard
Journal:  Int J Mol Sci       Date:  2020-02-27       Impact factor: 5.923
  3 in total

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