Literature DB >> 25653889

Chapter 3 - Restoring Vision to the Blind: Gene Therapy for Vision Loss.

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Abstract

Entities:  

Year:  2014        PMID： 25653889      PMCID： PMC4314998          DOI： 10.1167/tvst.3.7.5

Source DB:  PubMed          Journal:  Transl Vis Sci Technol        ISSN： 2164-2591            Impact factor:   3.283


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  67 in total

1.  A Pro23His mutation alters prenatal rod photoreceptor morphology in a transgenic swine model of retinitis pigmentosa.

Authors:  Patrick A Scott; Juan P Fernandez de Castro; Henry J Kaplan; Maureen A McCall
Journal:  Invest Ophthalmol Vis Sci       Date:  2014-04-28       Impact factor: 4.799

2.  Cone photoreceptors develop normally in the absence of functional rod photoreceptors in a transgenic swine model of retinitis pigmentosa.

Authors:  Juan P Fernandez de Castro; Patrick A Scott; James W Fransen; James Demas; Paul J DeMarco; Henry J Kaplan; Maureen A McCall
Journal:  Invest Ophthalmol Vis Sci       Date:  2014-04-17       Impact factor: 4.799

3.  Highly efficient endogenous human gene correction using designed zinc-finger nucleases.

Authors:  Fyodor D Urnov; Jeffrey C Miller; Ya-Li Lee; Christian M Beausejour; Jeremy M Rock; Sheldon Augustus; Andrew C Jamieson; Matthew H Porteus; Philip D Gregory; Michael C Holmes
Journal:  Nature       Date:  2005-04-03       Impact factor: 49.962

4.  Care for patients with ultra-rare disorders.

Authors:  Raoul C M Hennekam
Journal:  Eur J Med Genet       Date:  2010-12-10       Impact factor: 2.708

Review 5.  Gene mutations in retinitis pigmentosa and their clinical implications.

Authors:  D Y Wang; W M Chan; P O S Tam; L Baum; D S C Lam; K K L Chong; B J Fan; C P Pang
Journal:  Clin Chim Acta       Date:  2005-01       Impact factor: 3.786

6.  Inner limiting membrane barriers to AAV-mediated retinal transduction from the vitreous.

Authors:  Deniz Dalkara; Kathleen D Kolstad; Natalia Caporale; Meike Visel; Ryan R Klimczak; David V Schaffer; John G Flannery
Journal:  Mol Ther       Date:  2009-08-11       Impact factor: 11.454

Review 7.  ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering.

Authors:  Thomas Gaj; Charles A Gersbach; Carlos F Barbas
Journal:  Trends Biotechnol       Date:  2013-05-09       Impact factor: 19.536

8.  Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration.

Authors:  Francesca Simonelli; Albert M Maguire; Francesco Testa; Eric A Pierce; Federico Mingozzi; Jeannette L Bennicelli; Settimio Rossi; Kathleen Marshall; Sandro Banfi; Enrico M Surace; Junwei Sun; T Michael Redmond; Xiaosong Zhu; Kenneth S Shindler; Gui-Shuang Ying; Carmela Ziviello; Carmela Acerra; J Fraser Wright; Jennifer Wellman McDonnell; Katherine A High; Jean Bennett; Alberto Auricchio
Journal:  Mol Ther       Date:  2009-12-01       Impact factor: 11.454

9.  Improving CRISPR-Cas nuclease specificity using truncated guide RNAs.

Authors:  Yanfang Fu; Jeffry D Sander; Deepak Reyon; Vincent M Cascio; J Keith Joung
Journal:  Nat Biotechnol       Date:  2014-01-26       Impact factor: 54.908

10.  Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial.

Authors:  Robert E MacLaren; Markus Groppe; Alun R Barnard; Charles L Cottriall; Tanya Tolmachova; Len Seymour; K Reed Clark; Matthew J During; Frans P M Cremers; Graeme C M Black; Andrew J Lotery; Susan M Downes; Andrew R Webster; Miguel C Seabra
Journal:  Lancet       Date:  2014-01-16       Impact factor: 79.321
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  1 in total

1.  Paediatric retinal detachment: aetiology, characteristics and outcomes.

Authors:  Elizabeth McElnea; Kirk Stephenson; Sarah Gilmore; Michael O'Keefe; David Keegan
Journal:  Int J Ophthalmol       Date:  2018-02-18       Impact factor: 1.779
  1 in total

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