Literature DB >> 17296903

Molecular testing for hereditary retinal disease as part of clinical care.

Katy Downs1, David N Zacks, Rafael Caruso, Athanasios J Karoukis, Kari Branham, Beverly M Yashar, Mark H Haimann, Karmen Trzupek, Meira Meltzer, Delphine Blain, Julia E Richards, Richard G Weleber, John R Heckenlively, Paul A Sieving, Radha Ayyagari.   

Abstract

OBJECTIVE: To describe clinical molecular testing for hereditary retinal degenerations, highlighting results, interpretation, and patient education.
METHODS: Mutation analysis of 8 retinal genes was performed by dideoxy sequencing. Pretest and posttest genetic counseling was offered to patients. The laboratory report listed results and provided individualized interpretation.
RESULTS: A total of 350 tests were performed. The molecular basis of disease was determined in 133 of 266 diagnostic tests; the disease-causing mutations were not identified in the remaining 133 diagnostic tests. Predictive and carrier tests were requested for 9 and 75 nonsymptomatic patients with known familial mutations, respectively.
CONCLUSIONS: Molecular testing can confirm a clinical diagnosis, identify carrier status, and confirm or rule out the presence of a familial mutation in nonsymptomatic at-risk relatives. Because causative mutations cannot be identified in all patients with retinal diseases, it is essential that patients are counseled before testing regarding the benefits and limitations of this emerging diagnostic tool. CLINICAL RELEVANCE: The molecular definition of the genetic basis of disease provides a unique adjunct to the clinical care of patients with hereditary retinal degenerations.

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Year:  2007        PMID: 17296903     DOI: 10.1001/archopht.125.2.252

Source DB:  PubMed          Journal:  Arch Ophthalmol        ISSN: 0003-9950


  15 in total

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Authors:  Kaoru Fujinami; Jana Zernant; Ravinder K Chana; Genevieve A Wright; Kazushige Tsunoda; Yoko Ozawa; Kazuo Tsubota; Andrew R Webster; Anthony T Moore; Rando Allikmets; Michel Michaelides
Journal:  Invest Ophthalmol Vis Sci       Date:  2013-10-11       Impact factor: 4.799

2.  A novel compound heterozygous mutation in the BEST1 gene causes autosomal recessive Best vitelliform macular dystrophy.

Authors:  L Zhao; S Grob; R Corey; M Krupa; J Luo; H Du; C Lee; G Hughes; J Lee; J Quach; J Zhu; P X Shaw; I Kozak; K Zhang
Journal:  Eye (Lond)       Date:  2012-03-16       Impact factor: 3.775

3.  A Report on Molecular Diagnostic Testing for Inherited Retinal Dystrophies by Targeted Genetic Analyses.

Authors:  Hema L Ramkumar; Harini V Gudiseva; Kameron T Kishaba; John J Suk; Rohan Verma; Keerti Tadimeti; John A Thorson; Radha Ayyagari
Journal:  Genet Test Mol Biomarkers       Date:  2016-12-22

4.  High-throughput retina-array for screening 93 genes involved in inherited retinal dystrophy.

Authors:  Jin Song; Nizar Smaoui; Radha Ayyagari; David Stiles; Sonia Benhamed; Ian M MacDonald; Stephen P Daiger; Santa J Tumminia; Fielding Hejtmancik; Xinjing Wang
Journal:  Invest Ophthalmol Vis Sci       Date:  2011-11-25       Impact factor: 4.799

5.  PRPH2 mutation update: In silico assessment of 245 reported and 7 novel variants in patients with retinal disease.

Authors:  Manon H C A Peeters; Mubeen Khan; Anoek A M B Rooijakkers; Timo Mulders; Lonneke Haer-Wigman; Camiel J F Boon; Caroline C W Klaver; L Ingeborgh van den Born; Carel B Hoyng; Frans P M Cremers; Anneke I den Hollander; Claire-Marie Dhaenens; Rob W J Collin
Journal:  Hum Mutat       Date:  2021-09-20       Impact factor: 4.700

6.  Biallelic mutation of BEST1 causes a distinct retinopathy in humans.

Authors:  Rosemary Burgess; Ian D Millar; Bart P Leroy; Jill E Urquhart; Ian M Fearon; Elfrida De Baere; Peter D Brown; Anthony G Robson; Genevieve A Wright; Philippe Kestelyn; Graham E Holder; Andrew R Webster; Forbes D C Manson; Graeme C M Black
Journal:  Am J Hum Genet       Date:  2008-01       Impact factor: 11.025

Review 7.  Dawn of ocular gene therapy: implications for molecular diagnosis in retinal disease.

Authors:  Jacques Zaneveld; Feng Wang; Xia Wang; Rui Chen
Journal:  Sci China Life Sci       Date:  2013-02-08       Impact factor: 6.038

8.  Current understanding of genetics and genetic testing and information needs and preferences of adults with inherited retinal disease.

Authors:  Martin McKibbin; Mushtaq Ahmed; Matthew J Allsop; Louise Downey; Richard Gale; Hilary Louise Grant; Barbara Potrata; Thomas A Willis; Jenny Hewison
Journal:  Eur J Hum Genet       Date:  2014-01-08       Impact factor: 4.246

9.  UniPrime: a workflow-based platform for improved universal primer design.

Authors:  Michaël Bekaert; Emma C Teeling
Journal:  Nucleic Acids Res       Date:  2008-04-19       Impact factor: 16.971

10.  Management of a South African family with retinitis pigmentosa-should potential therapy influence translational research protocols?

Authors:  Lisa Roberts; George Rebello; Rajkumar Ramesar; Jacquie Greenberg
Journal:  J Ocul Biol Dis Infor       Date:  2008-05-29
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