Literature DB >> 34717818

Challenges in estimating numbers of vectors integrated in gene-modified cells using DNA sequence information.

Frederic D Bushman1, Adrian Cantu2, John Everett2, Denise Sabatino3, Charles Berry4.   

Abstract

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Year:  2021        PMID: 34717818      PMCID: PMC8636165          DOI: 10.1016/j.ymthe.2021.10.022

Source DB:  PubMed          Journal:  Mol Ther        ISSN: 1525-0016            Impact factor:   11.454


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  12 in total

1.  Bioinformatic clonality analysis of next-generation sequencing-derived viral vector integration sites.

Authors:  Anne Arens; Jens-Uwe Appelt; Cynthia C Bartholomae; Richard Gabriel; Anna Paruzynski; Derek Gustafson; Nathalie Cartier; Patrick Aubourg; Annette Deichmann; Hanno Glimm; Christof von Kalle; Manfred Schmidt
Journal:  Hum Gene Ther Methods       Date:  2012-05-04       Impact factor: 2.396

2.  Estimating abundances of retroviral insertion sites from DNA fragment length data.

Authors:  Charles C Berry; Nicolas A Gillet; Anat Melamed; Niall Gormley; Charles R M Bangham; Frederic D Bushman
Journal:  Bioinformatics       Date:  2012-01-11       Impact factor: 6.937

3.  Clonal tracking in gene therapy patients reveals a diversity of human hematopoietic differentiation programs.

Authors:  Emmanuelle Six; Agathe Guilloux; Adeline Denis; Arnaud Lecoules; Alessandra Magnani; Romain Vilette; Frances Male; Nicolas Cagnard; Marianne Delville; Elisa Magrin; Laure Caccavelli; Cécile Roudaut; Clemence Plantier; Steicy Sobrino; John Gregg; Christopher L Nobles; John K Everett; Salima Hacein-Bey-Abina; Anne Galy; Alain Fischer; Adrian J Thrasher; Isabelle André; Marina Cavazzana; Frederic D Bushman
Journal:  Blood       Date:  2020-04-09       Impact factor: 22.113

4.  Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency.

Authors:  Bryanna Reinhardt; Omar Habib; Kit L Shaw; Elizabeth Garabedian; Denise A Carbonaro-Sarracino; Dayna Terrazas; Beatriz Campo Fernandez; Satiro De Oliveira; Theodore B Moore; Alan K Ikeda; Barbara C Engel; Gregory M Podsakoff; Roger P Hollis; Augustine Fernandes; Connie Jackson; Sally Shupien; Suparna Mishra; Alejandra Davila; Jack Mottahedeh; Andrej Vitomirov; Wenzhao Meng; Aaron M Rosenfeld; Aoife M Roche; Pascha Hokama; Shantan Reddy; John Everett; Xiaoyan Wang; Eline T Luning Prak; Kenneth Cornetta; Michael S Hershfield; Robert Sokolic; Suk See De Ravin; Harry L Malech; Frederic D Bushman; Fabio Candotti; Donald B Kohn
Journal:  Blood       Date:  2021-10-14       Impact factor: 25.476

5.  Estimating and comparing microbial diversity in the presence of sequencing errors.

Authors:  Chun-Huo Chiu; Anne Chao
Journal:  PeerJ       Date:  2016-02-01       Impact factor: 2.984

6.  VISPA2: a scalable pipeline for high-throughput identification and annotation of vector integration sites.

Authors:  Giulio Spinozzi; Andrea Calabria; Stefano Brasca; Stefano Beretta; Ivan Merelli; Luciano Milanesi; Eugenio Montini
Journal:  BMC Bioinformatics       Date:  2017-11-25       Impact factor: 3.169

7.  INSPIIRED: Quantification and Visualization Tools for Analyzing Integration Site Distributions.

Authors:  Charles C Berry; Christopher Nobles; Emmanuelle Six; Yinghua Wu; Nirav Malani; Eric Sherman; Anatoly Dryga; John K Everett; Frances Male; Aubrey Bailey; Kyle Bittinger; Mary J Drake; Laure Caccavelli; Paul Bates; Salima Hacein-Bey-Abina; Marina Cavazzana; Frederic D Bushman
Journal:  Mol Ther Methods Clin Dev       Date:  2016-12-18       Impact factor: 6.698

8.  GENE-IS: Time-Efficient and Accurate Analysis of Viral Integration Events in Large-Scale Gene Therapy Data.

Authors:  Saira Afzal; Stefan Wilkening; Christof von Kalle; Manfred Schmidt; Raffaele Fronza
Journal:  Mol Ther Nucleic Acids       Date:  2016-12-10

9.  Variation in proviral content among human genomes mediated by LTR recombination.

Authors:  Jainy Thomas; Hervé Perron; Cédric Feschotte
Journal:  Mob DNA       Date:  2018-12-18

10.  A long-term study of AAV gene therapy in dogs with hemophilia A identifies clonal expansions of transduced liver cells.

Authors:  Giang N Nguyen; John K Everett; Samita Kafle; Aoife M Roche; Hayley E Raymond; Jacob Leiby; Christian Wood; Charles-Antoine Assenmacher; Elizabeth P Merricks; C Tyler Long; Haig H Kazazian; Timothy C Nichols; Frederic D Bushman; Denise E Sabatino
Journal:  Nat Biotechnol       Date:  2020-11-16       Impact factor: 54.908

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  2 in total

Review 1.  Evaluating the state of the science for adeno-associated virus integration: An integrated perspective.

Authors:  Denise E Sabatino; Frederic D Bushman; Randy J Chandler; Ronald G Crystal; Beverly L Davidson; Ricardo Dolmetsch; Kevin C Eggan; Guangping Gao; Irene Gil-Farina; Mark A Kay; Douglas M McCarty; Eugenio Montini; Adora Ndu; Jing Yuan
Journal:  Mol Ther       Date:  2022-06-10       Impact factor: 12.910

Review 2.  Liquid biopsy in lung cancer: significance in diagnostics, prediction, and treatment monitoring.

Authors:  Wen Li; Ji-Bin Liu; Li-Kun Hou; Fei Yu; Jie Zhang; Wei Wu; Xiao-Mei Tang; Feng Sun; Hai-Min Lu; Jing Deng; Jie Bai; Juan Li; Chun-Yan Wu; Qin-Lu Lin; Zhong-Wei Lv; Gao-Ren Wang; Geng-Xi Jiang; Yu-Shui Ma; Da Fu
Journal:  Mol Cancer       Date:  2022-01-20       Impact factor: 27.401

  2 in total

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