Literature DB >> 34012000

Double setback for ASO trials in Huntington disease.

Katie Kingwell.   

Abstract

Entities:  

Year:  2021        PMID： 34012000     DOI： 10.1038/d41573-021-00088-6

Source DB:  PubMed          Journal:  Nat Rev Drug Discov        ISSN： 1474-1776            Impact factor:   84.694


× No keyword cloud information.
  13 in total

Review 1.  CRISPR-Based Genome-Editing Tools for Huntington's Disease Research and Therapy.

Authors:  Yiyang Qin; Shihua Li; Xiao-Jiang Li; Su Yang
Journal:  Neurosci Bull       Date:  2022-05-24       Impact factor: 5.203

Review 2.  Potential disease-modifying therapies for Huntington's disease: lessons learned and future opportunities.

Authors:  Sarah J Tabrizi; Carlos Estevez-Fraga; Willeke M C van Roon-Mom; Michael D Flower; Rachael I Scahill; Edward J Wild; Ignacio Muñoz-Sanjuan; Cristina Sampaio; Anne E Rosser; Blair R Leavitt
Journal:  Lancet Neurol       Date:  2022-07       Impact factor: 59.935

3.  Ribonuclease recruitment using a small molecule reduced c9ALS/FTD r(G4C2) repeat expansion in vitro and in vivo ALS models.

Authors:  Jessica A Bush; Haruo Aikawa; Rita Fuerst; Yue Li; Andrei Ursu; Samantha M Meyer; Raphael I Benhamou; Jonathan L Chen; Tanya Khan; Sarah Wagner-Griffin; Montina J Van Meter; Yuquan Tong; Hailey Olafson; Kendra K McKee; Jessica L Childs-Disney; Tania F Gendron; Yongjie Zhang; Alyssa N Coyne; Eric T Wang; Ilyas Yildirim; Kye Won Wang; Leonard Petrucelli; Jeffrey D Rothstein; Matthew D Disney
Journal:  Sci Transl Med       Date:  2021-10-27       Impact factor: 19.319

Review 4.  [Disease-modifying treatment approaches in Huntington disease : Past and future].

Authors:  Wiebke Frank; Katrin S Lindenberg; Alzbeta Mühlbäck; Jan Lewerenz; G Bernhard Landwehrmeyer
Journal:  Nervenarzt       Date:  2021-11-11       Impact factor: 1.297

5.  Clinical advances of RNA therapeutics for treatment of neurological and neuromuscular diseases.

Authors:  Anja Holm; Stine N Hansen; Henrik Klitgaard; Sakari Kauppinen
Journal:  RNA Biol       Date:  2021-12-31       Impact factor: 4.766

Review 6.  A Double-Pronged Sword: XJB-5-131 Is a Suppressor of Somatic Instability and Toxicity in Huntington's Disease.

Authors:  Pater Wipf; Aris A Polyzos; Cynthia T McMurray
Journal:  J Huntingtons Dis       Date:  2022

7.  Distinct subcellular autophagy impairments in induced neurons from patients with Huntington's disease.

Authors:  Karolina Pircs; Janelle Drouin-Ouellet; Vivien Horváth; Jeovanis Gil; Melinda Rezeli; Raquel Garza; Daniela A Grassi; Yogita Sharma; Isabelle St-Amour; Kate Harris; Marie E Jönsson; Pia A Johansson; Romina Vuono; Shaline V Fazal; Thomas Stoker; Bob A Hersbach; Kritika Sharma; Jessica Lagerwall; Stina Lagerström; Petter Storm; Sébastien S Hébert; György Marko-Varga; Malin Parmar; Roger A Barker; Johan Jakobsson
Journal:  Brain       Date:  2022-09-14       Impact factor: 15.255

Review 8.  Nucleic Acid-Based Therapeutic Approach for Spinal and Bulbar Muscular Atrophy and Related Neurological Disorders.

Authors:  Tomoki Hirunagi; Kentaro Sahashi; Katherine G Meilleur; Masahisa Katsuno
Journal:  Genes (Basel)       Date:  2022-01-05       Impact factor: 4.096

Review 9.  Nanocarriers for Delivery of Oligonucleotides to the CNS.

Authors:  David Male; Radka Gromnicova
Journal:  Int J Mol Sci       Date:  2022-01-11       Impact factor: 5.923

Review 10.  Molecular Mechanisms in Pentanucleotide Repeat Diseases.

Authors:  Joana R Loureiro; Ana F Castro; Ana S Figueiredo; Isabel Silveira
Journal:  Cells       Date:  2022-01-08       Impact factor: 6.600
View more

北京卡尤迪生物科技股份有限公司 © 2022-2023.