Literature DB >> 33876307

The importance of genetic testing for dystonia patients and translational research.

Jelena Pozojevic1, Christian Beetz2, Ana Westenberger3,4.   

Abstract

Genetic testing through a variety of methods is a fundamental but underutilized approach for establishing the precise genetic diagnosis in patients with heritable forms of dystonia. Our knowledge of numerous dystonia-related genes, variants that they may contain, associated clinical presentations, and molecular disease mechanism may have significant translational potential for patients with genetically confirmed dystonia or their family members. Importantly, genetic testing permits the assembly of patient cohorts pertinent for dystonia-related research and developing therapeutics. Here we review the genetic testing approaches relevant to dystonia patients, and summarize and illustrate the multifold benefits of establishing an accurate molecular diagnosis for patients imminently or for translational research in the long run.

Entities:  

Keywords:  Dystonia; Genetic modifiers; Genetic testing; Precision medicine

Year:  2021        PMID: 33876307     DOI: 10.1007/s00702-021-02329-9

Source DB:  PubMed          Journal:  J Neural Transm (Vienna)        ISSN: 0300-9564            Impact factor:   3.575


  53 in total

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Authors:  Aida M Bertoli-Avella; Christian Beetz; Najim Ameziane; Maria Eugenia Rocha; Pilar Guatibonza; Catarina Pereira; Maria Calvo; Natalia Herrera-Ordonez; Monica Segura-Castel; Dan Diego-Alvarez; Michal Zawada; Krishna K Kandaswamy; Martin Werber; Omid Paknia; Susan Zielske; Dimitar Ugrinovski; Gitte Warnack; Kapil Kampe; Marius-Ionuț Iurașcu; Claudia Cozma; Florian Vogel; Amal Alhashem; Jozef Hertecant; Aisha M Al-Shamsi; Abdulrahman Faiz Alswaid; Wafaa Eyaid; Fuad Al Mutairi; Ahmed Alfares; Mohammed A Albalwi; Majid Alfadhel; Nouriya Abbas Al-Sannaa; Willie Reardon; Yasemin Alanay; Arndt Rolfs; Peter Bauer
Journal:  Eur J Hum Genet       Date:  2020-08-28       Impact factor: 4.246

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  2 in total

1.  Untwisting dystonia: stepping-up genetics, shifting pathophysiology, and strategizing care.

Authors:  Raymond L Rosales; Ana Westenberger
Journal:  J Neural Transm (Vienna)       Date:  2021-04-30       Impact factor: 3.575

Review 2.  The apparent paradox of phenotypic diversity and shared mechanisms across dystonia syndromes.

Authors:  Alessio Di Fonzo; Alberto Albanese; Hyder A Jinnah
Journal:  Curr Opin Neurol       Date:  2022-07-05       Impact factor: 6.283

  2 in total

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