Literature DB >> 33394000

Assessment of rAAVrh.74.MHCK7.micro-dystrophin Gene Therapy Using Magnetic Resonance Imaging in Children With Duchenne Muscular Dystrophy.

Rebecca J Willcocks1, Sean C Forbes1, Glenn A Walter1, Lee Sweeney1, Louise R Rodino-Klapac2, Jerry R Mendell3, Krista Vandenborne1.   

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Year:  2021        PMID： 33394000      PMCID： PMC7783546          DOI： 10.1001/jamanetworkopen.2020.31851

Source DB:  PubMed          Journal:  JAMA Netw Open        ISSN： 2574-3805


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  5 in total

1.  Multicenter prospective longitudinal study of magnetic resonance biomarkers in a large duchenne muscular dystrophy cohort.

Authors:  Rebecca J Willcocks; William D Rooney; William T Triplett; Sean C Forbes; Donovan J Lott; Claudia R Senesac; Michael J Daniels; Dah-Jyuu Wang; Ann T Harrington; Gihan I Tennekoon; Barry S Russman; Erika L Finanger; Barry J Byrne; Richard S Finkel; Glenn A Walter; H Lee Sweeney; Krista Vandenborne
Journal:  Ann Neurol       Date:  2016-02-19       Impact factor: 10.422

2.  Examination of effects of corticosteroids on skeletal muscles of boys with DMD using MRI and MRS.

Authors:  Ishu Arpan; Rebecca J Willcocks; Sean C Forbes; Richard S Finkel; Donovan J Lott; William D Rooney; William T Triplett; Claudia R Senesac; Michael J Daniels; Barry J Byrne; Erika L Finanger; Barry S Russman; Dah-Jyuu Wang; Gihan I Tennekoon; Glenn A Walter; H L Sweeney; Krista Vandenborne
Journal:  Neurology       Date:  2014-08-06       Impact factor: 9.910

3.  MR biomarkers predict clinical function in Duchenne muscular dystrophy.

Authors:  Alison M Barnard; Rebecca J Willcocks; William T Triplett; Sean C Forbes; Michael J Daniels; Saptarshi Chakraborty; Donovan J Lott; Claudia R Senesac; Erika L Finanger; Ann T Harrington; Gihan Tennekoon; Harneet Arora; Dah-Jyuu Wang; H Lee Sweeney; William D Rooney; Glenn A Walter; Krista Vandenborne
Journal:  Neurology       Date:  2020-02-05       Impact factor: 9.910

4.  Skeletal muscle magnetic resonance biomarkers correlate with function and sentinel events in Duchenne muscular dystrophy.

Authors:  Alison M Barnard; Rebecca J Willcocks; Erika L Finanger; Michael J Daniels; William T Triplett; William D Rooney; Donovan J Lott; Sean C Forbes; Dah-Jyuu Wang; Claudia R Senesac; Ann T Harrington; Richard S Finkel; Barry S Russman; Barry J Byrne; Gihan I Tennekoon; Glenn A Walter; H Lee Sweeney; Krista Vandenborne
Journal:  PLoS One       Date:  2018-03-19       Impact factor: 3.240

5.  Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial.

Authors:  Jerry R Mendell; Zarife Sahenk; Kelly Lehman; Carrie Nease; Linda P Lowes; Natalie F Miller; Megan A Iammarino; Lindsay N Alfano; Amanda Nicholl; Samiah Al-Zaidy; Sarah Lewis; Kathleen Church; Richard Shell; Linda H Cripe; Rachael A Potter; Danielle A Griffin; Eric Pozsgai; Ashish Dugar; Mark Hogan; Louise R Rodino-Klapac
Journal:  JAMA Neurol       Date:  2020-09-01       Impact factor: 18.302
  5 in total
  7 in total

1.  Genetic correction strategies for Duchenne Muscular Dystrophy and their impact on the heart.

Authors:  Jamie R Johnston; Elizabeth M McNally
Journal:  Prog Pediatr Cardiol       Date:  2021-11-02

2.  Myeloid mineralocorticoid receptors contribute to skeletal muscle repair in muscular dystrophy and acute muscle injury.

Authors:  Zachary M Howard; Neha Rastogi; Jeovanna Lowe; J Spencer Hauck; Pratham Ingale; Chetan Gomatam; Celso E Gomez-Sanchez; Elise P Gomez-Sanchez; Shyam S Bansal; Jill A Rafael-Fortney
Journal:  Am J Physiol Cell Physiol       Date:  2022-01-19       Impact factor: 4.249

Review 3.  Therapeutic Strategies for Dystrophin Replacement in Duchenne Muscular Dystrophy.

Authors:  Cedric Happi Mbakam; Gabriel Lamothe; Jacques P Tremblay
Journal:  Front Med (Lausanne)       Date:  2022-03-28

Review 4.  Molecular and cellular basis of genetically inherited skeletal muscle disorders.

Authors:  James J Dowling; Conrad C Weihl; Melissa J Spencer
Journal:  Nat Rev Mol Cell Biol       Date:  2021-07-13       Impact factor: 94.444

Review 5.  Muscle-MRI and Functional Levels for the Evaluation of Upper Limbs in Duchenne Muscular Dystrophy: A Critical Review of the Literature.

Authors:  Lara Cristiano; Claudia Brogna; Giorgio Tasca; Tommaso Verdolotti; Marika Pane; Eugenio Mercuri
Journal:  Medicina (Kaunas)       Date:  2022-03-17       Impact factor: 2.430

6.  Human dystrophin expressing chimeric (DEC) cell therapy ameliorates cardiac, respiratory, and skeletal muscle's function in Duchenne muscular dystrophy.

Authors:  Maria Siemionow; Paulina Langa; Michal Harasymczuk; Joanna Cwykiel; Magdalena Sielewicz; Jaroslaw Smieszek; Ahlke Heydemann
Journal:  Stem Cells Transl Med       Date:  2021-07-22       Impact factor: 6.940

Review 7.  Exon-Skipping in Duchenne Muscular Dystrophy.

Authors:  Shin'ichi Takeda; Paula R Clemens; Eric P Hoffman
Journal:  J Neuromuscul Dis       Date:  2021
  7 in total

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