Literature DB >> 33384365

RNA-targeted drugs for neuromuscular diseases.

Alessandra Ferlini1,2, Aurelie Goyenvalle3, Francesco Muntoni4,5.   

Abstract

Entities:  

Year:  2021        PMID: 33384365     DOI: 10.1126/science.aba4515

Source DB:  PubMed          Journal:  Science        ISSN: 0036-8075            Impact factor:   47.728


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  4 in total

1.  RNA-binding proteins direct myogenic cell fate decisions.

Authors:  Joshua R Wheeler; Oscar N Whitney; Thomas O Vogler; Eric D Nguyen; Bradley Pawlikowski; Evan Lester; Alicia Cutler; Tiffany Elston; Nicole Dalla Betta; Kevin R Parker; Kathryn E Yost; Hannes Vogel; Thomas A Rando; Howard Y Chang; Aaron M Johnson; Roy Parker; Bradley B Olwin
Journal:  Elife       Date:  2022-06-13       Impact factor: 8.713

2.  Palmitic acid conjugation enhances potency of tricyclo-DNA splice switching oligonucleotides.

Authors:  Karima Relizani; Lucía Echevarría; Faouzi Zarrouki; Cécile Gastaldi; Chloe Dambrune; Philippine Aupy; Adrian Haeberli; Marek Komisarski; Thomas Tensorer; Thibaut Larcher; Fedor Svinartchouk; Cyrille Vaillend; Luis Garcia; Aurélie Goyenvalle
Journal:  Nucleic Acids Res       Date:  2022-01-11       Impact factor: 16.971

Review 3.  Common and Rare 5'UTR Variants Altering Upstream Open Reading Frames in Cardiovascular Genomics.

Authors:  Omar Soukarieh; Caroline Meguerditchian; Carole Proust; Dylan Aïssi; Mélanie Eyries; Aurélie Goyenvalle; David-Alexandre Trégouët
Journal:  Front Cardiovasc Med       Date:  2022-03-21

4.  Partial Restoration of Brain Dystrophin and Behavioral Deficits by Exon Skipping in the Muscular Dystrophy X-Linked (mdx) Mouse.

Authors:  Cyrille Vaillend; Aurélie Goyenvalle; Faouzi Zarrouki; Karima Relizani; Flavien Bizot; Thomas Tensorer; Luis Garcia
Journal:  Ann Neurol       Date:  2022-06-13       Impact factor: 11.274

  4 in total

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