Literature DB >> 33058866

Identifying Novel Susceptibility Genes for Colorectal Cancer Risk From a Transcriptome-Wide Association Study of 125,478 Subjects.

Xingyi Guo1, Weiqiang Lin2, Wanqing Wen3, Jeroen Huyghe4, Stephanie Bien4, Qiuyin Cai3, Tabitha Harrison4, Zhishan Chen3, Conghui Qu4, Jiandong Bao3, Jirong Long3, Yuan Yuan2, Fangqin Wang2, Mengqiu Bai2, Goncalo R Abecasis5, Demetrius Albanes6, Sonja I Berndt6, Stéphane Bézieau7, D Timothy Bishop8, Hermann Brenner9, Stephan Buch10, Andrea Burnett-Hartman11, Peter T Campbell12, Sergi Castellví-Bel13, Andrew T Chan14, Jenny Chang-Claude15, Stephen J Chanock6, Sang Hee Cho16, David V Conti17, Albert de la Chapelle18, Edith J M Feskens19, Steven J Gallinger20, Graham G Giles21, Phyllis J Goodman22, Andrea Gsur23, Mark Guinter12, Marc J Gunter24, Jochen Hampe10, Heather Hampel25, Richard B Hayes26, Michael Hoffmeister27, Ellen Kampman19, Hyun Min Kang5, Temitope O Keku28, Hyeong Rok Kim29, Loic Le Marchand30, Soo Chin Lee31, Christopher I Li4, Li Li32, Annika Lindblom33, Noralane Lindor34, Roger L Milne21, Victor Moreno35, Neil Murphy12, Polly A Newcomb36, Deborah A Nickerson37, Kenneth Offit38, Rachel Pearlman25, Paul D P Pharoah39, Elizabeth A Platz40, John D Potter4, Gad Rennert41, Lori C Sakoda42, Clemens Schafmayer43, Stephanie L Schmit44, Robert E Schoen45, Fredrick R Schumacher46, Martha L Slattery47, Yu-Ru Su4, Catherine M Tangen22, Cornelia M Ulrich48, Franzel J B van Duijnhoven19, Bethany Van Guelpen49, Kala Visvanathan40, Pavel Vodicka50, Ludmila Vodickova50, Veronika Vymetalkova50, Xiaoliang Wang4, Emily White51, Alicja Wolk52, Michael O Woods53, Graham Casey54, Li Hsu4, Mark A Jenkins55, Stephen B Gruber17, Ulrike Peters51, Wei Zheng3.   

Abstract

BACKGROUND AND AIMS: Susceptibility genes and the underlying mechanisms for the majority of risk loci identified by genome-wide association studies (GWAS) for colorectal cancer (CRC) risk remain largely unknown. We conducted a transcriptome-wide association study (TWAS) to identify putative susceptibility genes.
METHODS: Gene-expression prediction models were built using transcriptome and genetic data from the 284 normal transverse colon tissues of European descendants from the Genotype-Tissue Expression (GTEx), and model performance was evaluated using data from The Cancer Genome Atlas (n = 355). We applied the gene-expression prediction models and GWAS data to evaluate associations of genetically predicted gene-expression with CRC risk in 58,131 CRC cases and 67,347 controls of European ancestry. Dual-luciferase reporter assays and knockdown experiments in CRC cells and tumor xenografts were conducted.
RESULTS: We identified 25 genes associated with CRC risk at a Bonferroni-corrected threshold of P < 9.1 × 10-6, including genes in 4 novel loci, PYGL (14q22.1), RPL28 (19q13.42), CAPN12 (19q13.2), MYH7B (20q11.22), and MAP1L3CA (20q11.22). In 9 known GWAS-identified loci, we uncovered 9 genes that have not been reported previously, whereas 4 genes remained statistically significant after adjusting for the lead risk variant of the locus. Through colocalization analysis in GWAS loci, we additionally identified 12 putative susceptibility genes that were supported by TWAS analysis at P < .01. We showed that risk allele of the lead risk variant rs1741640 affected the promoter activity of CABLES2. Knockdown experiments confirmed that CABLES2 plays a vital role in colorectal carcinogenesis.
CONCLUSIONS: Our study reveals new putative susceptibility genes and provides new insight into the biological mechanisms underlying CRC development.
Copyright © 2021 AGA Institute. Published by Elsevier Inc. All rights reserved.

Entities:  

Keywords:  CABLES2; Colorectal Cancer; Susceptibility Genes; TWAS

Mesh:

Substances:

Year:  2020        PMID: 33058866      PMCID: PMC7956223          DOI: 10.1053/j.gastro.2020.08.062

Source DB:  PubMed          Journal:  Gastroenterology        ISSN: 0016-5085            Impact factor:   33.883


  74 in total

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