Literature DB >> 32749600

Nerve ultrasound in hereditary transthyretin amyloidosis: red flags and possible progression biomarkers.

Alessandro Salvalaggio1,2, Daniele Coraci3, Mario Cacciavillani4, Laura Obici5, Anna Mazzeo6, Marco Luigetti7, Francesca Pastorelli8, Marina Grandis9,10, Tiziana Cavallaro11, Giulia Bisogni12, Alessandro Lozza5, Chiara Gemelli9, Luca Gentile6, Mario Ermani13, Gian Maria Fabrizi11, Rosaria Plasmati8, Marta Campagnolo13, Francesca Castellani13, Roberto Gasparotti14, Carlo Martinoli10,15, Luca Padua3,16, Chiara Briani13.   

Abstract

BACKGROUND: Diagnostic delay of hereditary transthyretin amyloidosis (ATTRv, v for variant) prevents timely treatment and, therefore, concurs to the mortality of the disease. The aim of the present study was to explore with nerve ultrasound (US) possible red flags for early diagnosis in ATTRv patients with carpal tunnel syndrome (CTS) and/or polyneuropathy and in pre-symptomatic carriers.
METHODS: Patients and pre-symptomatic carriers with a TTR gene mutation were enrolled from seven Italian centers. Severity of CTS was assessed with neurophysiology and clinical evaluation. Median nerve cross-section area (CSA) was measured with US in ATTRv carriers with CTS (TTR-CTS). One thousand one hundred ninety-six idiopathic CTS were used as controls. Nerve US was also performed in several nerve trunks (median, ulnar, radial, brachial plexi, tibial, peroneal, sciatic, sural) in ATTRv patients with polyneuropathy and in pre-symptomatic carriers.
RESULTS: Sixty-two subjects (34 men, 28 women, mean age 59.8 years ± 12) with TTR gene mutation were recruited. With regard to CTS, while in idiopathic CTS there was a direct correlation between CTS severity and median nerve CSA (r = 0.55, p < 0.01), in the subgroup of TTR-CTS subjects (16 subjects, 5 with bilateral CTS) CSA did not significantly correlate with CTS severity (r = - 0.473). ATTRv patients with polyneuropathy showed larger CSA than pre-symptomatic carriers in several nerve sites, more pronounced at brachial plexi (p < 0.001).
CONCLUSIONS: The present study identifies nerve morphological US patterns that may help in the early diagnosis (morpho-functional dissociation of median nerve in CTS) and monitoring of pre-symptomatic TTR carriers (larger nerve CSA at proximal nerve sites, especially at brachial plexi).

Entities:  

Keywords:  ATTRv; Amyloidotic polyneuropathy; Carpal tunnel syndrome; Nerve ultrasound; Transthyretin amyloidosis

Mesh:

Substances:

Year:  2020        PMID: 32749600      PMCID: PMC7815618          DOI: 10.1007/s00415-020-10127-8

Source DB:  PubMed          Journal:  J Neurol        ISSN: 0340-5354            Impact factor:   4.849


  2 in total

1.  Correction to: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis.

Authors:  Alejandra González-Duarte; John L Berk; Dianna Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Márcia Waddington-Cruz; Mitsuharu Ueda; Isabel M Conceição; Arnt V Kristen; Teresa Coelho; Cécile A Cauquil; Céline Tard; Madeline Merkel; Emre Aldinc; Jihong Chen; Marianne T Sweetser; Jing Jing Wang; David Adams
Journal:  J Neurol       Date:  2020-03       Impact factor: 4.849

2.  Arterial thrombo-embolic events in cardiac amyloidosis: a look beyond atrial fibrillation.

Authors:  Francesco Cappelli; Giacomo Tini; Domitilla Russo; Michele Emdin; Annamaria Del Franco; Giuseppe Vergaro; Gianluca Di Bella; Anna Mazzeo; Marco Canepa; Massimo Volpe; Federico Perfetto; Camillo Autore; Carlo Di Mario; Claudio Rapezzi; Maria Beatrice Musumeci
Journal:  Amyloid       Date:  2020-09-28       Impact factor: 7.141

  2 in total
  12 in total

1.  Patisiran in hATTR Amyloidosis: Six-Month Latency Period before Efficacy.

Authors:  Luca Gentile; Massimo Russo; Marco Luigetti; Giulia Bisogni; Andrea Di Paolantonio; Angela Romano; Valeria Guglielmino; Ilenia Arimatea; Mario Sabatelli; Antonio Toscano; Giuseppe Vita; Anna Mazzeo
Journal:  Brain Sci       Date:  2021-04-19

2.  Cutaneous silent period in ATTRv carriers: a possible early marker of nerve damage?

Authors:  Marco Luigetti; Andrea Di Paolantonio; Valeria Guglielmino; Angela Romano
Journal:  Neurol Sci       Date:  2022-08-09       Impact factor: 3.830

3.  Can we identify hereditary TTR amyloidosis by the screening of carpal tunnel syndrome patients?

Authors:  Daniele Severi; Francesco Aruta; Aniello Iovino; Emanuele Spina; Maria Nolano; Fiore Manganelli; Stefano Tozza
Journal:  Neurol Sci       Date:  2022-01-31       Impact factor: 3.830

4.  High-resolution ultrasound of peripheral nerves in late-onset hereditary transthyretin amyloidosis with polyneuropathy: similarities and differences with CIDP.

Authors:  Luca Leonardi; Giuseppe Di Pietro; Antonella Di Pasquale; Fiammetta Vanoli; Laura Fionda; Matteo Garibaldi; Eleonora Galosi; Girolamo Alfieri; Antonio Lauletta; Stefania Morino; Marco Salvetti; Andrea Truini; Giovanni Antonini
Journal:  Neurol Sci       Date:  2021-11-21       Impact factor: 3.830

5.  Peripheral nerve involvement in wild-type transthyretin amyloidosis.

Authors:  Marta Campagnolo; Mario Cacciavillani; Alberto Cipriani; Alessandro Salvalaggio; Francesca Castellani; Kalliopi Pilichou; Chiara Briani
Journal:  Neurol Sci       Date:  2022-10-19       Impact factor: 3.830

Review 6.  Novel approaches to diagnosis and management of hereditary transthyretin amyloidosis.

Authors:  Antonia Carroll; P James Dyck; Mamede de Carvalho; Marina Kennerson; Mary M Reilly; Matthew C Kiernan; Steve Vucic
Journal:  J Neurol Neurosurg Psychiatry       Date:  2022-03-07       Impact factor: 13.654

7.  Nerve Ultrasound Comparison Between Transthyretin Familial Amyloid Polyneuropathy and Chronic Inflammatory Demyelinating Polyneuropathy.

Authors:  Kang Du; Ke Xu; Si Cheng; He Lv; Wei Zhang; Zhaoxia Wang; Yun Yuan; Lingchao Meng
Journal:  Front Neurol       Date:  2021-02-26       Impact factor: 4.003

Review 8.  Nerve Ultrasound as Helpful Tool in Polyneuropathies.

Authors:  Magdalena Kramer; Alexander Grimm; Natalie Winter; Marc Dörner; Kathrin Grundmann-Hauser; Jan-Hendrik Stahl; Julia Wittlinger; Josua Kegele; Cornelius Kronlage; Sophia Willikens
Journal:  Diagnostics (Basel)       Date:  2021-01-31

9.  TTR Gly83Arg Mutation: Beyond Familial Vitreous Amyloidosis.

Authors:  Zhenxian Li; Kang Du; Xujun Chu; He Lv; Wei Zhang; Zhaoxia Wang; Yun Yuan; Lingchao Meng
Journal:  Front Neurol       Date:  2022-02-03       Impact factor: 4.003

10.  Progressive brachial plexus enlargement in hereditary transthyretin amyloidosis.

Authors:  Alessandro Salvalaggio; Daniele Coraci; Laura Obici; Mario Cacciavillani; Marco Luigetti; Anna Mazzeo; Francesca Pastorelli; Marina Grandis; Tiziana Cavallaro; Giulia Bisogni; Alessandro Lozza; Chiara Gemelli; Luca Gentile; Massimo Russo; Mario Ermani; Gian Maria Fabrizi; Rosaria Plasmati; Federica De Napoli; Marta Campagnolo; Francesca Castellani; Fabrizio Salvi; Silvia Fenu; Grazia Devigili; Davide Pareyson; Roberto Gasparotti; Claudio Rapezzi; Carlo Martinoli; Luca Padua; Chiara Briani
Journal:  J Neurol       Date:  2021-08-19       Impact factor: 4.849

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