Literature DB >> 32030522

Correction to: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis.

Alejandra González-Duarte1, John L Berk2, Dianna Quan3, Michelle L Mauermann4, Hartmut H Schmidt5, Michael Polydefkis6, Márcia Waddington-Cruz7, Mitsuharu Ueda8, Isabel M Conceição9, Arnt V Kristen10, Teresa Coelho11, Cécile A Cauquil12, Céline Tard13, Madeline Merkel14, Emre Aldinc14, Jihong Chen14, Marianne T Sweetser14, Jing Jing Wang14, David Adams15.   

Abstract

The original version of this article unfortunately contained a mistake.

Entities:  

Year:  2020        PMID: 32030522      PMCID: PMC7035215          DOI: 10.1007/s00415-020-09715-5

Source DB:  PubMed          Journal:  J Neurol        ISSN: 0340-5354            Impact factor:   4.849


Correction to: Journal of Neurology 10.1007/s00415-019-09602-8

The original version of this article unfortunately contained a mistake in Table 1.
Table 1

Disease characteristics of autonomic endpoints at baseline

CharacteristicPlacebo (n = 77)Patisiran (n = 148)Total (n = 225)
COMPASS-31 total score (range 0–100), mean (± SD)30.3 (16.4)30.6 (17.6)30.5 (17.1)
 Orthostatic intolerance (range: 0–40), mean (± SD)13.2 (11.2)14.2 (10.8)13.8 (10.9)
 Vasomotor (range 0–5), mean (± SD)1.0 (1.4)0.9 (1.44)1.0 (1.4)
 Secretomotor (range 0–15), mean (± SD)4.9 (3.7)4.2 (3.7)4.4 (3.7)
 Gastrointestinal (range 0–25), mean (± SD)8.1 (3.5)8.2 (4.3)8.1 (4.1)
 Bladder (range 0–10), mean (± SD)1.9 (2.7)2.0 (2.5)2.0 (2.5)
 Pupillomotor (range 0–5), mean (± SD)1.1 (1.1)1.2 (1.2)1.2 (1.2)
mBMI (kg/m2 × g/L), mean (± SD)989.9 (214.2)969.7 (210.5)976.6 (211.5)
 BMI (kg/m2), mean (± SD)23.6 (4.3)23.0 (4.4)23.2 (4.4)
 Albumin (g/L), mean (± SD)41.8 (3.4)42.1 (3.5)42.0 (3.5)
 Weight (kg), mean (± SD)67.5 (15.7)67.3 (16.6)67.4 (16.3)
mNIS + 7 total score (range 0–304), mean (± SD)74.6 (37.0)80.9 (41.5)78.8 (40.1)
 Postural blood pressure (range 0–2), mean (± SD)0.6 (0.7)0.7 (0.8)0.6 (0.8)
Norfolk QOL-DN total score (range − 4 to 136), mean (± SD)55.5 (24.3)59.6 (28.2)58.3 (27.0)
 Autonomic neuropathy domain (range 0–12), mean (± SD)2.9 (2.9)3.0 (2.8)3.0 (2.8)

BMI body mass index, COMPASS-31 Composite Autonomic Symptom Score-31, mBMI modified body mass index, mNIS + 7 modified Neuropathy Impairment Score + 7, Norfolk QOL-DN Norfolk Quality of Life-Diabetic Neuropathy

Disease characteristics of autonomic endpoints at baseline BMI body mass index, COMPASS-31 Composite Autonomic Symptom Score-31, mBMI modified body mass index, mNIS + 7 modified Neuropathy Impairment Score + 7, Norfolk QOL-DN Norfolk Quality of Life-Diabetic Neuropathy Units for albumin were given as g/dL. It should be g/L.
  4 in total

1.  High-resolution ultrasound of peripheral nerves in late-onset hereditary transthyretin amyloidosis with polyneuropathy: similarities and differences with CIDP.

Authors:  Luca Leonardi; Giuseppe Di Pietro; Antonella Di Pasquale; Fiammetta Vanoli; Laura Fionda; Matteo Garibaldi; Eleonora Galosi; Girolamo Alfieri; Antonio Lauletta; Stefania Morino; Marco Salvetti; Andrea Truini; Giovanni Antonini
Journal:  Neurol Sci       Date:  2021-11-21       Impact factor: 3.830

2.  Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-LRx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy.

Authors:  Teresa Coelho; Yukio Ando; Merrill D Benson; John L Berk; Márcia Waddington-Cruz; Peter J Dyck; Julian D Gillmore; Sami L Khella; William J Litchy; Laura Obici; Cecilia Monteiro; Li-Jung Tai; Nicholas J Viney; Gustavo Buchele; Michela Brambatti; Shiangtung W Jung; Louis St L O'Dea; Sotirios Tsimikas; Eugene Schneider; Richard S Geary; Brett P Monia; Morie Gertz
Journal:  Neurol Ther       Date:  2021-02-26

3.  Nerve ultrasound in hereditary transthyretin amyloidosis: red flags and possible progression biomarkers.

Authors:  Alessandro Salvalaggio; Daniele Coraci; Mario Cacciavillani; Laura Obici; Anna Mazzeo; Marco Luigetti; Francesca Pastorelli; Marina Grandis; Tiziana Cavallaro; Giulia Bisogni; Alessandro Lozza; Chiara Gemelli; Luca Gentile; Mario Ermani; Gian Maria Fabrizi; Rosaria Plasmati; Marta Campagnolo; Francesca Castellani; Roberto Gasparotti; Carlo Martinoli; Luca Padua; Chiara Briani
Journal:  J Neurol       Date:  2020-08-04       Impact factor: 4.849

4.  Characteristics of Patients with Late- vs. Early-Onset Val30Met Transthyretin Amyloidosis from the Transthyretin Amyloidosis Outcomes Survey (THAOS).

Authors:  Márcia Waddington-Cruz; Jonas Wixner; Leslie Amass; Jan Kiszko; Doug Chapman; Yukio Ando
Journal:  Neurol Ther       Date:  2021-05-22
  4 in total

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