Literature DB >> 32680806

Immune-related Adverse Events of Pembrolizumab in a Large Real-world Cohort of Patients With NSCLC With a PD-L1 Expression ≥ 50% and Their Relationship With Clinical Outcomes.

Alessio Cortellini1, Alex Friedlaender2, Giuseppe L Banna3, Giampiero Porzio4, Melissa Bersanelli5, Federico Cappuzzo6, Joachim G J V Aerts7, Raffaele Giusti8, Emilio Bria9, Diego Cortinovis10, Francesco Grossi11, Maria R Migliorino12, Domenico Galetta13, Francesco Passiglia14, Rossana Berardi15, Francesca Mazzoni16, Vincenzo Di Noia17, Diego Signorelli18, Alessandro Tuzi19, Alain Gelibter20, Paolo Marchetti21, Marianna Macerelli22, Francesca Rastelli23, Rita Chiari24, Danilo Rocco25, Alessandro Inno26, Pietro Di Marino27, Giovanni Mansueto28, Federica Zoratto29, Matteo Santoni30, Marianna Tudini31, Michele Ghidini11, Marco Filetti8, Annamaria Catino13, Pamela Pizzutilo13, Luca Sala10, Mario Alberto Occhipinti20, Fabrizio Citarella32, Russano Marco32, Mariangela Torniai15, Luca Cantini33, Alessandro Follador22, Vincenzo Sforza34, Olga Nigro19, Miriam G Ferrara9, Ettore D'Argento35, Alessandro Leonetti5, Linda Pettoruti5, Lorenzo Antonuzzo16, Simona Scodes6, Lorenza Landi6, Giorgia Guaitoli36, Cinzia Baldessari36, Federica Bertolini36, Luigi Della Gravara25, Maria Giovanna Dal Bello37, Robert A Belderbos7, Marco De Filippis14, Cristina Cecchi14, Serena Ricciardi12, Clelia Donisi38, Alessandro De Toma18, Claudia Proto18, Alfredo Addeo2, Ornella Cantale3, Biagio Ricciuti39, Carlo Genova37, Alessandro Morabito34, Daniele Santini32, Corrado Ficorella4, Katia Cannita40.   

Abstract

BACKGROUND: The role of immune-related adverse events (irAEs), as a surrogate predictor of the efficacy of checkpoint inhibitors, has not yet been described in the setting of first-line, single-agent pembrolizumab for patients with metastatic non-small-cell lung-cancer (NSCLC) with a programmed death-ligand 1 (PD-L1) expression of ≥ 50%. PATIENTS AND METHODS: We previously conducted a multicenter retrospective analysis in patients with treatment-naive metastatic NSCLC and a PD-L1 expression of ≥ 50% receiving first-line pembrolizumab. Here, we report the results of the irAE analysis and the potential correlation between irAEs and clinical outcomes.
RESULTS: A total of 1010 patients were included in this analysis; after a 6-week landmark selection, 877 (86.8%) patients were included in the efficacy analysis. Any grade irAEs (P < .0001), grade 3/4 irAEs (P = .0025), leading to discontinuation irAEs (P = .0144), multiple-site and single-site irAEs (P < .0001), cutaneous irAEs (P = .0001), endocrine irAEs (P = .0227), pulmonary irAEs (P = .0479), and rheumatologic irAEs (P = .0018) were significantly related to a higher objective response rate. Any grade irAEs (P < .0001), single-site irAEs (P < .0001), multiple-site irAEs (P = .0005), cutaneous irAEs (P = .0042), endocrine irAEs (P < .0001), gastrointestinal irAEs (P = .0391), and rheumatologic irAEs (P = .0086) were significantly related to progression-free survival. Any grade irAEs (P < .0001), single-site irAEs (P < .0001), multiple-site irAEs (P = .0003), cutaneous irAEs (P = .0002), endocrine irAEs (P = .0001), and rheumatologic irAEs (P = .0214) were significantly related to overall survival.
CONCLUSIONS: This study confirms the feasibility and the safety of first-line, single-agent pembrolizumab, in a large, real-world cohort of patients with NSCLC with PD-L1 expression ≥ 50%. The occurrence of irAEs may be a surrogate of clinical activity and improved outcomes in this setting.
Copyright © 2020 Elsevier Inc. All rights reserved.

Entities:  

Keywords:  First line; NSCLC; PD-L1; Pembrolizumab; irAEs

Year:  2020        PMID: 32680806     DOI: 10.1016/j.cllc.2020.06.010

Source DB:  PubMed          Journal:  Clin Lung Cancer        ISSN: 1525-7304            Impact factor:   4.785


  22 in total

1.  Lung nodule radio-guided localization and uniportal video-assisted thoracoscopic surgery resection.

Authors:  Carlos Carvajal; Felipe González; Rafael Beltrán; Ricardo Buitrago; Amelia de Los Reyes; Augusto Llamas; Julián Beltrán; José Carreño
Journal:  Updates Surg       Date:  2021-01-04

2.  Clinical outcomes of NSCLC patients experiencing early immune-related adverse events to PD-1/PD-L1 checkpoint inhibitors leading to treatment discontinuation.

Authors:  Marco Russano; Alessio Cortellini; Raffaele Giusti; Alessandro Russo; Federica Zoratto; Francesca Rastelli; Alain Gelibter; Rita Chiari; Olga Nigro; Michele De Tursi; Sergio Bracarda; Stefania Gori; Francesco Grossi; Melissa Bersanelli; Lorenzo Calvetti; Vincenzo Di Noia; Mario Scartozzi; Massimo Di Maio; Paolo Bossi; Alfredo Falcone; Fabrizio Citarella; Francesco Pantano; Corrado Ficorella; Marco Filetti; Vincenzo Adamo; Enzo Veltri; Federica Pergolesi; Mario Alberto Occhipinti; Linda Nicolardi; Alessandro Tuzi; Pietro Di Marino; Serena Macrini; Alessandro Inno; Michele Ghidini; Sebastiano Buti; Giuseppe Aprile; Eleonora Lai; Marco Audisio; Salvatore Intagliata; Riccardo Marconcini; Davide Brocco; Giampiero Porzio; Marta Piras; Erika Rijavec; Francesca Simionato; Clara Natoli; Marcello Tiseo; Bruno Vincenzi; Giuseppe Tonini; Daniele Santini
Journal:  Cancer Immunol Immunother       Date:  2021-08-31       Impact factor: 6.968

Review 3.  Associations between immune-related thyroid dysfunction and efficacy of immune checkpoint inhibitors: a systematic review and meta-analysis.

Authors:  Yee-Ming Melody Cheung; Wei Wang; Bradley McGregor; Ole-Petter Riksfjord Hamnvik
Journal:  Cancer Immunol Immunother       Date:  2022-01-13       Impact factor: 6.630

4.  Improved survival and disease control following pembrolizumab-induced immune-related adverse events in high PD-L1 expressing non-small cell lung cancer with brain metastases.

Authors:  Michael Zhang; Adrian J Rodrigues; Erqi L Pollom; Iris C Gibbs; Scott G Soltys; Steven L Hancock; Joel W Neal; Sukhmani K Padda; Kavitha J Ramchandran; Heather A Wakelee; Steven D Chang; Michael Lim; Melanie Hayden Gephart; Gordon Li
Journal:  J Neurooncol       Date:  2021-01-07       Impact factor: 4.130

5.  Severe immune-related hyperthermia followed by immune-related pneumonitis with PD-1 inhibitor (sintilimab) in small cell lung cancer: A case report.

Authors:  Yi-Hui Li; Yang Zhou; Yuan-Yuan Liu; Guang-Ju Zhang; Lei Xiao; Na Li; Hai-Feng Qin; Jian-Gong Wang; Li Zhang
Journal:  Thorac Cancer       Date:  2021-05-05       Impact factor: 3.500

6.  Baseline BMI and BMI variation during first line pembrolizumab in NSCLC patients with a PD-L1 expression ≥ 50%: a multicenter study with external validation.

Authors:  Alessio Cortellini; Biagio Ricciuti; Marcello Tiseo; Emilio Bria; Giuseppe L Banna; Joachim Gjv Aerts; Fausto Barbieri; Raffaele Giusti; Diego L Cortinovis; Maria R Migliorino; Annamaria Catino; Francesco Passiglia; Mariangela Torniai; Alessandro Morabito; Carlo Genova; Francesca Mazzoni; Vincenzo Di Noia; Diego Signorelli; Alain Gelibter; Mario Alberto Occhipinti; Francesca Rastelli; Rita Chiari; Danilo Rocco; Alessandro Inno; Michele De Tursi; Pietro Di Marino; Giovanni Mansueto; Federica Zoratto; Francesco Grossi; Marco Filetti; Pamela Pizzutilo; Marco Russano; Fabrizio Citarella; Luca Cantini; Giada Targato; Olga Nigro; Miriam G Ferrara; Sebastiano Buti; Simona Scodes; Lorenza Landi; Giorgia Guaitoli; Luigi Della Gravara; Fabrizio Tabbò; Serena Ricciardi; Alessandro De Toma; Alex Friedlaender; Fausto Petrelli; Alfredo Addeo; Giampiero Porzio; Corrado Ficorella
Journal:  J Immunother Cancer       Date:  2020-10       Impact factor: 13.751

7.  Immune-Related Adverse Events Predict the Efficacy of Immune Checkpoint Inhibitors in Lung Cancer Patients: A Meta-Analysis.

Authors:  Donghui Wang; Cen Chen; Yanli Gu; Wanjun Lu; Ping Zhan; Hongbing Liu; Tangfeng Lv; Yong Song; Fang Zhang
Journal:  Front Oncol       Date:  2021-03-01       Impact factor: 6.244

8.  First-line immunotherapy in non-small cell lung cancer patients with poor performance status: a systematic review and meta-analysis.

Authors:  Francesco Facchinetti; Massimo Di Maio; Fabiana Perrone; Marcello Tiseo
Journal:  Transl Lung Cancer Res       Date:  2021-06

9.  Persistent Response and Prolonged Survival Following Pembrolizumab Discontinuation Due to Long-Lasting Autoimmune Colitis in Advanced NSCLC: A Case Report.

Authors:  Angela Damato; Loredana De Marco; Silvia Serra; Mario Larocca; Alicia Garcia Arias; Ermanno Rondini; Carmine Pinto
Journal:  Front Oncol       Date:  2021-06-17       Impact factor: 6.244

10.  The Gustave Roussy Immune (GRIm)-Score Variation Is an Early-on-Treatment Biomarker of Outcome in Advanced Non-Small Cell Lung Cancer (NSCLC) Patients Treated with First-Line Pembrolizumab.

Authors:  Edoardo Lenci; Luca Cantini; Federica Pecci; Valeria Cognigni; Veronica Agostinelli; Giulia Mentrasti; Alessio Lupi; Nicoletta Ranallo; Francesco Paoloni; Silvia Rinaldi; Linda Nicolardi; Andrea Caglio; Sophie Aerts; Alessio Cortellini; Corrado Ficorella; Rita Chiari; Massimo Di Maio; Anne-Marie C Dingemans; Joachim G J V Aerts; Rossana Berardi
Journal:  J Clin Med       Date:  2021-03-02       Impact factor: 4.241

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