Literature DB >> 32601388

Patient and family social media use surrounding a novel treatment for a rare genetic disease: a qualitative interview study.

Alexander A Iyer1,2, Julie R Barzilay3, Holly K Tabor4.   

Abstract

PURPOSE: Advances in gene therapy and precision medicine have led to a growing number of novel treatments for rare genetic diseases. Patients/families may lack access to up-to-date, accurate, and relevant information about these treatments. Social media offers one potentially important resource for these communities. Our goal was to understand how patients/families with spinal muscular atrophy (SMA)-a rare genetic condition-used social media to share, consume, and evaluate information about the novel treatment nusinersen (Spinraza) following the drug's approval.
METHODS: We conducted qualitative, semistructured interviews with 20 SMA patients or parents of patients, deriving themes and subthemes through content and thematic network analysis. Participants also completed a demographic survey.
RESULTS: Participants described leveraging social media to learn about nusinersen treatment, make informed treatment decisions, and advocate for/access treatment. They also described critically evaluating the trustworthiness of nusinersen-related information on social media and the privacy risks of social media use.
CONCLUSION: Patients/families used social media to navigate the new and dynamic landscape of nusinersen treatment for SMA, while attempting to mitigate misinformation and privacy risks. As new treatments become available, providers and patients/families may benefit from proactively discussing social media use, so as to maximize important benefits while minimizing risks.

Entities:  

Keywords:  gene therapy; nusinersen (Spinraza); rare genetic disease; social media; spinal muscular atrophy

Mesh:

Year:  2020        PMID: 32601388     DOI: 10.1038/s41436-020-0890-6

Source DB:  PubMed          Journal:  Genet Med        ISSN: 1098-3600            Impact factor:   8.822


  23 in total

1.  #Cleft: The use of Social Media Amongst Parents of Infants with Clefts.

Authors:  Joseph S Khouri; Melisande J McCheyne; Clinton S Morrison
Journal:  Cleft Palate Craniofac J       Date:  2018-02-22

Review 2.  Nusinersen, an antisense oligonucleotide drug for spinal muscular atrophy.

Authors:  David R Corey
Journal:  Nat Neurosci       Date:  2017-02-13       Impact factor: 24.884

3.  Ethical Challenges Confronted When Providing Nusinersen Treatment for Spinal Muscular Atrophy.

Authors:  Alyssa M Burgart; David Magnus; Holly K Tabor; Erin Daksha-Talati Paquette; Joel Frader; Jaqueline J Glover; Brian M Jackson; Charlotte H Harrison; David K Urion; Robert J Graham; John F Brandsema; Chris Feudtner
Journal:  JAMA Pediatr       Date:  2018-02-01       Impact factor: 16.193

Review 4.  Spinal muscular atrophy.

Authors:  Mitchell R Lunn; Ching H Wang
Journal:  Lancet       Date:  2008-06-21       Impact factor: 79.321

5.  Perspectives on Spinraza (Nusinersen) Treatment Study: Views of Individuals and Parents of Children Diagnosed with Spinal Muscular Atrophy.

Authors:  Michelle Pacione; Carly E Siskind; John W Day; Holly K Tabor
Journal:  J Neuromuscul Dis       Date:  2019

6.  Pan-ethnic carrier screening and prenatal diagnosis for spinal muscular atrophy: clinical laboratory analysis of >72,400 specimens.

Authors:  Elaine A Sugarman; Narasimhan Nagan; Hui Zhu; Viatcheslav R Akmaev; Zhaoqing Zhou; Elizabeth M Rohlfs; Kerry Flynn; Brant C Hendrickson; Thomas Scholl; Deborah Alexa Sirko-Osadsa; Bernice A Allitto
Journal:  Eur J Hum Genet       Date:  2011-08-03       Impact factor: 4.246

7.  Nusinersen in later-onset spinal muscular atrophy: Long-term results from the phase 1/2 studies.

Authors:  Basil T Darras; Claudia A Chiriboga; Susan T Iannaccone; Kathryn J Swoboda; Jacqueline Montes; Laurence Mignon; Shuting Xia; C Frank Bennett; Kathie M Bishop; Jeremy M Shefner; Allison M Green; Peng Sun; Ishir Bhan; Sarah Gheuens; Eugene Schneider; Wildon Farwell; Darryl C De Vivo
Journal:  Neurology       Date:  2019-04-24       Impact factor: 9.910

Review 8.  A new dimension of health care: systematic review of the uses, benefits, and limitations of social media for health communication.

Authors:  S Anne Moorhead; Diane E Hazlett; Laura Harrison; Jennifer K Carroll; Anthea Irwin; Ciska Hoving
Journal:  J Med Internet Res       Date:  2013-04-23       Impact factor: 5.428

9.  Intrathecal Injections in Children With Spinal Muscular Atrophy: Nusinersen Clinical Trial Experience.

Authors:  Manon Haché; Kathryn J Swoboda; Navil Sethna; Alan Farrow-Gillespie; Alexander Khandji; Shuting Xia; Kathie M Bishop
Journal:  J Child Neurol       Date:  2016-01-27       Impact factor: 1.987

Review 10.  Social media use in healthcare: A systematic review of effects on patients and on their relationship with healthcare professionals.

Authors:  Edin Smailhodzic; Wyanda Hooijsma; Albert Boonstra; David J Langley
Journal:  BMC Health Serv Res       Date:  2016-08-26       Impact factor: 2.655

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  3 in total

1.  Factors affecting pathways to care for children and adolescents with complex vascular malformations: parental perspectives.

Authors:  Bryan A Sisk; Anna Kerr; Katherine A King
Journal:  Orphanet J Rare Dis       Date:  2022-07-15       Impact factor: 4.303

Review 2.  Mini-Review: Genetic Literacy and Engagement With Genetic Testing for Autism Spectrum Disorder.

Authors:  India D Little; Chris Gunter
Journal:  Front Genet       Date:  2021-06-29       Impact factor: 4.599

3.  Opportunities and pitfalls of social media research in rare genetic diseases: a systematic review.

Authors:  Emily G Miller; Amanda L Woodward; Grace Flinchum; Jennifer L Young; Holly K Tabor; Meghan C Halley
Journal:  Genet Med       Date:  2021-07-19       Impact factor: 8.864

  3 in total

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