Literature DB >> 28192393

Nusinersen, an antisense oligonucleotide drug for spinal muscular atrophy.

David R Corey1.   

Abstract

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Year:  2017        PMID： 28192393     DOI： 10.1038/nn.4508

Source DB:  PubMed          Journal:  Nat Neurosci        ISSN： 1097-6256            Impact factor:   24.884


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  81 in total

1.  PEGylation of therapeutic oligonucletides: From linear to highly branched PEG architectures.

Authors:  Xueguang Lu; Ke Zhang
Journal:  Nano Res       Date:  2018-07-06       Impact factor: 8.897

Review 2.  RNA epigenetics and cardiovascular diseases.

Authors:  Lisa E Dorn; Simon Tual-Chalot; Konstantinos Stellos; Federica Accornero
Journal:  J Mol Cell Cardiol       Date:  2019-03-14       Impact factor: 5.000

Review 3.  Nusinersen: The First Option Beyond Supportive Care for Spinal Muscular Atrophy.

Authors:  Vikas Maharshi; Shazia Hasan
Journal:  Clin Drug Investig       Date:  2017-09       Impact factor: 2.859

4.  Progress towards drug discovery for Friedreich's Ataxia: Identifying synthetic oligonucleotides that more potently activate expression of human frataxin protein.

Authors:  Xiulong Shen; Johnathan Wong; Thahza P Prakash; Frank Rigo; Yanjie Li; Marek Napierala; David R Corey
Journal:  Bioorg Med Chem       Date:  2020-04-05       Impact factor: 3.641

Review 5.  Gene Editing and Gene-Based Therapeutics for Cardiomyopathies.

Authors:  Joyce C Ohiri; Elizabeth M McNally
Journal:  Heart Fail Clin       Date:  2018-04       Impact factor: 3.179

6.  Effects of Astroglia on Motor Neurons in Spinal Muscular Atrophy.

Authors:  Bert M Verheijen
Journal:  J Neurosci       Date:  2017-09-06       Impact factor: 6.167

Review 7.  Drug development in the era of precision medicine.

Authors:  Sarah A Dugger; Adam Platt; David B Goldstein
Journal:  Nat Rev Drug Discov       Date:  2017-12-08       Impact factor: 84.694

Review 8.  Lysosomal storage diseases.

Authors:  Frances M Platt; Alessandra d'Azzo; Beverly L Davidson; Elizabeth F Neufeld; Cynthia J Tifft
Journal:  Nat Rev Dis Primers       Date:  2018-10-01       Impact factor: 52.329

9.  Next generation miRNA inhibition using short anti-seed PNAs encapsulated in PLGA nanoparticles.

Authors:  Shipra Malik; Jihoon Lim; Frank J Slack; Demetrios T Braddock; Raman Bahal
Journal:  J Control Release       Date:  2020-08-21       Impact factor: 9.776

Review 10.  MicroRNA-induced silencing in epilepsy: Opportunities and challenges for clinical application.

Authors:  Durgesh Tiwari; Katrina Peariso; Christina Gross
Journal:  Dev Dyn       Date:  2017-10-04       Impact factor: 3.780
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