Literature DB >> 32564147

Real-world data for pediatric medulloblastoma: can we improve outcomes?

Paula Sedano1, Carmen González-San Segundo1, Lourdes De Ingunza1, Pedro Cuesta-Álvaro2, Marta Pérez-Somarriba3, Francisco Diaz-Gutiérrez1, Carmen Garrido Colino4, Alvaro Lassaletta5.   

Abstract

Medulloblastoma (MB) is a malignant embryonal tumor that develops especially in childhood, with overall survival (OS) at 5 years of up to 70%. The objective of this study is to analyze treatment delivery variables in a retrospective cohort and evaluate the impact of these treatment quality parameters on survival. From 2000 to 2018, 40 pediatric patients with medulloblastoma, treated according to current international protocols, were retrospectively analyzed. Treatment delivery quality indicators were analyzed including the extent of surgery, radiotherapy (RT) parameters, and chemotherapy variables, related with time and dose-intensity deviations. With a median follow-up of 74 months (range, 6-195), OS at 5 years was 74 ± 7%, 81 ± 8% for standard-risk, and 55 ± 16% for high-risk patients (p = 0.090). Disease-free survival at 5 years was not significantly affected by extent of surgery (p = 0.428) and RT-related variables such as surgery-RT interval (p = 0.776) neither RT duration (p = 0.172) or maintenance chemotherapy compliance (p = 0.634). Multivariate analysis identified risk groups predictive of worse DFS (p = 0.032) and leptomeningeal dissemination associated with inferior OS (p = 0.029).
Conclusion: Treatment delivery optimization has improved survival rates of patients with MB. Despite this, in our study, we have not established a clear influence of the considered radiotherapy and chemotherapy treatment quality parameters on outcomes. What is Known: • Improvement in treatment modalities during the last decades has reached a 5-year OS of up to 70% in these patients. • Extent of resection and radiotherapy parameters such as interval between surgery-radiotherapy and radiotherapy duration has been described as probable survival prognostic factors. What is New: • Differences in medulloblastoma survival rates between prospective studies and retrospective series. • The impact on survival of the three main treatment variables, surgery, radiotherapy and chemotherapy, susceptible to improvement.

Entities:  

Keywords:  Children; Medulloblastoma; Radiotherapy; Surgery; Survival; Treatment quality

Mesh:

Year:  2020        PMID: 32564147     DOI: 10.1007/s00431-020-03722-4

Source DB:  PubMed          Journal:  Eur J Pediatr        ISSN: 0340-6199            Impact factor:   3.183


  2 in total

1.  Children treated for medulloblastoma and supratentorial primitive neuroectodermal tumor in Norway from 1974 through 2013: Unexplainable regional differences in survival.

Authors:  Einar Stensvold; Tor Åge Myklebust; Johan Cappelen; Bernt J Due-Tønnessen; Paulina Due-Tønnessen; Aleksandra Kepka; Tom Børge Johannesen; Bård Krossnes; Tryggve Lundar; Snezana Maric; Hrvoje Miletic; Viggo Moholdt; Kristin Smistad Myrmel; Terje Nordberg; Jana Rydland; Tore Stokland; Kristin Solem; Ole Solheim; Ingrid Torsvik; Gry C Wikran; Bernward Zeller; Finn Wesenberg; Anne Grete Bechensteen; Petter Brandal
Journal:  Pediatr Blood Cancer       Date:  2019-07-01       Impact factor: 3.167

2.  Medulloblastoma: time-dose relationship based on a 30-year review.

Authors:  J O del Charco; T W Bolek; W M McCollough; B L Maria; A Kedar; R C Braylan; J P Mickle; J M Buatti; N P Mendenhall; R B Marcus
Journal:  Int J Radiat Oncol Biol Phys       Date:  1998-08-01       Impact factor: 7.038

  2 in total
  3 in total

1.  High expression of Toll-like receptor 7 is a survival factor in pediatric medulloblastoma.

Authors:  Lourdes Alvarez-Arellano; Pilar Eguía-Aguilar; Patricia Piña-Sánchez; Nadia González-García; Alam Palma-Guzman; Mario Perezpeña-Diazconti; Carmen Maldonado-Bernal
Journal:  Childs Nerv Syst       Date:  2021-09-04       Impact factor: 1.475

2.  TOP2A correlates with poor prognosis and affects radioresistance of medulloblastoma.

Authors:  Yufeng Zhang; Haiyan Yang; Liwen Wang; Huandi Zhou; Ge Zhang; Zhiqing Xiao; Xiaoying Xue
Journal:  Front Oncol       Date:  2022-07-15       Impact factor: 5.738

3.  RBM5-AS1 promotes radioresistance in medulloblastoma through stabilization of SIRT6 protein.

Authors:  Chuanying Zhu; Keke Li; Mawei Jiang; Siyu Chen
Journal:  Acta Neuropathol Commun       Date:  2021-07-05       Impact factor: 7.801

  3 in total

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