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Literature DB >> 32165573

Treating sickle cell anemia.

John F Tisdale¹, Swee Lay Thein², William A Eaton³.

Abstract

Entities: Chemical Disease Gene Species

Mesh：

Substances：

Year: 2020 PMID： 32165573 PMCID： PMC7299198 DOI： 10.1126/science.aba3827

Source DB: PubMed Journal: Science ISSN： 0036-8075 Impact factor: 47.728

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14 in total

1. Linus Pauling and sickle cell disease.

Authors: William A Eaton
Journal: Biophys Chem Date: 2003 Impact factor: 2.352

Review 2. Treating sickle cell disease by targeting HbS polymerization.

Authors: William A Eaton; H Franklin Bunn
Journal: Blood Date: 2017-04-06 Impact factor: 22.113

Review 3. Lentiviral and genome-editing strategies for the treatment of β-hemoglobinopathies.

Authors: Elisa Magrin; Annarita Miccio; Marina Cavazzana
Journal: Blood Date: 2019-10-10 Impact factor: 22.113

4. Gene Therapy in a Patient with Sickle Cell Disease.

Authors: Jean-Antoine Ribeil; Salima Hacein-Bey-Abina; Emmanuel Payen; Alessandra Magnani; Michaela Semeraro; Elisa Magrin; Laure Caccavelli; Benedicte Neven; Philippe Bourget; Wassim El Nemer; Pablo Bartolucci; Leslie Weber; Hervé Puy; Jean-François Meritet; David Grevent; Yves Beuzard; Stany Chrétien; Thibaud Lefebvre; Robert W Ross; Olivier Negre; Gabor Veres; Laura Sandler; Sandeep Soni; Mariane de Montalembert; Stéphane Blanche; Philippe Leboulch; Marina Cavazzana
Journal: N Engl J Med Date: 2017-03-02 Impact factor: 91.245

5. Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin.

Authors: C May; S Rivella; J Callegari; G Heller; K M Gaensler; L Luzzatto; M Sadelain
Journal: Nature Date: 2000-07-06 Impact factor: 49.962

Review 6. Emerging Genetic Therapy for Sickle Cell Disease.

Authors: Stuart H Orkin; Daniel E Bauer
Journal: Annu Rev Med Date: 2018-10-24 Impact factor: 13.739

Review 7. Recent progress in understanding and manipulating haemoglobin switching for the haemoglobinopathies.

Authors: Divya S Vinjamur; Daniel E Bauer; Stuart H Orkin
Journal: Br J Haematol Date: 2017-11-28 Impact factor: 6.998

8. Crizanlizumab for the Prevention of Pain Crises in Sickle Cell Disease.

Authors: Kenneth I Ataga; Abdullah Kutlar; Julie Kanter; Darla Liles; Rodolfo Cancado; João Friedrisch; Troy H Guthrie; Jennifer Knight-Madden; Ofelia A Alvarez; Victor R Gordeuk; Sandra Gualandro; Marina P Colella; Wally R Smith; Scott A Rollins; Jonathan W Stocker; Russell P Rother
Journal: N Engl J Med Date: 2016-12-03 Impact factor: 91.245

9. Hydroxyurea enhances fetal hemoglobin production in sickle cell anemia.

Authors: O S Platt; S H Orkin; G Dover; G P Beardsley; B Miller; D G Nathan
Journal: J Clin Invest Date: 1984-08 Impact factor: 14.808

10. CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells.

Authors: Daniel P Dever; Rasmus O Bak; Andreas Reinisch; Joab Camarena; Gabriel Washington; Carmencita E Nicolas; Mara Pavel-Dinu; Nivi Saxena; Alec B Wilkens; Sruthi Mantri; Nobuko Uchida; Ayal Hendel; Anupama Narla; Ravindra Majeti; Kenneth I Weinberg; Matthew H Porteus
Journal: Nature Date: 2016-11-07 Impact factor: 49.962

11 in total

1. Curative vs targeted therapy for SCD: does it make more sense to address the root cause than target downstream events?

Authors: Marilyn J Telen
Journal: Blood Adv Date: 2020-07-28

2. Collaborative science to advance gene therapies in resource-limited parts of the world.

Authors: Joseph M McCune; Susan C Stevenson; Brian P Doehle; Cameron C Trenor; Emily H Turner; Jonathan M Spector
Journal: Mol Ther Date: 2021-08-30 Impact factor: 11.454

Review 3. Development and clinical translation of ex vivo gene therapy.

Authors: Xiaomo Wu; Xiaorong He; Fahui Liu; Xiaochang Jiang; Ping Wang; Jinyan Zhang; Ju Jiang
Journal: Comput Struct Biotechnol J Date: 2022-06-11 Impact factor: 6.155

4. A unified model of human hemoglobin switching through single-cell genome editing.

Authors: Yong Shen; Jeffrey M Verboon; Yuannyu Zhang; Nan Liu; Yoon Jung Kim; Samantha Marglous; Satish K Nandakumar; Richard A Voit; Claudia Fiorini; Ayesha Ejaz; Anindita Basak; Stuart H Orkin; Jian Xu; Vijay G Sankaran
Journal: Nat Commun Date: 2021-08-17 Impact factor: 17.694

5. Feature tracking microfluidic analysis reveals differential roles of viscosity and friction in sickle cell blood.

Authors: Hannah M Szafraniec; José M Valdez; Elizabeth Iffrig; Wilbur A Lam; John M Higgins; Philip Pearce; David K Wood
Journal: Lab Chip Date: 2022-04-12 Impact factor: 6.799

Review 6. Health-Related Quality of Life and Adherence to Hydroxyurea and Other Disease-Modifying Therapies among Individuals with Sickle Cell Disease: A Systematic Review.

Authors: Mira Yang; Lena Elmuti; Sherif M Badawy
Journal: Biomed Res Int Date: 2022-07-18 Impact factor: 3.246