Literature DB >> 31712809

Clinical Outcomes Among Patients With Drug-resistant Tuberculosis Receiving Bedaquiline- or Delamanid-Containing Regimens.

R R Kempker1, L Mikiashvili2, Y Zhao3, D Benkeser3, K Barbakadze2, N Bablishvili2, Z Avaliani2, C A Peloquin4, H M Blumberg1,5, M Kipiani2.   

Abstract

BACKGROUND: Bedaquiline and delamanid are newly available drugs for treating multidrug-resistant tuberculosis (MDR-TB); however, there are limited data guiding their use and no comparison studies.
METHODS: We conducted a prospective, observational study among patients with MDR-TB in Georgia who were receiving a bedaquiline- or delamanid-based treatment regimen. Monthly sputum cultures, minimal inhibitory concentration testing, and adverse event monitoring were performed. Primary outcomes were culture conversion rates and clinical outcomes. Targeted maximum likelihood estimation and super learning were utilized to produce a covariate-adjusted proportion of outcomes for each regimen.
RESULTS: Among 156 patients with MDR-TB, 100 were enrolled and 95 were receiving a bedaquiline-based (n = 64) or delamanid-based (n = 31) regimen. Most were male (82%) and the median age was 38 years. Rates of previous treatment (56%) and cavitary disease (61%) were high. The most common companion drugs included linezolid, clofazimine, cycloserine, and a fluoroquinolone. The median numbers of effective drugs received among patients on bedaquiline-based (4; interquartile range [IQR], 4-4) and delamanid-based (4; IQR, 3.5-5) regimens were similar. Rates of acquired drug resistance were significantly higher among patients receiving delamanid versus bedaquiline (36% vs 10%, respectively; P < .01). Adjusted rates of sputum culture conversion at 2 months (67% vs 47%, respectively; P = .10) and 6 months (95% vs 74%, respectively; P < .01), as well as more favorable clinical outcomes (96% vs 72%, respectively; P < .01), were higher among patients receiving bedaquiline versus delamanid.
CONCLUSIONS: Among patients with MDR-TB, bedaquiline-based regimens were associated with higher rates of sputum culture conversion, more favorable outcomes, and a lower rate of acquired drug resistance versus delamanid-based regimens.
© The Author(s) 2019. Published by Oxford University Press for the Infectious Diseases Society of America. All rights reserved. For permissions, e-mail: journals.permissions@oup.com.

Entities:  

Keywords:  bedaquiline; culture conversion; delamanid; multidrug-resistant; tuberculosis

Year:  2020        PMID: 31712809      PMCID: PMC7713674          DOI: 10.1093/cid/ciz1107

Source DB:  PubMed          Journal:  Clin Infect Dis        ISSN: 1058-4838            Impact factor:   9.079


  21 in total

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Authors:  Nafees Ahmad; Shama D Ahuja; Onno W Akkerman; Jan-Willem C Alffenaar; Laura F Anderson; Parvaneh Baghaei; Didi Bang; Pennan M Barry; Mayara L Bastos; Digamber Behera; Andrea Benedetti; Gregory P Bisson; Martin J Boeree; Maryline Bonnet; Sarah K Brode; James C M Brust; Ying Cai; Eric Caumes; J Peter Cegielski; Rosella Centis; Pei-Chun Chan; Edward D Chan; Kwok-Chiu Chang; Macarthur Charles; Andra Cirule; Margareth Pretti Dalcolmo; Lia D'Ambrosio; Gerard de Vries; Keertan Dheda; Aliasgar Esmail; Jennifer Flood; Gregory J Fox; Mathilde Fréchet-Jachym; Geisa Fregona; Regina Gayoso; Medea Gegia; Maria Tarcela Gler; Sue Gu; Lorenzo Guglielmetti; Timothy H Holtz; Jennifer Hughes; Petros Isaakidis; Leah Jarlsberg; Russell R Kempker; Salmaan Keshavjee; Faiz Ahmad Khan; Maia Kipiani; Serena P Koenig; Won-Jung Koh; Afranio Kritski; Liga Kuksa; Charlotte L Kvasnovsky; Nakwon Kwak; Zhiyi Lan; Christoph Lange; Rafael Laniado-Laborín; Myungsun Lee; Vaira Leimane; Chi-Chiu Leung; Eric Chung-Ching Leung; Pei Zhi Li; Phil Lowenthal; Ethel L Maciel; Suzanne M Marks; Sundari Mase; Lawrence Mbuagbaw; Giovanni B Migliori; Vladimir Milanov; Ann C Miller; Carole D Mitnick; Chawangwa Modongo; Erika Mohr; Ignacio Monedero; Payam Nahid; Norbert Ndjeka; Max R O'Donnell; Nesri Padayatchi; Domingo Palmero; Jean William Pape; Laura J Podewils; Ian Reynolds; Vija Riekstina; Jérôme Robert; Maria Rodriguez; Barbara Seaworth; Kwonjune J Seung; Kathryn Schnippel; Tae Sun Shim; Rupak Singla; Sarah E Smith; Giovanni Sotgiu; Ganzaya Sukhbaatar; Payam Tabarsi; Simon Tiberi; Anete Trajman; Lisa Trieu; Zarir F Udwadia; Tjip S van der Werf; Nicolas Veziris; Piret Viiklepp; Stalz Charles Vilbrun; Kathleen Walsh; Janice Westenhouse; Wing-Wai Yew; Jae-Joon Yim; Nicola M Zetola; Matteo Zignol; Dick Menzies
Journal:  Lancet       Date:  2018-09-08       Impact factor: 79.321

2.  Bedaquiline Resistance: Its Emergence, Mechanism, and Prevention.

Authors:  Thi Van Anh Nguyen; Richard M Anthony; Anne-Laure Bañuls; Thi Van Anh Nguyen; Dinh Hoa Vu; Jan-Willem C Alffenaar
Journal:  Clin Infect Dis       Date:  2018-05-02       Impact factor: 9.079

3.  Final treatment outcomes of multidrug- and extensively drug-resistant tuberculosis patients in Latvia receiving delamanid-containing regimens.

Authors:  Liga Kuksa; Linda Barkane; Norbert Hittel; Rajesh Gupta
Journal:  Eur Respir J       Date:  2017-11-09       Impact factor: 16.671

4.  Doubly robust nonparametric inference on the average treatment effect.

Authors:  D Benkeser; M Carone; M J Van Der Laan; P B Gilbert
Journal:  Biometrika       Date:  2017-10-16       Impact factor: 2.445

5.  Global programmatic use of bedaquiline and delamanid for the treatment of multidrug-resistant tuberculosis.

Authors:  V Cox; G Brigden; R H Crespo; E Lessem; S Lynch; M L Rich; B Waning; J Furin
Journal:  Int J Tuberc Lung Dis       Date:  2018-04-01       Impact factor: 2.373

6.  Examples of bedaquiline introduction for the management of multidrug-resistant tuberculosis in five countries.

Authors:  L Guglielmetti; C Hewison; Z Avaliani; J Hughes; N Kiria; N Lomtadze; N Ndjeka; S Setkina; A Shabangu; W Sikhondze; A Skrahina; N Veziris; J Furin
Journal:  Int J Tuberc Lung Dis       Date:  2017-02-01       Impact factor: 2.373

7.  Delamanid for multidrug-resistant pulmonary tuberculosis.

Authors:  Maria Tarcela Gler; Vija Skripconoka; Epifanio Sanchez-Garavito; Heping Xiao; Jose L Cabrera-Rivero; Dante E Vargas-Vasquez; Mengqiu Gao; Mohamed Awad; Seung-Kyu Park; Tae Sun Shim; Gee Young Suh; Manfred Danilovits; Hideo Ogata; Anu Kurve; Joon Chang; Katsuhiro Suzuki; Thelma Tupasi; Won-Jung Koh; Barbara Seaworth; Lawrence J Geiter; Charles D Wells
Journal:  N Engl J Med       Date:  2012-06-07       Impact factor: 91.245

8.  MIC of Delamanid (OPC-67683) against Mycobacterium tuberculosis Clinical Isolates and a Proposed Critical Concentration.

Authors:  Kelly Stinson; Natalia Kurepina; Amour Venter; Mamoru Fujiwara; Masanori Kawasaki; Juliano Timm; Elena Shashkina; Barry N Kreiswirth; Yongge Liu; Makoto Matsumoto; Lawrence Geiter
Journal:  Antimicrob Agents Chemother       Date:  2016-05-23       Impact factor: 5.191

9.  Sensititre MYCOTB MIC plate for testing Mycobacterium tuberculosis susceptibility to first- and second-line drugs.

Authors:  Jongseok Lee; Derek T Armstrong; Willy Ssengooba; Jeong-Ae Park; Yeuni Yu; Francis Mumbowa; Carolyn Namaganda; Gerald Mboowa; Germine Nakayita; Sandra Armakovitch; Gina Chien; Sang-Nae Cho; Laura E Via; Clifton E Barry; Jerrold J Ellner; David Alland; Susan E Dorman; Moses L Joloba
Journal:  Antimicrob Agents Chemother       Date:  2013-10-07       Impact factor: 5.191

10.  pncA Gene Mutations Associated with Pyrazinamide Resistance in Drug-Resistant Tuberculosis, South Africa and Georgia.

Authors:  Salim Allana; Elena Shashkina; Barun Mathema; Nino Bablishvili; Nestani Tukvadze; N Sarita Shah; Russell R Kempker; Henry M Blumberg; Pravi Moodley; Koleka Mlisana; James C M Brust; Neel R Gandhi
Journal:  Emerg Infect Dis       Date:  2017-03       Impact factor: 6.883

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  12 in total

1.  Linezolid Exposure Is Associated with Cytopenias in Patients Treated for Multidrug-Resistant Tuberculosis.

Authors:  Daniel S Graciaa; Maia Kipiani; Matthew J Magee; Lali Mikiashvili; Ketevan Barbakadze; Nino Bablishvili; Sara C Auld; Wael A Alghamdi; Mohammad H Alshaer; Charles A Peloquin; Zaza Avaliani; Henry M Blumberg; Russell R Kempker
Journal:  Antimicrob Agents Chemother       Date:  2022-08-02       Impact factor: 5.938

2.  Long term outcomes of patients with tuberculous meningitis: The impact of drug resistance.

Authors:  Emily E Evans; Teona Avaliani; Mariam Gujabidze; Tinatin Bakuradze; Maia Kipiani; Shorena Sabanadze; Alison G C Smith; Zaza Avaliani; Jeffrey M Collins; Russell R Kempker
Journal:  PLoS One       Date:  2022-06-24       Impact factor: 3.752

3.  Cycloserine and Linezolid for Tuberculosis Meningitis: Pharmacokinetic Evidence of Potential Usefulness.

Authors:  Russell R Kempker; Alison G C Smith; Teona Avaliani; Mariam Gujabidze; Tinatin Bakuradze; Shorena Sabanadze; Zaza Avaliani; Jeffrey M Collins; Henry M Blumberg; Mohammad H Alshaer; Charles A Peloquin; Maia Kipiani
Journal:  Clin Infect Dis       Date:  2022-09-10       Impact factor: 20.999

4.  Bedaquiline-containing regimens and multidrug-resistant tuberculosis: a systematic review and meta-analysis.

Authors:  Hossein Hatami; Giovanni Sotgiu; Narjess Bostanghadiri; Sahel Shafiee Dolat Abadi; Bita Mesgarpour; Hossein Goudarzi; Giovanni Battista Migliori; Mohammad Javad Nasiri
Journal:  J Bras Pneumol       Date:  2022-05-30       Impact factor: 2.800

5.  Population Pharmacokinetics of Linezolid in Tuberculosis Patients: Dosing Regimen Simulation and Target Attainment Analysis.

Authors:  Wael A Alghamdi; Mohammad H Al-Shaer; Guohua An; Abdullah Alsultan; Maia Kipiani; Ketevan Barbakadze; Lali Mikiashvili; David Ashkin; David E Griffith; J Peter Cegielski; Russell R Kempker; Charles A Peloquin
Journal:  Antimicrob Agents Chemother       Date:  2020-09-21       Impact factor: 5.191

6.  Treatment Outcomes Among Pediatric Patients With Highly Drug-Resistant Tuberculosis: The Role of New and Repurposed Second-Line Tuberculosis Drugs.

Authors:  Tea Madzgharashvili; Argita D Salindri; Matthew J Magee; Nestani Tukvadze; Zaza Avaliani; Henry M Blumberg; Russell R Kempker; Nino Lomtadze
Journal:  J Pediatric Infect Dis Soc       Date:  2021-04-30       Impact factor: 3.164

7.  Pharmacokinetics of bedaquiline, delamanid and clofazimine in patients with multidrug-resistant tuberculosis.

Authors:  Wael A Alghamdi; Mohammad H Al-Shaer; Maia Kipiani; Ketevan Barbakadze; Lali Mikiashvili; Russell R Kempker; Charles A Peloquin
Journal:  J Antimicrob Chemother       Date:  2021-03-12       Impact factor: 5.790

8.  Treatment Outcomes of Patients with Multidrug-Resistant Tuberculosis: Concern to Bedaquiline: Authors' Reply.

Authors:  Yewon Kang; Jeongha Mok
Journal:  Tuberc Respir Dis (Seoul)       Date:  2021-09-13

9.  Effectiveness and Cardiac Safety of Bedaquiline-Based Therapy for Drug-Resistant Tuberculosis: A Prospective Cohort Study.

Authors:  James C M Brust; Neel R Gandhi; Sean Wasserman; Gary Maartens; Shaheed V Omar; Nazir A Ismail; Angela Campbell; Lindsay Joseph; Alexandria Hahn; Salim Allana; Alfonso C Hernandez-Romieu; Chenshu Zhang; Koleka Mlisana; Charle A Viljoen; Benjamin Zalta; Ismaeel Ebrahim; Meghan Franczek; Iqbal Master; Limpho Ramangoaela; Julian Te Riele; Graeme Meintjes
Journal:  Clin Infect Dis       Date:  2021-12-06       Impact factor: 9.079

10.  Long-Term Mortality and Active Tuberculosis Disease Among Patients Who Were Lost to Follow-Up During Second-Line Tuberculosis Treatment in 2011-2014: Population-Based Study in the Country of Georgia.

Authors:  Giorgi Kuchukhidze; Davit Baliashvili; Natalia Adamashvili; Ana Kasradze; Russell R Kempker; Matthew J Magee
Journal:  Open Forum Infect Dis       Date:  2021-03-15       Impact factor: 3.835

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