Literature DB >> 31706131

Myoclonus-dystonia: Distinctive motor and non-motor phenotype from other dystonia syndromes.

Elze R Timmers1, Marenka Smit2, Anouk Kuiper3, Anna L Bartels4, Sterre van der Veen5, A M Madelein van der Stouwe6, Patrick Santens7, Bruno Bergmans8, Marina A J Tijssen9.   

Abstract

BACKGROUND: Myoclonus-dystonia (M-D) due to a pathogenic variant of SGCE is an autosomal dominant inherited movement disorder. Apart from motor symptoms, psychiatric disorders are highly prevalent in patients with M-D. Previous studies suggest, but never tested directly, that the type of psychiatric disorder differs between dystonia syndromes, probably related to disease specific pathology. Little is known about other non-motor symptoms (NMS) in M-D. Here, we systematically study NMS in M-D in direct comparison to other types of dystonia and healthy controls.
METHODS: Standardized questionnaires were used to assess type and severity of psychiatric co-morbidity, sleep problems, fatigue and quality of life. Results of M-D patients with a pathogenic variant of SGCE were compared to results of idiopathic cervical dystonia (CD) patients, dopa-responsive dystonia (DRD) patients with a pathogenic variant of GCH1 and controls.
RESULTS: We included 164 participants: 41 M-D, 51 CD, 19 DRD patients, 53 controls. Dystonia patients (M-D, CD and DRD) had an increased prevalence of psychiatric disorders compared to controls (56-74% vs. 29%). In M-D we found a significantly increased prevalence of obsessive-compulsive disorder (OCD) and psychosis compared to CD and DRD. All dystonia patients had more sleep problems (49-68% vs. 36%) and fatigue (42-73% vs. 15%) than controls. Compared to other dystonia subtypes, M-D patients reported less excessive daytime sleepiness and fatigue.
CONCLUSION: Psychiatric comorbidity is frequent in all dystonia types, but OCD and psychosis are more common in M-D patients. Further research is necessary to elucidate underlying pathways.
Copyright © 2019 Elsevier Ltd. All rights reserved.

Entities:  

Keywords:  Cervical dystonia; Dopa-responsive dystonia; Myoclonus-dystonia; Non-motor symptoms; Quality of life

Year:  2019        PMID: 31706131     DOI: 10.1016/j.parkreldis.2019.10.015

Source DB:  PubMed          Journal:  Parkinsonism Relat Disord        ISSN: 1353-8020            Impact factor:   4.891


  5 in total

Review 1.  ε-Sarcoglycan: Unraveling the Myoclonus-Dystonia Gene.

Authors:  Ana Cazurro-Gutiérrez; Anna Marcé-Grau; Marta Correa-Vela; Ainara Salazar; María I Vanegas; Alfons Macaya; Àlex Bayés; Belén Pérez-Dueñas
Journal:  Mol Neurobiol       Date:  2021-04-22       Impact factor: 5.590

Review 2.  Dystonia updates: definition, nomenclature, clinical classification, and etiology.

Authors:  Karen Grütz; Christine Klein
Journal:  J Neural Transm (Vienna)       Date:  2021-02-19       Impact factor: 3.575

3.  A mixed-ethnicity myoclonus-dystonia patient with a novel SGCE nonsense mutation: a case report.

Authors:  Meliza Angelica J de Leon; Raymond L Rosales; Christine Klein; Ana Westenberger
Journal:  BMC Neurol       Date:  2022-01-05       Impact factor: 2.474

4.  Delayed Diagnoses of SGCE Myoclonus-Dystonia.

Authors:  M Georgeta Varga; Nikita P Nand; Mark S LeDoux
Journal:  Tremor Other Hyperkinet Mov (N Y)       Date:  2020-07-28

5.  Population Prevalence of Deleterious SGCE Variants.

Authors:  Mark S LeDoux
Journal:  Tremor Other Hyperkinet Mov (N Y)       Date:  2020-11-04
  5 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.