Literature DB >> 31537456

AAV6 Is Superior to Clade F AAVs in Stimulating Homologous Recombination-Based Genome Editing in Human HSPCs.

Amanda M Dudek1, Matthew H Porteus2.   

Abstract

Entities:  

Year:  2019        PMID: 31537456      PMCID: PMC6822226          DOI: 10.1016/j.ymthe.2019.09.005

Source DB:  PubMed          Journal:  Mol Ther        ISSN: 1525-0016            Impact factor:   11.454


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  39 in total

1.  Targeting DNA double-strand breaks with TAL effector nucleases.

Authors:  Michelle Christian; Tomas Cermak; Erin L Doyle; Clarice Schmidt; Feng Zhang; Aaron Hummel; Adam J Bogdanove; Daniel F Voytas
Journal:  Genetics       Date:  2010-07-26       Impact factor: 4.562

2.  Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus.

Authors:  X Xiao; J Li; R J Samulski
Journal:  J Virol       Date:  1998-03       Impact factor: 5.103

Review 3.  Gene targeting using zinc finger nucleases.

Authors:  Matthew H Porteus; Dana Carroll
Journal:  Nat Biotechnol       Date:  2005-08       Impact factor: 54.908

4.  Identification of liver-specific enhancer-promoter activity in the 3' untranslated region of the wild-type AAV2 genome.

Authors:  Grant J Logan; Allison P Dane; Claus V Hallwirth; Christine M Smyth; Emilie E Wilkie; Anais K Amaya; Erhua Zhu; Neeta Khandekar; Samantha L Ginn; Sophia H Y Liao; Sharon C Cunningham; Natsuki Sasaki; Martí Cabanes-Creus; Patrick P L Tam; David W Russell; Leszek Lisowski; Ian E Alexander
Journal:  Nat Genet       Date:  2017-06-19       Impact factor: 38.330

5.  A TALE nuclease architecture for efficient genome editing.

Authors:  Jeffrey C Miller; Siyuan Tan; Guijuan Qiao; Kyle A Barlow; Jianbin Wang; Danny F Xia; Xiangdong Meng; David E Paschon; Elo Leung; Sarah J Hinkley; Gladys P Dulay; Kevin L Hua; Irina Ankoudinova; Gregory J Cost; Fyodor D Urnov; H Steve Zhang; Michael C Holmes; Lei Zhang; Philip D Gregory; Edward J Rebar
Journal:  Nat Biotechnol       Date:  2010-12-22       Impact factor: 54.908

6.  CRISPR-Mediated Integration of Large Gene Cassettes Using AAV Donor Vectors.

Authors:  Rasmus O Bak; Matthew H Porteus
Journal:  Cell Rep       Date:  2017-07-18       Impact factor: 9.423

7.  Large-scale analysis of adeno-associated virus vector integration sites in normal human cells.

Authors:  Daniel G Miller; Grant D Trobridge; Lisa M Petek; Michael A Jacobs; Rajinder Kaul; David W Russell
Journal:  J Virol       Date:  2005-09       Impact factor: 5.103

8.  Optimization of Recombinant Adeno-Associated Virus-Mediated Expression for Large Transgenes, Using a Synthetic Promoter and Tandem Array Enhancers.

Authors:  Ziying Yan; Xingshen Sun; Zehua Feng; Guiying Li; John T Fisher; Zoe A Stewart; John F Engelhardt
Journal:  Hum Gene Ther       Date:  2015-04-20       Impact factor: 5.695

9.  Promoterless gene targeting without nucleases ameliorates haemophilia B in mice.

Authors:  A Barzel; N K Paulk; Y Shi; Y Huang; K Chu; F Zhang; P N Valdmanis; L P Spector; M H Porteus; K M Gaensler; M A Kay
Journal:  Nature       Date:  2014-10-29       Impact factor: 49.962

10.  Priming Human Repopulating Hematopoietic Stem and Progenitor Cells for Cas9/sgRNA Gene Targeting.

Authors:  Carsten T Charlesworth; Joab Camarena; M Kyle Cromer; Sriram Vaidyanathan; Rasmus O Bak; Jason M Carte; Jason Potter; Daniel P Dever; Matthew H Porteus
Journal:  Mol Ther Nucleic Acids       Date:  2018-05-03       Impact factor: 8.886

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  9 in total

1.  Reply to "Efficient Nuclease-free HR by Clade F AAV Requires High MOIs with High Quality Vectors".

Authors:  Geoffrey L Rogers; Hsu-Yu Chen; Heidy Morales; Paula M Cannon
Journal:  Mol Ther       Date:  2019-11-11       Impact factor: 11.454

2.  Reply to "Efficient Nuclease-free HR by Clade F AAV Requires High MOIs with High Quality Vectors".

Authors:  Amanda M Dudek; Matthew H Porteus
Journal:  Mol Ther       Date:  2019-11-11       Impact factor: 11.454

3.  Efficient Nuclease-free HR by Clade F AAV Requires High MOIs with High Quality Vectors.

Authors:  Saswati Chatterjee
Journal:  Mol Ther       Date:  2019-11-11       Impact factor: 11.454

4.  Adeno-Associated Virus and Hematopoietic Stem Cells: The Potential of Adeno-Associated Virus Hematopoietic Stem Cells in Genetic Medicines.

Authors:  Saswati Chatterjee; Venkatesh Sivanandam; Kamehameha Kai-Min Wong
Journal:  Hum Gene Ther       Date:  2020-05       Impact factor: 5.695

Review 5.  Understanding and overcoming adverse consequences of genome editing on hematopoietic stem and progenitor cells.

Authors:  Byung-Chul Lee; Richard J Lozano; Cynthia E Dunbar
Journal:  Mol Ther       Date:  2021-09-10       Impact factor: 11.454

6.  Enhanced Transduction of Human Hematopoietic Stem Cells by AAV6 Vectors: Implications in Gene Therapy and Genome Editing.

Authors:  Hua Yang; Keyun Qing; Geoffrey D Keeler; Ling Yin; Mario Mietzsch; Chen Ling; Brad E Hoffman; Mavis Agbandje-McKenna; Mengqun Tan; Wei Wang; Arun Srivastava
Journal:  Mol Ther Nucleic Acids       Date:  2020-03-29       Impact factor: 8.886

7.  Molecular characterization of precise in vivo targeted gene integration in human cells using AAVHSC15.

Authors:  Huei-Mei Chen; Rachel Resendes; Azita Ghodssi; Danielle Sookiasian; Michael Tian; Serena Dollive; Laura Adamson-Small; Nancy Avila; Cagdas Tazearslan; John F Thompson; Jeff L Ellsworth; Omar Francone; Albert Seymour; Jason B Wright
Journal:  PLoS One       Date:  2020-05-26       Impact factor: 3.240

Review 8.  Optimization of AAV vectors to target persistent viral reservoirs.

Authors:  Rossana Colón-Thillet; Keith R Jerome; Daniel Stone
Journal:  Virol J       Date:  2021-04-23       Impact factor: 5.913

9.  Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease.

Authors:  Annalisa Lattanzi; Joab Camarena; Premanjali Lahiri; Helen Segal; Waracharee Srifa; Christopher A Vakulskas; Richard L Frock; Josefin Kenrick; Ciaran Lee; Narae Talbott; Jason Skowronski; M Kyle Cromer; Carsten T Charlesworth; Rasmus O Bak; Sruthi Mantri; Gang Bao; David DiGiusto; John Tisdale; J Fraser Wright; Neehar Bhatia; Maria Grazia Roncarolo; Daniel P Dever; Matthew H Porteus
Journal:  Sci Transl Med       Date:  2021-06-16       Impact factor: 17.956

  9 in total

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