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Literature DB >> 30855744

A New Class of Medicines through DNA Editing.

Matthew H Porteus¹.

Abstract

Mesh：

Substances：

Year: 2019 PMID： 30855744 DOI： 10.1056/NEJMra1800729

Source DB: PubMed Journal: N Engl J Med ISSN： 0028-4793 Impact factor: 91.245

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Cited

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66 in total

1. Gene therapy for inherited arrhythmias.

Authors: Vassilios J Bezzerides; Maksymilian Prondzynski; Lucie Carrier; William T Pu
Journal: Cardiovasc Res Date: 2020-07-15 Impact factor: 10.787

2. Hijack of CRISPR defences by selfish genes holds clinical promise.

Authors: Fyodor D Urnov
Journal: Nature Date: 2019-07 Impact factor: 49.962

Review 3. Gene therapy using haematopoietic stem and progenitor cells.

Authors: Giuliana Ferrari; Adrian J Thrasher; Alessandro Aiuti
Journal: Nat Rev Genet Date: 2020-12-10 Impact factor: 53.242

4. The technical risks of human gene editing.

Authors: Benjamin Davies
Journal: Hum Reprod Date: 2019-11-01 Impact factor: 6.918

Review 5. [Ex vivo stem cell gene therapy of the skin : Ready for clinical use?]

Authors: Ulrich Koller
Journal: Hautarzt Date: 2020-02 Impact factor: 0.751

Review 6. The Landscape of Early Clinical Gene Therapies outside of Oncology.

Authors: Laure Rittié; Takis Athanasopoulos; Miguel Calero-Garcia; Marie L Davies; David J Dow; Steven J Howe; Alastair Morrison; Ida Ricciardelli; Aurore Saudemont; Laurent Jespers; Timothy M Clay
Journal: Mol Ther Date: 2019-09-06 Impact factor: 11.454

A New Class of Medicines through DNA Editing.

1. Gene therapy for inherited arrhythmias.

2. Hijack of CRISPR defences by selfish genes holds clinical promise.

Review 3. Gene therapy using haematopoietic stem and progenitor cells.

4. The technical risks of human gene editing.

Review 5. [Ex vivo stem cell gene therapy of the skin : Ready for clinical use?]

Review 6. The Landscape of Early Clinical Gene Therapies outside of Oncology.

7. AAV6 Is Superior to Clade F AAVs in Stimulating Homologous Recombination-Based Genome Editing in Human HSPCs.

Review 8. CRISPR-Based Therapeutic Genome Editing: Strategies and In Vivo Delivery by AAV Vectors.

Review 9. CRISPR-Cas9: A Preclinical and Clinical Perspective for the Treatment of Human Diseases.

Review 10. Human inborn errors of immunity: An expanding universe.