Literature DB >> 30846493

T-cell replete haploidentical bone marrow transplantation and post-transplant cyclophosphamide for patients with inborn errors.

Mathias Kurzay1, Fabian Hauck1, Irene Schmid1, Volker Wiebking1, Anna Eichinger1, Eva Jung1, Ann Boekstegers1, Tobias Feuchtinger1, Christoph Klein1, Michael H Albert2.   

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Year:  2019        PMID: 30846493      PMCID: PMC6886426          DOI: 10.3324/haematol.2018.215285

Source DB:  PubMed          Journal:  Haematologica        ISSN: 0390-6078            Impact factor:   9.941


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  14 in total

1.  Single-Center Experience of Unrelated and Haploidentical Stem Cell Transplantation with TCRαβ and CD19 Depletion in Children with Primary Immunodeficiency Syndromes.

Authors:  Dmitry Balashov; Anna Shcherbina; Michael Maschan; Pavel Trakhtman; Yulia Skvortsova; Larisa Shelikhova; Alexandra Laberko; Anna Livshits; Galina Novichkova; Alexei Maschan
Journal:  Biol Blood Marrow Transplant       Date:  2015-07-15       Impact factor: 5.742

2.  HLA-haploidentical stem cell transplantation after removal of αβ+ T and B cells in children with nonmalignant disorders.

Authors:  Alice Bertaina; Pietro Merli; Sergio Rutella; Daria Pagliara; Maria Ester Bernardo; Riccardo Masetti; Daniela Pende; Michela Falco; Rupert Handgretinger; Francesca Moretta; Barbarella Lucarelli; Letizia P Brescia; Giuseppina Li Pira; Manuela Testi; Caterina Cancrini; Nabil Kabbara; Rita Carsetti; Andrea Finocchi; Alessandro Moretta; Lorenzo Moretta; Franco Locatelli
Journal:  Blood       Date:  2014-05-28       Impact factor: 22.113

3.  Reduced toxicity, myeloablative HLA-haploidentical hematopoietic stem cell transplantation with post-transplantation cyclophosphamide for sickle cell disease.

Authors:  Volker Wiebking; Sebastian Hütker; Irene Schmid; Stefanie Immler; Tobias Feuchtinger; Michael H Albert
Journal:  Ann Hematol       Date:  2017-06-01       Impact factor: 3.673

4.  Busulfan conditioning enhances engraftment of hematopoietic donor-derived cells in the brain compared with irradiation.

Authors:  Fiona L Wilkinson; Ana Sergijenko; Kia J Langford-Smith; Marcela Malinowska; Rob F Wynn; Brian W Bigger
Journal:  Mol Ther       Date:  2013-02-19       Impact factor: 11.454

5.  Reduced-toxicity alternate-donor stem cell transplantation with posttransplant cyclophosphamide for primary immunodeficiency disorders.

Authors:  Neha Rastogi; Satyendra Katewa; Dhwanee Thakkar; Shruti Kohli; Sagar Nivargi; Satya Prakash Yadav
Journal:  Pediatr Blood Cancer       Date:  2017-09-13       Impact factor: 3.167

6.  Treosulfan-based conditioning regimens for allogeneic haematopoietic stem cell transplantation in children with non-malignant diseases.

Authors:  M A Slatter; H Boztug; U Pötschger; K-W Sykora; A Lankester; I Yaniv; P Sedlacek; E Glogova; P Veys; A R Gennery; C Peters
Journal:  Bone Marrow Transplant       Date:  2015-08-10       Impact factor: 5.483

7.  Haploidentical Related Donor Hematopoietic Stem Cell Transplantation for Dedicator-of-Cytokinesis 8 Deficiency Using Post-Transplantation Cyclophosphamide.

Authors:  Nirali N Shah; Alexandra F Freeman; Helen Su; Kristen Cole; Mark Parta; Niki M Moutsopoulos; Safa Baris; Elif Karakoc-Aydiner; Thomas E Hughes; Heidi H Kong; Steve M Holland; Dennis D Hickstein
Journal:  Biol Blood Marrow Transplant       Date:  2017-03-10       Impact factor: 5.742

8.  T-cell receptor αβ+ and CD19+ cell-depleted haploidentical and mismatched hematopoietic stem cell transplantation in primary immune deficiency.

Authors:  Ravi M Shah; Reem Elfeky; Zohreh Nademi; Waseem Qasim; Persis Amrolia; Robert Chiesa; Kanchan Rao; Giovanna Lucchini; Juliana M F Silva; Austen Worth; Dawn Barge; David Ryan; Jane Conn; Andrew J Cant; Roderick Skinner; Intan Juliana Abd Hamid; Terence Flood; Mario Abinun; Sophie Hambleton; Andrew R Gennery; Paul Veys; Mary Slatter
Journal:  J Allergy Clin Immunol       Date:  2017-08-03       Impact factor: 10.793

Review 9.  Donor Specific Anti-HLA Antibody and Risk of Graft Failure in Haploidentical Stem Cell Transplantation.

Authors:  Piyanuch Kongtim; Kai Cao; Stefan O Ciurea
Journal:  Adv Hematol       Date:  2016-01-24

10.  Diagnosis and severity criteria for sinusoidal obstruction syndrome/veno-occlusive disease in pediatric patients: a new classification from the European society for blood and marrow transplantation.

Authors:  S Corbacioglu; E Carreras; M Ansari; A Balduzzi; S Cesaro; J-H Dalle; F Dignan; B Gibson; T Guengoer; B Gruhn; A Lankester; F Locatelli; A Pagliuca; C Peters; P G Richardson; A S Schulz; P Sedlacek; J Stein; K-W Sykora; J Toporski; E Trigoso; K Vetteranta; J Wachowiak; E Wallhult; R Wynn; I Yaniv; A Yesilipek; M Mohty; P Bader
Journal:  Bone Marrow Transplant       Date:  2017-07-31       Impact factor: 5.483

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  10 in total

1.  Mismatched related vs matched unrelated donors in TCRαβ/CD19-depleted HSCT for primary immunodeficiencies.

Authors:  Alexandra Laberko; Elvira Sultanova; Elena Gutovskaya; Irina Shipitsina; Larisa Shelikhova; Elena Kurnikova; Yakov Muzalevskii; Alexei Kazachenok; Dmitriy Pershin; Kirill Voronin; Anna Shcherbina; Michael Maschan; Alexey Maschan; Dmitry Balashov
Journal:  Blood       Date:  2019-11-14       Impact factor: 22.113

Review 2.  Allogeneic hematopoietic stem cell transplantation in adults with primary immunodeficiency.

Authors:  Emma C Morris
Journal:  Hematology Am Soc Hematol Educ Program       Date:  2020-12-04

3.  Hematopoietic Cell Transplantation for Inborn Errors of Immunity Other than Severe Combined Immunodeficiency in Japan: Retrospective Analysis for 1985-2016.

Authors:  Satoshi Miyamoto; Katsutsugu Umeda; Mio Kurata; Masakatsu Yanagimachi; Akihiro Iguchi; Yoji Sasahara; Keiko Okada; Takashi Koike; Reo Tanoshima; Masataka Ishimura; Masafumi Yamada; Maho Sato; Yoshiyuki Takahashi; Michiko Kajiwara; Hiroshi Kawaguchi; Masami Inoue; Yoshiko Hashii; Hiromasa Yabe; Koji Kato; Yoshiko Atsuta; Kohsuke Imai; Tomohiro Morio
Journal:  J Clin Immunol       Date:  2022-01-04       Impact factor: 8.317

4.  Prospective Study of a Novel, Radiation-Free, Reduced-Intensity Bone Marrow Transplantation Platform for Primary Immunodeficiency Diseases.

Authors:  Dimana Dimitrova; Juan Gea-Banacloche; Seth M Steinberg; Jennifer L Sadler; Stephanie N Hicks; Ellen Carroll; Jennifer S Wilder; Mark Parta; Lauren Skeffington; Thomas E Hughes; Jenny E Blau; Miranda M Broadney; Jeremy J Rose; Amy P Hsu; Rochelle Fletcher; Natalia S Nunes; Xiao-Yi Yan; William G Telford; Veena Kapoor; Jeffrey I Cohen; Alexandra F Freeman; Elizabeth Garabedian; Steven M Holland; Andrea Lisco; Harry L Malech; Luigi D Notarangelo; Irini Sereti; Nirali N Shah; Gulbu Uzel; Christa S Zerbe; Daniel H Fowler; Ronald E Gress; Christopher G Kanakry; Jennifer A Kanakry
Journal:  Biol Blood Marrow Transplant       Date:  2019-09-04       Impact factor: 5.742

5.  HLA-Haploidentical Hematopoietic Cell Transplantation for Treatment of Nonmalignant Diseases Using Nonmyeloablative Conditioning and Post-Transplant Cyclophosphamide.

Authors:  Kanwaldeep K Mallhi; Meera A Srikanthan; Kelsey K Baker; Haydar A Frangoul; Troy R Torgerson; Aleksandra Petrovic; Amy E Geddis; Paul A Carpenter; K Scott Baker; Brenda M Sandmaier; Monica S Thakar; Suzanne Skoda-Smith; Hans-Peter Kiem; Rainer Storb; Ann E Woolfrey; Lauri M Burroughs
Journal:  Biol Blood Marrow Transplant       Date:  2020-03-28       Impact factor: 5.742

Review 6.  Allogeneic HSCT in Adolescents and Young Adults With Primary Immunodeficiencies.

Authors:  Emma C Morris; Michael H Albert
Journal:  Front Pediatr       Date:  2019-10-24       Impact factor: 3.418

Review 7.  Hematopoietic Stem Cell Transplantation for Combined Immunodeficiencies, on Behalf of IEWP-EBMT.

Authors:  Benedicte Neven; Francesca Ferrua
Journal:  Front Pediatr       Date:  2020-01-24       Impact factor: 3.418

8.  Salvage HLA-haploidentical hematopoietic stem cell transplantation with post-transplant cyclophosphamide for graft failure in non-malignant disorders.

Authors:  Michael H Albert; Mehtap Sirin; Manfred Hoenig; Fabian Hauck; Catharina Schuetz; Rajat Bhattacharyya; Polina Stepensky; Elad Jacoby; Tayfun Güngör; Rita Beier; Ansgar Schulz
Journal:  Bone Marrow Transplant       Date:  2021-05-09       Impact factor: 5.483

Review 9.  EBMT/ESID inborn errors working party guidelines for hematopoietic stem cell transplantation for inborn errors of immunity.

Authors:  A C Lankester; M H Albert; C Booth; A R Gennery; T Güngör; M Hönig; E C Morris; D Moshous; B Neven; A Schulz; M Slatter; P Veys
Journal:  Bone Marrow Transplant       Date:  2021-07-05       Impact factor: 5.483

10.  Haploidentical Hematopoietic Cell Transplantation Using Post-transplant Cyclophosphamide for Children with Non-malignant Diseases.

Authors:  Hasan Hashem; Rula Najjar; Mayada Abu-Shanap; Eman Khattab; Rawad Rihani; Abdelghani Tbakhi; Iyad Sultan
Journal:  J Clin Immunol       Date:  2021-08-06       Impact factor: 8.317

  10 in total

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