Literature DB >> 34226669

EBMT/ESID inborn errors working party guidelines for hematopoietic stem cell transplantation for inborn errors of immunity.

A C Lankester1, M H Albert2, C Booth3, A R Gennery4, T Güngör5, M Hönig6, E C Morris7, D Moshous8,9,10, B Neven8,9,11, A Schulz6, M Slatter4, P Veys3.   

Abstract

Entities:  

Year:  2021        PMID： 34226669     DOI： 10.1038/s41409-021-01378-8

Source DB:  PubMed          Journal:  Bone Marrow Transplant        ISSN： 0268-3369            Impact factor:   5.483


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  76 in total

1.  Hematopoietic Stem Cell Transplantation as Treatment for Patients with DOCK8 Deficiency.

Authors:  Susanne E Aydin; Alexandra F Freeman; Waleed Al-Herz; Hamoud A Al-Mousa; Rand K Arnaout; Roland C Aydin; Vincent Barlogis; Bernd H Belohradsky; Carmem Bonfim; Robbert G Bredius; Julia I Chu; Oana C Ciocarlie; Figen Doğu; Hubert B Gaspar; Raif S Geha; Andrew R Gennery; Fabian Hauck; Abbas Hawwari; Dennis D Hickstein; Manfred Hoenig; Aydan Ikinciogullari; Christoph Klein; Ashish Kumar; Marianne R S Ifversen; Susanne Matthes; Ayse Metin; Benedicte Neven; Sung-Yun Pai; Suhag H Parikh; Capucine Picard; Ellen D Renner; Özden Sanal; Ansgar S Schulz; Friedhelm Schuster; Nirali N Shah; Evan B Shereck; Mary A Slatter; Helen C Su; Joris van Montfrans; Wilhelm Woessmann; John B Ziegler; Michael H Albert
Journal:  J Allergy Clin Immunol Pract       Date:  2018-11-02

2.  Autoimmune and inflammatory manifestations occur frequently in patients with primary immunodeficiencies.

Authors:  Alain Fischer; Johan Provot; Jean-Philippe Jais; Alexandre Alcais; Nizar Mahlaoui
Journal:  J Allergy Clin Immunol       Date:  2017-02-10       Impact factor: 10.793

3.  Transplantation of hematopoietic stem cells and long-term survival for primary immunodeficiencies in Europe: entering a new century, do we do better?

Authors:  Andrew R Gennery; Mary A Slatter; Laure Grandin; Pierre Taupin; Andrew J Cant; Paul Veys; Persis J Amrolia; H Bobby Gaspar; E Graham Davies; Wilhelm Friedrich; Manfred Hoenig; Luigi D Notarangelo; Evelina Mazzolari; Fulvio Porta; Robbert G M Bredius; Arjen C Lankester; Nico M Wulffraat; Reinhard Seger; Tayfun Güngör; Anders Fasth; Petr Sedlacek; Benedicte Neven; Stephane Blanche; Alain Fischer; Marina Cavazzana-Calvo; Paul Landais
Journal:  J Allergy Clin Immunol       Date:  2010-07-31       Impact factor: 10.793

4.  Targeted busulfan-based reduced-intensity conditioning and HLA-matched HSCT cure hemophagocytic lymphohistiocytosis.

Authors:  Matthias Felber; Colin G Steward; Karim Kentouche; Anders Fasth; Robert F Wynn; Ulrike Zeilhofer; Veronika Haunerdinger; Benjamin Volkmer; Seraina Prader; Bernd Gruhn; Stephan Ehl; Kai Lehmberg; Daniel Müller; Andrew R Gennery; Michael H Albert; Fabian Hauck; Kanchan Rao; Paul Veys; Moustapha Hassan; Arjan C Lankester; Jana Pachlopnik Schmid; Mathias M Hauri-Hohl; Tayfun Güngör
Journal:  Blood Adv       Date:  2020-05-12

5.  Allogeneic hematopoietic stem cell transplantation in leukocyte adhesion deficiency type I and III.

Authors:  Shahrzad Bakhtiar; Emilia Salzmann-Manrique; Henric-Jan Blok; Dirk-Jan Eikema; Sheree Hazelaar; Mouhab Ayas; Amos Toren; Gal Goldstein; Despina Moshous; Franco Locatelli; Pietro Merli; Gerard Michel; Gülyüz Öztürk; Ansgar Schulz; Carsten Heilmann; Marianne Ifversen; Rob F Wynn; Olga Aleinikova; Yves Bertrand; Abdelghani Tbakhi; Paul Veys; Musa Karakukcu; Alphan Kupesiz; Ardeshir Ghavamzadeh; Rupert Handgretinger; Emel Unal; Antonio Perez-Martinez; Muge Gokce; Fulvio Porta; Tekin Aksu; Gülsün Karasu; Isabel Badell; Per Ljungman; Elena Skorobogatova; Akif Yesilipek; Tsila Zuckerman; Robbert R G Bredius; Polina Stepensky; Bella Shadur; Mary Slatter; Andrew R Gennery; Michael H Albert; Peter Bader; Arjan Lankester
Journal:  Blood Adv       Date:  2021-01-12

6.  Hematopoietic stem cell transplantation for CD40 ligand deficiency: Results from an EBMT/ESID-IEWP-SCETIDE-PIDTC study.

Authors:  Francesca Ferrua; Stefania Galimberti; Virginie Courteille; Mary Anne Slatter; Claire Booth; Despina Moshous; Benedicte Neven; Stephane Blanche; Marina Cavazzana; Alexandra Laberko; Anna Shcherbina; Dmitry Balashov; Elena Soncini; Fulvio Porta; Hamoud Al-Mousa; Bandar Al-Saud; Hasan Al-Dhekri; Rand Arnaout; Renata Formankova; Yves Bertrand; Andrzej Lange; Joanne Smart; Beata Wolska-Kusnierz; Victor M Aquino; Christopher C Dvorak; Anders Fasth; Fanny Fouyssac; Carsten Heilmann; Manfred Hoenig; Catharina Schuetz; Jadranka Kelečić; Robbert G M Bredius; Arjan C Lankester; Caroline A Lindemans; Felipe Suarez; Kathleen E Sullivan; Michael H Albert; Krzysztof Kałwak; Vincent Barlogis; Monica Bhatia; Victoria Bordon; Wojciech Czogala; Laura Alonso; Figen Dogu; Jolanta Gozdzik; Aydan Ikinciogullari; Gergely Kriván; Per Ljungman; Isabelle Meyts; Peter Mustillo; Angela R Smith; Carsten Speckmann; Mikael Sundin; Steven John Keogh; Peter John Shaw; Jaap Jan Boelens; Ansgar S Schulz; Petr Sedlacek; Paul Veys; Nizar Mahlaoui; Ales Janda; E Graham Davies; Alain Fischer; Morton J Cowan; Andrew Richard Gennery
Journal:  J Allergy Clin Immunol       Date:  2019-01-17       Impact factor: 10.793

7.  Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.

Authors:  Donald B Kohn; Claire Booth; Kit L Shaw; Jinhua Xu-Bayford; Elizabeth Garabedian; Valentina Trevisan; Denise A Carbonaro-Sarracino; Kajal Soni; Dayna Terrazas; Katie Snell; Alan Ikeda; Diego Leon-Rico; Theodore B Moore; Karen F Buckland; Ami J Shah; Kimberly C Gilmour; Satiro De Oliveira; Christine Rivat; Gay M Crooks; Natalia Izotova; John Tse; Stuart Adams; Sally Shupien; Hilory Ricketts; Alejandra Davila; Chilenwa Uzowuru; Amalia Icreverzi; Provaboti Barman; Beatriz Campo Fernandez; Roger P Hollis; Maritess Coronel; Allen Yu; Krista M Chun; Christian E Casas; Ruixue Zhang; Serena Arduini; Frances Lynn; Mahesh Kudari; Andrea Spezzi; Marco Zahn; Rene Heimke; Ivan Labik; Roberta Parrott; Rebecca H Buckley; Lilith Reeves; Kenneth Cornetta; Robert Sokolic; Michael Hershfield; Manfred Schmidt; Fabio Candotti; Harry L Malech; Adrian J Thrasher; H Bobby Gaspar
Journal:  N Engl J Med       Date:  2021-05-11       Impact factor: 91.245

8.  Human Inborn Errors of Immunity: 2019 Update on the Classification from the International Union of Immunological Societies Expert Committee.

Authors:  Stuart G Tangye; Waleed Al-Herz; Aziz Bousfiha; Talal Chatila; Charlotte Cunningham-Rundles; Amos Etzioni; Jose Luis Franco; Steven M Holland; Christoph Klein; Tomohiro Morio; Hans D Ochs; Eric Oksenhendler; Capucine Picard; Jennifer Puck; Troy R Torgerson; Jean-Laurent Casanova; Kathleen E Sullivan
Journal:  J Clin Immunol       Date:  2020-01-17       Impact factor: 8.317

9.  Human Inborn Errors of Immunity: 2019 Update of the IUIS Phenotypical Classification.

Authors:  Aziz Bousfiha; Leila Jeddane; Capucine Picard; Waleed Al-Herz; Fatima Ailal; Talal Chatila; Charlotte Cunningham-Rundles; Amos Etzioni; Jose Luis Franco; Steven M Holland; Christoph Klein; Tomohiro Morio; Hans D Ochs; Eric Oksenhendler; Jennifer Puck; Troy R Torgerson; Jean-Laurent Casanova; Kathleen E Sullivan; Stuart G Tangye
Journal:  J Clin Immunol       Date:  2020-02-11       Impact factor: 8.317

10.  Hematopoietic Cell Transplantation in Patients With Primary Immune Regulatory Disorders (PIRD): A Primary Immune Deficiency Treatment Consortium (PIDTC) Survey.

Authors:  Alice Y Chan; Jennifer W Leiding; Xuerong Liu; Brent R Logan; Lauri M Burroughs; Eric J Allenspach; Suzanne Skoda-Smith; Gulbu Uzel; Luigi D Notarangelo; Mary Slatter; Andrew R Gennery; Angela R Smith; Sung-Yun Pai; Michael B Jordan; Rebecca A Marsh; Morton J Cowan; Christopher C Dvorak; John A Craddock; Susan E Prockop; Shanmuganathan Chandrakasan; Neena Kapoor; Rebecca H Buckley; Suhag Parikh; Deepak Chellapandian; Benjamin R Oshrine; Jeffrey J Bednarski; Megan A Cooper; Shalini Shenoy; Blachy J Davila Saldana; Lisa R Forbes; Caridad Martinez; Elie Haddad; David C Shyr; Karin Chen; Kathleen E Sullivan; Jennifer Heimall; Nicola Wright; Monica Bhatia; Geoffrey D E Cuvelier; Frederick D Goldman; Isabelle Meyts; Holly K Miller; Markus G Seidel; Mark T Vander Lugt; Rosa Bacchetta; Katja G Weinacht; Jeffrey R Andolina; Emi Caywood; Hey Chong; Maria Teresa de la Morena; Victor M Aquino; Evan Shereck; Jolan E Walter; Morna J Dorsey; Christine M Seroogy; Linda M Griffith; Donald B Kohn; Jennifer M Puck; Michael A Pulsipher; Troy R Torgerson
Journal:  Front Immunol       Date:  2020-02-21       Impact factor: 7.561
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  12 in total

Review 1.  Conditioning regimens for inborn errors of immunity: current perspectives and future strategies.

Authors:  Akira Nishimura; Satoshi Miyamoto; Kohsuke Imai; Tomohiro Morio
Journal:  Int J Hematol       Date:  2022-06-08       Impact factor: 2.490

Review 2.  Unresolved issues in allogeneic hematopoietic cell transplantation for non-malignant diseases.

Authors:  Katsutsugu Umeda
Journal:  Int J Hematol       Date:  2022-05-14       Impact factor: 2.490

Review 3.  Thymus Functionality Needs More Than a Few TECs.

Authors:  Pratibha Bhalla; Dong-Ming Su; Nicolai S C van Oers
Journal:  Front Immunol       Date:  2022-06-10       Impact factor: 8.786

4.  Lentiviral gene therapy prevents anti-human acid α-glucosidase antibody formation in murine Pompe disease.

Authors:  Qiushi Liang; Eva C Vlaar; Fabio Catalano; Joon M Pijnenburg; Merel Stok; Yvette van Helsdingen; Arnold G Vulto; Wendy W J Unger; Ans T van der Ploeg; W W M Pim Pijnappel; Niek P van Til
Journal:  Mol Ther Methods Clin Dev       Date:  2022-05-04       Impact factor: 5.849

5.  Indications for haematopoietic cell transplantation for haematological diseases, solid tumours and immune disorders: current practice in Europe, 2022.

Authors:  John A Snowden; Isabel Sánchez-Ortega; Selim Corbacioglu; Grzegorz W Basak; Christian Chabannon; Rafael de la Camara; Harry Dolstra; Rafael F Duarte; Bertram Glass; Raffaella Greco; Arjan C Lankester; Mohamad Mohty; Bénédicte Neven; Régis Peffault de Latour; Paolo Pedrazzoli; Zinaida Peric; Ibrahim Yakoub-Agha; Anna Sureda; Nicolaus Kröger
Journal:  Bone Marrow Transplant       Date:  2022-05-19       Impact factor: 5.174

6.  Bayesian Modeling Immune Reconstitution Apply to CD34+ Selected Stem Cell Transplantation for Severe Combined Immunodeficiency.

Authors:  Jean-Sebastien Diana; Naïm Bouazza; Chloe Couzin; Martin Castelle; Alessandra Magnani; Elisa Magrin; Jeremie Rosain; Jean-Marc Treluyer; Capucine Picard; Despina Moshous; Stéphane Blanche; Bénédicte Neven; Marina Cavazzana
Journal:  Front Pediatr       Date:  2022-02-15       Impact factor: 3.418

7.  Case Report: Rubella Virus-Induced Cutaneous Granulomas in Two Pediatric Patients With DNA Double Strand Breakage Repair Disorders - Outcome After Hematopoietic Stem Cell Transplantation.

Authors:  Ulrich Baumann; Johannes H Schulte; Jonathan P Groß; Rita Beier; Marius Ludwig; Volker Wahn; Jörg Hofmann; Britta Maecker-Kolhoff; Martin Sauer; Petra Kaiser-Labusch; Negin Karimian; Ulrike Blume-Peytavi; Franziska Ghoreschi; Hagen Ott; Ludmila Perelygina; Christian Klemann; Oliver Blankenstein; Horst von Bernuth; Renate Krüger
Journal:  Front Immunol       Date:  2022-06-02       Impact factor: 8.786

Review 8.  Allogeneic Hematopoietic Cell Transplantation for Patients With Deficiency of Adenosine Deaminase 2 (DADA2): Approaches, Obstacles and Special Considerations.

Authors:  Hasan Hashem; Dimana Dimitrova; Isabelle Meyts
Journal:  Front Immunol       Date:  2022-07-07       Impact factor: 8.786

Review 9.  Inborn errors of immunity caused by defects in the DNA damage response pathways: Importance of minimizing treatment-related genotoxicity.

Authors:  Benjamin Fournier; Nizar Mahlaoui; Despina Moshous; Jean-Pierre de Villartay
Journal:  Pediatr Allergy Immunol       Date:  2022-06       Impact factor: 5.464

Review 10.  Therapeutic Drug Monitoring of Conditioning Agents in Pediatric Allogeneic Stem Cell Transplantation; Where do We Stand?

Authors:  M Y Eileen C van der Stoep; Lisa V E Oostenbrink; Robbert G M Bredius; Dirk Jan A R Moes; Henk-Jan Guchelaar; Juliette Zwaveling; Arjan C Lankester
Journal:  Front Pharmacol       Date:  2022-03-07       Impact factor: 5.810
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