Literature DB >> 30559070

AAV-CRISPR Persistence in the Eye of the Beholder.

Alessandra Recchia1.   

Abstract

Mesh：

Year:  2018        PMID： 30559070      PMCID： PMC6320338          DOI： 10.1016/j.ymthe.2018.12.007

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  18 in total

1.  AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice.

Authors:  Chady H Hakim; Nalinda B Wasala; Christopher E Nelson; Lakmini P Wasala; Yongping Yue; Jacqueline A Louderman; Thais B Lessa; Aihua Dai; Keqing Zhang; Gregory J Jenkins; Michael E Nance; Xiufang Pan; Kasun Kodippili; N Nora Yang; Shi-Jie Chen; Charles A Gersbach; Dongsheng Duan
Journal:  JCI Insight       Date:  2018-12-06

2.  A split-Cas9 architecture for inducible genome editing and transcription modulation.

Authors:  Bernd Zetsche; Sara E Volz; Feng Zhang
Journal:  Nat Biotechnol       Date:  2015-02       Impact factor: 54.908

3.  Cas9/sgRNA selective targeting of the P23H Rhodopsin mutant allele for treating retinitis pigmentosa by intravitreal AAV9.PHP.B-based delivery.

Authors:  Serena G Giannelli; Mirko Luoni; Valerio Castoldi; Luca Massimino; Tommaso Cabassi; Debora Angeloni; Gian Carlo Demontis; Letizia Leocani; Massimiliano Andreazzoli; Vania Broccoli
Journal:  Hum Mol Genet       Date:  2018-03-01       Impact factor: 6.150

4.  Long-Term Effects of In Vivo Genome Editing in the Mouse Retina Using Campylobacter jejuni Cas9 Expressed via Adeno-Associated Virus.

Authors:  Dong Hyun Jo; Taeyoung Koo; Chang Sik Cho; Jin Hyoung Kim; Jin-Soo Kim; Jeong Hun Kim
Journal:  Mol Ther       Date:  2018-10-17       Impact factor: 11.454

5.  Orthogonal Cas9 proteins for RNA-guided gene regulation and editing.

Authors:  Kevin M Esvelt; Prashant Mali; Jonathan L Braff; Mark Moosburner; Stephanie J Yaung; George M Church
Journal:  Nat Methods       Date:  2013-09-29       Impact factor: 28.547

6.  Nrl knockdown by AAV-delivered CRISPR/Cas9 prevents retinal degeneration in mice.

Authors:  Wenhan Yu; Suddhasil Mookherjee; Vijender Chaitankar; Suja Hiriyanna; Jung-Woong Kim; Matthew Brooks; Yasaman Ataeijannati; Xun Sun; Lijin Dong; Tiansen Li; Anand Swaroop; Zhijian Wu
Journal:  Nat Commun       Date:  2017-03-14       Impact factor: 14.919

7.  Treatment of a metabolic liver disease by in vivo genome base editing in adult mice.

Authors:  Lukas Villiger; Hiu Man Grisch-Chan; Helen Lindsay; Femke Ringnalda; Chiara B Pogliano; Gabriella Allegri; Ralph Fingerhut; Johannes Häberle; Joao Matos; Mark D Robinson; Beat Thöny; Gerald Schwank
Journal:  Nat Med       Date:  2018-10-08       Impact factor: 53.440

8.  In Vivo CRISPR/Cas9 Gene Editing Corrects Retinal Dystrophy in the S334ter-3 Rat Model of Autosomal Dominant Retinitis Pigmentosa.

Authors:  Benjamin Bakondi; Wenjian Lv; Bin Lu; Melissa K Jones; Yuchun Tsai; Kevin J Kim; Rachelle Levy; Aslam Abbasi Akhtar; Joshua J Breunig; Clive N Svendsen; Shaomei Wang
Journal:  Mol Ther       Date:  2015-12-15       Impact factor: 11.454

9.  In vivo Editing of the Human Mutant Rhodopsin Gene by Electroporation of Plasmid-based CRISPR/Cas9 in the Mouse Retina.

Authors:  Maria Carmela Latella; Maria Teresa Di Salvo; Fabienne Cocchiarella; Daniela Benati; Giulia Grisendi; Antonella Comitato; Valeria Marigo; Alessandra Recchia
Journal:  Mol Ther Nucleic Acids       Date:  2016-11-22       Impact factor: 10.183

Review 10.  In vivo genome editing in animals using AAV-CRISPR system: applications to translational research of human disease.

Authors:  Cia-Hin Lau; Yousin Suh
Journal:  F1000Res       Date:  2017-12-20
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  2 in total

1.  Effect of connective tissue growth factor gene editing using adeno-associated virus-mediated CRISPR-Cas9 on rabbit glaucoma filtering surgery outcomes.

Authors:  Eun Jung Lee; Jong Chul Han; Do Young Park; Junhun Cho; Changwon Kee
Journal:  Gene Ther       Date:  2020-06-15       Impact factor: 5.250

2.  Non-viral delivery of CRISPR-Cas9 complexes for targeted gene editing via a polymer delivery system.

Authors:  Jonathan O'Keeffe Ahern; Irene Lara-Sáez; Dezhong Zhou; Rodolfo Murillas; Jose Bonafont; Ángeles Mencía; Marta García; Darío Manzanares; Jennifer Lynch; Ruth Foley; Qian Xu; A Sigen; Fernando Larcher; Wenxin Wang
Journal:  Gene Ther       Date:  2021-08-06       Impact factor: 4.184
  2 in total

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