Literature DB >> 30486680

ALS longitudinal studies with frequent data collection at home: study design and baseline data.

Seward B Rutkove1, Kristin Qi1, Kerisa Shelton2, Julie Liss3, Visar Berisha4, Jeremy M Shefner2.   

Abstract

OBJECTIVE: To design an ALS clinical study in which patients are remotely recruited, screened, enrolled and then assessed via daily data collection at home by themselves or caregivers.
METHODS: This observational, natural-history study included two academic medical centers, one providing overall clinical management and the other overseeing computing and web-services design and management. Both healthy and ALS subjects were recruited on the Internet via advertisement on governmental and foundation websites as well as through Facebook and Google paid advertisements. Individuals underwent screening and enrollment remotely, including signing an electronic informed consent form. Participants were then provided self-measurement equipment and instructed on their use through a series of web-based videos. The equipment included a handgrip dynamometer, spirometer with smartphone connection, electrical impedance myography device, and an activity tracker. ALS Functional Rating Scale-Revised data were also collected. Subjects were asked to collect data daily for three months and twice-weekly for the subsequent six months.
RESULTS: One hundred and eleven ALS patients and 30 healthy individuals enrolled in the study from across 41 states (74 men, 62 women). Baseline median ALSFRS-R score was 33. Seventy two percent of the ALS patients sent equipment and 88% of the healthy subjects sent equipment were able to complete a first set of measurements. Expected baseline differences between the ALS patients and healthy participants were identified for all measures.
CONCLUSIONS: It is possible to design and institute an at-home based study in ALS patients, using a number of state-of-the-art approaches, including web-based consenting and training and Internet-connected measurement devices.

Entities:  

Year:  2018        PMID: 30486680      PMCID: PMC6513689          DOI: 10.1080/21678421.2018.1541095

Source DB:  PubMed          Journal:  Amyotroph Lateral Scler Frontotemporal Degener        ISSN: 2167-8421            Impact factor:   4.092


  5 in total

1.  The ALSFRS-R: a revised ALS functional rating scale that incorporates assessments of respiratory function. BDNF ALS Study Group (Phase III).

Authors:  J M Cedarbaum; N Stambler; E Malta; C Fuller; D Hilt; B Thurmond; A Nakanishi
Journal:  J Neurol Sci       Date:  1999-10-31       Impact factor: 3.181

Review 2.  Analysis of start-up, retention, and adherence in ALS clinical trials.

Authors:  Nazem Atassi; Padmaja Yerramilli-Rao; Jackie Szymonifka; Hong Yu; Marianne Kearney; Daniela Grasso; Jing Deng; Mark Levine-Weinberg; Jordan Shapiro; Alexandra Lee; Lucia Joseph; Eric A Macklin; Merit E Cudkowicz
Journal:  Neurology       Date:  2013-09-04       Impact factor: 9.910

3.  Safety and efficacy of edaravone in well defined patients with amyotrophic lateral sclerosis: a randomised, double-blind, placebo-controlled trial.

Authors: 
Journal:  Lancet Neurol       Date:  2017-05-15       Impact factor: 44.182

4.  Use of High-Frequency In-Home Monitoring Data May Reduce Sample Sizes Needed in Clinical Trials.

Authors:  Hiroko H Dodge; Jian Zhu; Nora C Mattek; Daniel Austin; Judith Kornfeld; Jeffrey A Kaye
Journal:  PLoS One       Date:  2015-09-17       Impact factor: 3.240

Review 5.  ALS Clinical Trials Review: 20 Years of Failure. Are We Any Closer to Registering a New Treatment?

Authors:  Dmitry Petrov; Colin Mansfield; Alain Moussy; Olivier Hermine
Journal:  Front Aging Neurosci       Date:  2017-03-22       Impact factor: 5.750

  5 in total
  18 in total

1.  Robust Estimation of Hypernasality in Dysarthria with Acoustic Model Likelihood Features.

Authors:  Michael Saxon; Ayush Tripathi; Yishan Jiao; Julie Liss; Visar Berisha
Journal:  IEEE/ACM Trans Audio Speech Lang Process       Date:  2020-08-07

2.  A Bioimpedance-Based Device to Assess the Volume Conduction Properties of the Tongue in Neurological Disorders Affecting Bulbar function.

Authors:  Xuesong Luo; Hilda Victoria Gutierrez Pulido; Seward Rutkove; Benjamin Sanchez
Journal:  IEEE Open J Eng Med Biol       Date:  2021-10-06

3.  OBJECTIVE ASSESSMENT OF VOCAL TREMOR.

Authors:  Jacob Peplinski; Visar Berisha; Julie Liss; Shira Hahn; Jeremy Shefner; Seward Rutkove; Kristin Qi; Kerisa Shelton
Journal:  Proc IEEE Int Conf Acoust Speech Signal Process       Date:  2019-04-17

4.  Repeatability of Commonly Used Speech and Language Features for Clinical Applications.

Authors:  Gabriela M Stegmann; Shira Hahn; Julie Liss; Jeremy Shefner; Seward B Rutkove; Kan Kawabata; Samarth Bhandari; Kerisa Shelton; Cayla Jessica Duncan; Visar Berisha
Journal:  Digit Biomark       Date:  2020-12-02

5.  Accelerometry for remote monitoring of physical activity in amyotrophic lateral sclerosis: a longitudinal cohort study.

Authors:  Ruben P A van Eijk; Jaap N E Bakers; Tommy M Bunte; Arianne J de Fockert; Marinus J C Eijkemans; Leonard H van den Berg
Journal:  J Neurol       Date:  2019-06-11       Impact factor: 4.849

6.  Validation of the portable Bluetooth® Air Next spirometer in patients with different respiratory diseases.

Authors:  Konstantinos P Exarchos; Athena Gogali; Agni Sioutkou; Christos Chronis; Sofia Peristeri; Konstantinos Kostikas
Journal:  Respir Res       Date:  2020-04-06

Review 7.  New technologies and Amyotrophic Lateral Sclerosis - Which step forward rushed by the COVID-19 pandemic?

Authors:  Susana Pinto; Stefano Quintarelli; Vincenzo Silani
Journal:  J Neurol Sci       Date:  2020-08-05       Impact factor: 3.181

Review 8.  Differential Diagnosis of Apraxia of Speech in Children and Adults: A Scoping Review.

Authors:  Kristen M Allison; Claire Cordella; Jenya Iuzzini-Seigel; Jordan R Green
Journal:  J Speech Lang Hear Res       Date:  2020-08-12       Impact factor: 2.297

9.  Improved ALS clinical trials through frequent at-home self-assessment: a proof of concept study.

Authors:  Seward B Rutkove; Pushpa Narayanaswami; Visar Berisha; Julie Liss; Shira Hahn; Kerisa Shelton; Kristin Qi; Sarbesh Pandeya; Jeremy M Shefner
Journal:  Ann Clin Transl Neurol       Date:  2020-06-09       Impact factor: 4.511

10.  Early detection and tracking of bulbar changes in ALS via frequent and remote speech analysis.

Authors:  Gabriela M Stegmann; Shira Hahn; Julie Liss; Jeremy Shefner; Seward Rutkove; Kerisa Shelton; Cayla Jessica Duncan; Visar Berisha
Journal:  NPJ Digit Med       Date:  2020-10-13
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