Literature DB >> 30315484

Clinical characteristics and surgical outcome in USP8-mutated human adrenocorticotropic hormone-secreting pituitary adenomas.

Marco Losa1, Pietro Mortini2, Angela Pagnano2, Mario Detomas2, Maria Francesca Cassarino3, Francesca Pecori Giraldi3,4.   

Abstract

PURPOSE: somatic mutations in the ubiquitin-specific protease 8 (USP8) gene have recently been described in patients with Cushing's disease (CD). The aim of the study is to verify whether USP8 mutation may predict early and late outcome of pituitary surgery in patients with CD operated at a single institution.
METHODS: We performed a retrospective genetic analysis of 92 adrenocorticotropic hormone (ACTH)-secreting pituitary adenomas. Specimens were screened for USP8 hotspot mutations in the exon 14 with Sanger sequencing. Hormonal and surgical data were compared between USP8 variant carriers and wild-type tumors.
RESULTS: USP8 variants were detected in 22 adenomas (23.9%) with higher prevalence in women (28.9% vs. 5.3% in men; p < 0.05). No significant difference in hormonal levels and tumoral features in relation to USP8 status was observed. Interestingly, USP8-variant carriers were more likely to achieve surgical remission than wild-type adenomas (100% vs. 75.7%; p = 0.01). Conversely, recurrence of CD occurred in 23% of USP8-mutated patients and in 13% of patients with wild-type adenoma. The recurrence-free survival did not differ significantly between the two groups (p = 0.42).
CONCLUSIONS: ACTH-secreting pituitary adenomas carrying somatic USP8 mutations are associated with a greater likelihood of surgical remission in patients operated by a single neurosurgeon. Recurrence rates are not related with USP8-variant status.

Entities:  

Keywords:  Adrenocorticotropin; Cortisol; Pituitary neoplasms; Pituitary surgery

Mesh:

Substances:

Year:  2018        PMID: 30315484     DOI: 10.1007/s12020-018-1776-0

Source DB:  PubMed          Journal:  Endocrine        ISSN: 1355-008X            Impact factor:   3.633


  29 in total

1.  Long-term results after microsurgery for Cushing disease: experience with 426 primary operations over 35 years.

Authors:  Bernd Markus Hofmann; Michal Hlavac; Ramon Martinez; Michael Buchfelder; Otto Albrecht Müller; Rudolf Fahlbusch
Journal:  J Neurosurg       Date:  2008-01       Impact factor: 5.115

2.  The Gene of the Ubiquitin-Specific Protease 8 Is Frequently Mutated in Adenomas Causing Cushing's Disease.

Authors:  Luis G Perez-Rivas; Marily Theodoropoulou; Francesco Ferraù; Clara Nusser; Kohei Kawaguchi; Constantine A Stratakis; Fabio Rueda Faucz; Luiz E Wildemberg; Guillaume Assié; Rudi Beschorner; Christina Dimopoulou; Michael Buchfelder; Vera Popovic; Christina M Berr; Miklós Tóth; Arif Ibrahim Ardisasmita; Jürgen Honegger; Jerôme Bertherat; Monica R Gadelha; Felix Beuschlein; Günter Stalla; Masayuki Komada; Márta Korbonits; Martin Reincke
Journal:  J Clin Endocrinol Metab       Date:  2015-05-05       Impact factor: 5.958

Review 3.  Diagnosis and Clinical Genetics of Cushing Syndrome in Pediatrics.

Authors:  Constantine A Stratakis
Journal:  Endocrinol Metab Clin North Am       Date:  2016-06       Impact factor: 4.741

4.  EGFR as a therapeutic target for human, canine, and mouse ACTH-secreting pituitary adenomas.

Authors:  Hidenori Fukuoka; Odelia Cooper; Anat Ben-Shlomo; Adam Mamelak; Song-Guang Ren; Dave Bruyette; Shlomo Melmed
Journal:  J Clin Invest       Date:  2011-11-21       Impact factor: 14.808

5.  Desmopressin stimulation test before and after pituitary surgery in patients with Cushing's disease.

Authors:  M Losa; P Mortini; S Dylgjeri; R Barzaghi; A Franzin; C Mandelli; M Giovanelli
Journal:  Clin Endocrinol (Oxf)       Date:  2001-07       Impact factor: 3.478

6.  Treatment of Cushing's Syndrome: An Endocrine Society Clinical Practice Guideline.

Authors:  Lynnette K Nieman; Beverly M K Biller; James W Findling; M Hassan Murad; John Newell-Price; Martin O Savage; Antoine Tabarin
Journal:  J Clin Endocrinol Metab       Date:  2015-07-29       Impact factor: 5.958

7.  Persistent adrenocorticotropin response to desmopressin in the early postoperative period predicts recurrence of Cushing's disease.

Authors:  Marco Losa; Roberto Bianchi; Raffaella Barzaghi; Massimo Giovanelli; Pietro Mortini
Journal:  J Clin Endocrinol Metab       Date:  2009-07-07       Impact factor: 5.958

8.  Outcome of Transsphenoidal Surgery for Cushing Disease: A Single-Center Experience Over 32 Years.

Authors:  William F Chandler; Ariel L Barkan; Todd Hollon; Alla Sakharova; Jayson Sack; Barunashish Brahma; David E Schteingart
Journal:  Neurosurgery       Date:  2016-02       Impact factor: 4.654

9.  Gene expression profiling in human corticotroph tumours reveals distinct, neuroendocrine profiles.

Authors:  Maria Francesca Cassarino; Alberto G Ambrogio; Andrea Cassarino; Maria Rosa Terreni; Davide Gentilini; Antonella Sesta; Francesco Cavagnini; Marco Losa; Francesca Pecori Giraldi
Journal:  J Neuroendocrinol       Date:  2018-08-07       Impact factor: 3.627

10.  USP8 Mutations in Pituitary Cushing Adenomas-Targeted Analysis by Next-Generation Sequencing.

Authors:  Cora Ballmann; Anne Thiel; Hannah E Korah; Anna-Carinna Reis; Wolfgang Saeger; Stefanie Stepanow; Karl Köhrer; Guido Reifenberger; Christiane B Knobbe-Thomsen; Ulrich J Knappe; Ute I Scholl
Journal:  J Endocr Soc       Date:  2018-02-19
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  16 in total

1.  Cushing's disease due to somatic USP8 mutations: a systematic review and meta-analysis.

Authors:  Ingrid Quevedo Wanichi; Beatriz Marinho de Paula Mariani; Fernando Pereira Frassetto; Sheila Aparecida Coelho Siqueira; Nina Rosa de Castro Musolino; Malebranche Berardo Carneiro Cunha-Neto; Gilberto Ochman; Valter Angelo Sperling Cescato; Marcio Carlos Machado; Ericka Barbosa Trarbach; Marcello Delano Bronstein; Maria Candida Barisson Villares Fragoso
Journal:  Pituitary       Date:  2019-08       Impact factor: 4.107

2.  Ubiquitin-Specific Protease 8 Mutant Corticotrope Adenomas Present Unique Secretory and Molecular Features and Shed Light on the Role of Ubiquitylation on ACTH Processing.

Authors:  Antonella Sesta; Maria Francesca Cassarino; Mariarosa Terreni; Alberto G Ambrogio; Laura Libera; Donatella Bardelli; Giovanni Lasio; Marco Losa; Francesca Pecori Giraldi
Journal:  Neuroendocrinology       Date:  2019-10-16       Impact factor: 4.914

3.  Germline USP8 Mutation Associated With Pediatric Cushing Disease and Other Clinical Features: A New Syndrome.

Authors:  Michal Cohen; Rebecca Persky; Rachel Stegemann; Laura C Hernández-Ramírez; Deena Zeltser; Maya B Lodish; Anlu Chen; Margaret F Keil; Christina Tatsi; Fabio R Faucz; David A Buchner; Constantine A Stratakis; Dov Tiosano
Journal:  J Clin Endocrinol Metab       Date:  2019-10-01       Impact factor: 5.958

4.  USP8, USP48, and BRAF mutations differ in their genotype-phenotype correlation in Asian Indian patients with Cushing's disease.

Authors:  Ananth P Abraham; Rekha Pai; Daniel L Beno; Geeta Chacko; Hesarghatta Shyamasunder Asha; Simon Rajaratnam; Nitin Kapoor; Nihal Thomas; Ari G Chacko
Journal:  Endocrine       Date:  2021-10-18       Impact factor: 3.633

Review 5.  Genetic Basis of ACTH-Secreting Adenomas.

Authors:  Pietro Locantore; Rosa Maria Paragliola; Gianluca Cera; Roberto Novizio; Ettore Maggio; Vittoria Ramunno; Andrea Corsello; Salvatore Maria Corsello
Journal:  Int J Mol Sci       Date:  2022-06-19       Impact factor: 6.208

Review 6.  Drug resistance in pituitary tumours: from cell membrane to intracellular signalling.

Authors:  Erika Peverelli; Donatella Treppiedi; Federica Mangili; Rosa Catalano; Anna Spada; Giovanna Mantovani
Journal:  Nat Rev Endocrinol       Date:  2021-06-30       Impact factor: 43.330

Review 7.  Cushing syndrome: Old and new genes.

Authors:  Christina Tatsi; Chelsi Flippo; Constantine A Stratakis
Journal:  Best Pract Res Clin Endocrinol Metab       Date:  2020-04-02       Impact factor: 4.690

Review 8.  Emerging Role of USP8, HMGA, and Non-Coding RNAs in Pituitary Tumorigenesis.

Authors:  Daniela D'Angelo; Marco De Martino; Claudio Arra; Alfredo Fusco
Journal:  Cancers (Basel)       Date:  2019-09-04       Impact factor: 6.639

Review 9.  The Genetics of Pituitary Adenomas.

Authors:  Christina Tatsi; Constantine A Stratakis
Journal:  J Clin Med       Date:  2019-12-21       Impact factor: 4.241

10.  Sexual Dimorphism in Cellular and Molecular Features in Human ACTH-Secreting Pituitary Adenomas.

Authors:  Francesca Pecori Giraldi; Maria Francesca Cassarino; Antonella Sesta; Mariarosa Terreni; Giovanni Lasio; Marco Losa
Journal:  Cancers (Basel)       Date:  2020-03-13       Impact factor: 6.639

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