Literature DB >> 30307929

Sangamo's landmark genome editing trial gets mixed reception.

Cormac Sheridan.   

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Year:  2018        PMID: 30307929     DOI: 10.1038/nbt1018-907

Source DB:  PubMed          Journal:  Nat Biotechnol        ISSN: 1087-0156            Impact factor:   54.908


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  3 in total

1.  Mammoth, Arbor and Beam launch new wave of CRISPR startups.

Authors:  Cormac Sheridan
Journal:  Nat Biotechnol       Date:  2018-06-06       Impact factor: 54.908

2.  Keep calm and edit on.

Authors: 
Journal:  Nat Biotechnol       Date:  2018-08-06       Impact factor: 54.908

3.  CRISPR therapeutics push into human testing.

Authors:  Cormac Sheridan
Journal:  Nat Biotechnol       Date:  2017-01-10       Impact factor: 54.908

  3 in total
  11 in total

Review 1.  Targeting cancer epigenetics with CRISPR-dCAS9: Principles and prospects.

Authors:  Mohammad Mijanur Rahman; Trygve O Tollefsbol
Journal:  Methods       Date:  2020-04-18       Impact factor: 3.608

Review 2.  CRISPR/Cas9 for the treatment of haematological diseases: a journey from bacteria to the bedside.

Authors:  Olivier Humbert; Clare Samuelson; Hans-Peter Kiem
Journal:  Br J Haematol       Date:  2020-06-07       Impact factor: 6.998

Review 3.  Therapeutic Options for Mucopolysaccharidoses: Current and Emerging Treatments.

Authors:  Kazuki Sawamoto; Molly Stapleton; Carlos J Alméciga-Díaz; Angela J Espejo-Mojica; Juan Camilo Losada; Diego A Suarez; Shunji Tomatsu
Journal:  Drugs       Date:  2019-07       Impact factor: 11.431

Review 4.  Precision Medicine for Lysosomal Disorders.

Authors:  Filippo Pinto E Vairo; Diana Rojas Málaga; Francyne Kubaski; Carolina Fischinger Moura de Souza; Fabiano de Oliveira Poswar; Guilherme Baldo; Roberto Giugliani
Journal:  Biomolecules       Date:  2020-07-26

Review 5.  Genome Editing for Mucopolysaccharidoses.

Authors:  Edina Poletto; Guilherme Baldo; Natalia Gomez-Ospina
Journal:  Int J Mol Sci       Date:  2020-01-13       Impact factor: 5.923

6.  A few ethical issues in translational research for gene and cell therapy.

Authors:  Luciana Riva; Carlo Petrini
Journal:  J Transl Med       Date:  2019-11-28       Impact factor: 5.531

Review 7.  Gene Therapy for Mucopolysaccharidosis Type II-A Review of the Current Possibilities.

Authors:  Paweł Zapolnik; Antoni Pyrkosz
Journal:  Int J Mol Sci       Date:  2021-05-23       Impact factor: 5.923

Review 8.  Mucopolysaccharidosis Type I.

Authors:  Francyne Kubaski; Fabiano de Oliveira Poswar; Kristiane Michelin-Tirelli; Ursula da Silveira Matte; Dafne D Horovitz; Anneliese Lopes Barth; Guilherme Baldo; Filippo Vairo; Roberto Giugliani
Journal:  Diagnostics (Basel)       Date:  2020-03-16

9.  Gene editing and CRISPR in the clinic: current and future perspectives.

Authors:  Matthew P Hirakawa; Raga Krishnakumar; Jerilyn A Timlin; James P Carney; Kimberly S Butler
Journal:  Biosci Rep       Date:  2020-04-30       Impact factor: 3.840

10.  A qPCR method for genome editing efficiency determination and single-cell clone screening in human cells.

Authors:  Bo Li; Naixia Ren; Lele Yang; Junhao Liu; Qilai Huang
Journal:  Sci Rep       Date:  2019-12-11       Impact factor: 4.379

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