Cormac Sheridan. Show Affiliations »
Abstract
Mesh: See more » BiotechnologyCRISPR-Cas SystemsClinical Trials as TopicGene EditingHumansMucopolysaccharidosis II/enzymologyMucopolysaccharidosis II/geneticsMucopolysaccharidosis II/therapyZinc Finger Nucleases/genetics
Substances: See more » Zinc Finger Nucleases
Year: 2018 PMID: 30307929 DOI: 10.1038/nbt1018-907
Source DB: PubMed Journal: Nat Biotechnol ISSN: 1087-0156 Impact factor: 54.908