Literature DB >> 29896650

Congenital Diabetes: Comprehensive Genetic Testing Allows for Improved Diagnosis and Treatment of Diabetes and Other Associated Features.

Lisa R Letourneau1, Siri Atma W Greeley2.   

Abstract

PURPOSE OF REVIEW: The goal of this review is to provide updates on congenital (neonatal) diabetes from 2011 to present, with an emphasis on publications from 2015 to present. RECENT
FINDINGS: There has been continued worldwide progress in uncovering the genetic causes of diabetes presenting within the first year of life, including the recognition of nine new causes since 2011. Management has continued to be refined based on underlying molecular cause, and longer-term experience has provided better understanding of the effectiveness, safety, and sustainability of treatment. Associated conditions have been further clarified, such as neurodevelopmental delays and pancreatic insufficiency, including a better appreciation for how these "secondary" conditions impact quality of life for patients and their families. While continued research is essential to understand all forms of congenital diabetes, these cases remain a compelling example of personalized genetic medicine.

Entities:  

Keywords:  Congenital diabetes; Monogenic diabetes; NDM; Neonatal diabetes; PNDM; TNDM

Mesh:

Substances:

Year:  2018        PMID: 29896650      PMCID: PMC6341981          DOI: 10.1007/s11892-018-1016-2

Source DB:  PubMed          Journal:  Curr Diab Rep        ISSN: 1534-4827            Impact factor:   4.810


  103 in total

1.  Creation of the Web-based University of Chicago Monogenic Diabetes Registry: using technology to facilitate longitudinal study of rare subtypes of diabetes.

Authors:  Siri Atma W Greeley; Rochelle N Naylor; Lindsay S Cook; Susan E Tucker; Rebecca B Lipton; Louis H Philipson
Journal:  J Diabetes Sci Technol       Date:  2011-07-01

2.  A gene encoding a transmembrane protein is mutated in patients with diabetes mellitus and optic atrophy (Wolfram syndrome).

Authors:  H Inoue; Y Tanizawa; J Wasson; P Behn; K Kalidas; E Bernal-Mizrachi; M Mueckler; H Marshall; H Donis-Keller; P Crock; D Rogers; M Mikuni; H Kumashiro; K Higashi; G Sobue; Y Oka; M A Permutt
Journal:  Nat Genet       Date:  1998-10       Impact factor: 38.330

3.  Hypoglycemia in sulfonylurea-treated KCNJ11-neonatal diabetes: Mild-moderate symptomatic episodes occur infrequently but none involving unconsciousness or seizures.

Authors:  Monica S Lanning; David Carmody; Łukasz Szczerbiński; Lisa R Letourneau; Rochelle N Naylor; Siri Atma W Greeley
Journal:  Pediatr Diabetes       Date:  2017-12-05       Impact factor: 4.866

4.  A case of novel de novo paired box gene 6 (PAX6) mutation with early-onset diabetes mellitus and aniridia.

Authors:  M Nishi; M Sasahara; T Shono; S Saika; Y Yamamoto; K Ohkawa; H Furuta; T Nakao; H Sasaki; K Nanjo
Journal:  Diabet Med       Date:  2005-05       Impact factor: 4.359

5.  Dominant ER Stress-Inducing WFS1 Mutations Underlie a Genetic Syndrome of Neonatal/Infancy-Onset Diabetes, Congenital Sensorineural Deafness, and Congenital Cataracts.

Authors:  Elisa De Franco; Sarah E Flanagan; Takuya Yagi; Damien Abreu; Jana Mahadevan; Matthew B Johnson; Garan Jones; Fernanda Acosta; Mphele Mulaudzi; Ngee Lek; Vera Oh; Oliver Petz; Richard Caswell; Sian Ellard; Fumihiko Urano; Andrew T Hattersley
Journal:  Diabetes       Date:  2017-05-03       Impact factor: 9.461

6.  Recovered insulin production after thiamine administration in permanent neonatal diabetes mellitus with a novel solute carrier family 19 member 2 (SLC19A2) mutation.

Authors:  Chengjun Sun; Zhou Pei; Miaoying Zhang; Bijun Sun; Lin Yang; Zhuhui Zhao; Ruoqian Cheng; Feihong Luo
Journal:  J Diabetes       Date:  2017-05-29       Impact factor: 4.006

7.  Mutations in GLIS3 are responsible for a rare syndrome with neonatal diabetes mellitus and congenital hypothyroidism.

Authors:  Valérie Senée; Claude Chelala; Sabine Duchatelet; Daorong Feng; Hervé Blanc; Jack-Christophe Cossec; Céline Charon; Marc Nicolino; Pascal Boileau; Douglas R Cavener; Pierre Bougnères; Doris Taha; Cécile Julier
Journal:  Nat Genet       Date:  2006-05-21       Impact factor: 38.330

8.  The effect of early, comprehensive genomic testing on clinical care in neonatal diabetes: an international cohort study.

Authors:  Elisa De Franco; Sarah E Flanagan; Jayne A L Houghton; Hana Lango Allen; Deborah J G Mackay; I Karen Temple; Sian Ellard; Andrew T Hattersley
Journal:  Lancet       Date:  2015-07-28       Impact factor: 79.321

9.  Diabetes Presentation in Infancy: High Risk of Diabetic Ketoacidosis.

Authors:  Lisa R Letourneau; David Carmody; Kristen Wroblewski; Anna M Denson; May Sanyoura; Rochelle N Naylor; Louis H Philipson; Siri Atma W Greeley
Journal:  Diabetes Care       Date:  2017-08-04       Impact factor: 19.112

10.  GATA6 mutations cause a broad phenotypic spectrum of diabetes from pancreatic agenesis to adult-onset diabetes without exocrine insufficiency.

Authors:  Elisa De Franco; Charles Shaw-Smith; Sarah E Flanagan; Maggie H Shepherd; Andrew T Hattersley; Sian Ellard
Journal:  Diabetes       Date:  2012-12-06       Impact factor: 9.461

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  1 in total

Review 1.  Monogenic Diabetes: From Genetic Insights to Population-Based Precision in Care. Reflections From a Diabetes Care Editors' Expert Forum.

Authors:  Matthew C Riddle; Louis H Philipson; Stephen S Rich; Annelie Carlsson; Paul W Franks; Siri Atma W Greeley; John J Nolan; Ewan R Pearson; Philip S Zeitler; Andrew T Hattersley
Journal:  Diabetes Care       Date:  2020-12       Impact factor: 19.112

  1 in total

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