Literature DB >> 29773230

Medications received by patients with juvenile dermatomyositis.

Takayuki Kishi1, Nastaran Bayat1, Michael M Ward2, Adam M Huber3, Lan Wu1, Gulnara Mamyrova4, Ira N Targoff5, William J Warren-Hicks6, Frederick W Miller1, Lisa G Rider7.   

Abstract

OBJECTIVE: Few controlled studies are available to guide treatment decisions in juvenile dermatomyositis (JDM). This study evaluated therapies received, changes of treatment over time, and factors associated with medication choices in JDM.
METHODS: We performed a retrospective analysis of the number and type of therapies and duration of treatment for 320 patients with JDM enrolled in a North American registry. Kaplan-Meier and logistic regression analysis were used to assess the association of demographic and clinical features and autoantibodies with medication usage.
RESULTS: High-dose oral prednisone was the primary therapy given to 99% of patients. 1997 was determined to be a threshold year for increasing usage of medications other than prednisone. The median time to half the initial oral prednisone dose was shorter in patients diagnosed after vs. before 1997 (10 vs. 19 months, P < 0.01). Patients received intravenous methylprednisolone (IVMP), methotrexate, intravenous immunoglobulin, antimalarial drugs, and combination therapy more frequently when diagnosed after 1997. IVMP was frequently received by patients with severe illness onset, anti-p155/140 (anti-TIF1) and anti-MJ (anti-NXP2) autoantibodies. Treatment with methotrexate was associated with older age at diagnosis and anti-MJ autoantibodies, while antimalarial therapy was associated with anti-p155/140 autoantibodies and mild onset severity.
CONCLUSION: Oral prednisone has been the mainstay of therapy in JDM, and prednisone was reduced faster in patients diagnosed after 1997 when there was also an increase in other medications. Specific medications received by patients with JDM correlated with year and age at diagnosis, myositis autoantibodies, onset severity, and illness features. Published by Elsevier Inc.

Entities:  

Keywords:  Juvenile dermatomyositis; Medications; Methotrexate; Myositis autoantibodies; Prednisone; Treatment

Mesh:

Substances:

Year:  2018        PMID: 29773230      PMCID: PMC6162169          DOI: 10.1016/j.semarthrit.2018.03.016

Source DB:  PubMed          Journal:  Semin Arthritis Rheum        ISSN: 0049-0172            Impact factor:   5.532


  40 in total

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2.  Consensus treatments for moderate juvenile dermatomyositis: beyond the first two months. Results of the second Childhood Arthritis and Rheumatology Research Alliance consensus conference.

Authors:  Adam M Huber; Angela B Robinson; Ann M Reed; Leslie Abramson; Sharon Bout-Tabaku; Ruy Carrasco; Megan Curran; Brian M Feldman; Harry Gewanter; Thomas Griffin; Kathleen Haines; Mark F Hoeltzel; Josephine Isgro; Philip Kahn; Bianca Lang; Patti Lawler; Bracha Shaham; Heinrike Schmeling; Rosie Scuccimarri; Michael Shishov; Elizabeth Stringer; Julie Wohrley; Norman T Ilowite; Carol Wallace
Journal:  Arthritis Care Res (Hoboken)       Date:  2012-04       Impact factor: 4.794

3.  Juvenile dermatomyositis: new insights and new treatment strategies.

Authors:  Neil Martin; Charles K Li; Lucy R Wedderburn
Journal:  Ther Adv Musculoskelet Dis       Date:  2012-02       Impact factor: 5.346

4.  Race, Income, and Disease Outcomes in Juvenile Dermatomyositis.

Authors:  Kathryn Phillippi; Mark Hoeltzel; Angela Byun Robinson; Susan Kim
Journal:  J Pediatr       Date:  2017-03-03       Impact factor: 4.406

5.  Drug therapy of the idiopathic inflammatory myopathies: predictors of response to prednisone, azathioprine, and methotrexate and a comparison of their efficacy.

Authors:  M M Joffe; L A Love; R L Leff; D D Fraser; I N Targoff; J E Hicks; P H Plotz; F W Miller
Journal:  Am J Med       Date:  1993-04       Impact factor: 4.965

Review 6.  The juvenile idiopathic inflammatory myopathies: pathogenesis, clinical and autoantibody phenotypes, and outcomes.

Authors:  L G Rider; K Nistala
Journal:  J Intern Med       Date:  2016-03-30       Impact factor: 8.989

7.  Prednisone versus prednisone plus ciclosporin versus prednisone plus methotrexate in new-onset juvenile dermatomyositis: a randomised trial.

Authors:  Nicolino Ruperto; Angela Pistorio; Sheila Oliveira; Francesco Zulian; Ruben Cuttica; Angelo Ravelli; Michel Fischbach; Bo Magnusson; Gary Sterba; Tadej Avcin; Karine Brochard; Fabrizia Corona; Frank Dressler; Valeria Gerloni; Maria T Apaz; Claudia Bracaglia; Adriana Cespedes-Cruz; Rolando Cimaz; Gerard Couillault; Rik Joos; Pierre Quartier; Ricardo Russo; Marc Tardieu; Nico Wulffraat; Blanca Bica; Pavla Dolezalova; Virginia Ferriani; Berit Flato; Ana G Bernard-Medina; Troels Herlin; Maria Trachana; Antonella Meini; Emma Allain-Launay; Clarissa Pilkington; Veronika Vargova; Carine Wouters; Simona Angioloni; Alberto Martini
Journal:  Lancet       Date:  2015-11-30       Impact factor: 79.321

8.  Pharmacokinetic study of oral prednisolone compared with intravenous methylprednisolone in patients with juvenile dermatomyositis.

Authors:  Kelly A Rouster-Stevens; Aneel Gursahaney; Ka-Leung Ngai; Jennifer A Daru; Lauren M Pachman
Journal:  Arthritis Rheum       Date:  2008-02-15

9.  Comparison of clinical features and drug therapies among European and Latin American patients with juvenile dermatomyositis.

Authors:  Dinara Guseinova; Alessandro Consolaro; Lucia Trail; Cristina Ferrari; Angela Pistorio; Nicolino Ruperto; Antonella Buoncompagni; Clarissa Pilkington; Susan Maillard; Sheila K Oliveira; Flavio Sztajnbok; Ruben Cuttica; Fabrizia Corona; Maria Martha Katsicas; Ricardo Russo; Virginia Ferriani; Ruben Burgos-Vargas; Eunice Solis-Vallejo; Marcia Bandeira; Vicente Baca; Claudia Saad-Magalhaes; Clovis A Silva; Roberto Barcellona; Luciana Breda; Rolando Cimaz; Romina Gallizzi; Rosaria Garozzo; Silvana Martino; Antonella Meini; Achille Stabile; Alberto Martini; Angelo Ravelli
Journal:  Clin Exp Rheumatol       Date:  2011-02-23       Impact factor: 4.473

10.  Is juvenile dermatomyositis a different disease in children up to three years of age at onset than in children above three years at onset? A retrospective review of 23 years of a single center's experience.

Authors:  Anjali Patwardhan; Robert Rennebohm; Igor Dvorchik; Charles H Spencer
Journal:  Pediatr Rheumatol Online J       Date:  2012-09-20       Impact factor: 3.054

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  8 in total

1.  Corticosteroid discontinuation, complete clinical response and remission in juvenile dermatomyositis.

Authors:  Takayuki Kishi; William Warren-Hicks; Nastaran Bayat; Ira N Targoff; Adam M Huber; Michael M Ward; Lisa G Rider
Journal:  Rheumatology (Oxford)       Date:  2021-05-14       Impact factor: 7.580

2.  Long-term outcomes in Juvenile Myositis patients.

Authors:  Vladislav Tsaltskan; Annette Aldous; Sam Serafi; Anna Yakovleva; Heidi Sami; Gulnara Mamyrova; Ira N Targoff; Adam Schiffenbauer; Frederick W Miller; Samuel J Simmens; Rodolfo Curiel; Olcay Y Jones; Lisa G Rider
Journal:  Semin Arthritis Rheum       Date:  2019-06-28       Impact factor: 5.532

3.  Anti-Ro52 autoantibodies are associated with interstitial lung disease and more severe disease in patients with juvenile myositis.

Authors:  Sara Sabbagh; Iago Pinal-Fernandez; Lisa G Rider; Andrew Lee Mammen; Takayuki Kishi; Ira N Targoff; Frederick W Miller
Journal:  Ann Rheum Dis       Date:  2019-04-24       Impact factor: 19.103

4.  Anti-MDA5 autoantibodies associated with juvenile dermatomyositis constitute a distinct phenotype in North America.

Authors:  Gulnara Mamyrova; Takayuki Kishi; Min Shi; Ira N Targoff; Adam M Huber; Rodolfo V Curiel; Frederick W Miller; Lisa G Rider
Journal:  Rheumatology (Oxford)       Date:  2021-04-06       Impact factor: 7.580

Review 5.  Updates on interferon in juvenile dermatomyositis: pathogenesis and therapy.

Authors:  Hanna Kim
Journal:  Curr Opin Rheumatol       Date:  2021-09-01       Impact factor: 4.941

6.  Serum biomarkers of glucocorticoid response and safety in anti-neutrophil cytoplasmic antibody-associated vasculitis and juvenile dermatomyositis.

Authors:  Laurie S Conklin; Peter A Merkel; Lauren M Pachman; Hemang Parikh; Shefa Tawalbeh; Jesse M Damsker; David D Cuthbertson; Gabrielle A Morgan; Paul A Monach; Yetrib Hathout; Kanneboyina Nagaraju; John van den Anker; Carol A McAlear; Eric P Hoffman
Journal:  Steroids       Date:  2018-10-21       Impact factor: 2.668

7.  Anti-mitochondrial autoantibodies are associated with cardiomyopathy, dysphagia, and features of more severe disease in adult-onset myositis.

Authors:  Sara E Sabbagh; Iago Pinal-Fernandez; Maria Casal-Dominguez; Jemima Albayda; Julie J Paik; Frederick W Miller; Lisa G Rider; Andrew L Mammen; Lisa Christopher-Stine
Journal:  Clin Rheumatol       Date:  2021-04-13       Impact factor: 2.980

8.  Juvenile Dermatomyositis: New Clues to Diagnosis and Therapy.

Authors:  Lauren M Pachman; Brian E Nolan; Deidre DeRanieri; Amer M Khojah
Journal:  Curr Treatm Opt Rheumatol       Date:  2021-02-06
  8 in total

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