Literature DB >> 29635265

Voretigene neparvovec-rzyl (Luxturna) for inherited retinal dystrophy.

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Abstract

Entities:  

Keywords:  adverse effects; dosage; drug interactions; efficacy; eye; safety

Mesh：

Substances：

Year:  2018        PMID： 29635265

Source DB:  PubMed          Journal:  Med Lett Drugs Ther        ISSN： 0025-732X            Impact factor:   1.909


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  13 in total

1.  Five Years of Successful Inducible Transgene Expression Following Locoregional Adeno-Associated Virus Delivery in Nonhuman Primates with No Detectable Immunity.

Authors:  Mickaël Guilbaud; Marie Devaux; Celia Couzinié; Johanne Le Duff; Alice Toromanoff; Céline Vandamme; Nicolas Jaulin; Gwladys Gernoux; Thibaut Larcher; Philippe Moullier; Caroline Le Guiner; Oumeya Adjali
Journal:  Hum Gene Ther       Date:  2019-04-16       Impact factor: 5.695

Review 2.  RPGR gene therapy presents challenges in cloning the coding sequence.

Authors:  Cristina Martinez-Fernandez De La Camara; Jasmina Cehajic-Kapetanovic; Robert E MacLaren
Journal:  Expert Opin Biol Ther       Date:  2019-10-20       Impact factor: 4.388

3.  Long-Term Effects of Gene Therapy in a Novel Mouse Model of Human MFRP-Associated Retinopathy.

Authors:  Anil Chekuri; Bhubanananda Sahu; Venkata Ramana Murthy Chavali; Marina Voronchikhina; Angel Soto-Hermida; John J Suk; Akhila N Alapati; Dirk-Uwe Bartsch; Raul Ayala-Ramirez; Juan C Zenteno; Astra Dinculescu; Monica M Jablonski; Shyamanga Borooah; Radha Ayyagari
Journal:  Hum Gene Ther       Date:  2019-01-16       Impact factor: 5.695

Review 4.  Restoring Vision to the Blind with Chemical Photoswitches.

Authors:  Ivan Tochitsky; Michael A Kienzler; Ehud Isacoff; Richard H Kramer
Journal:  Chem Rev       Date:  2018-06-06       Impact factor: 60.622

5.  Dual ABCA4-AAV Vector Treatment Reduces Pathogenic Retinal A2E Accumulation in a Mouse Model of Autosomal Recessive Stargardt Disease.

Authors:  Frank M Dyka; Laurie L Molday; Vince A Chiodo; Robert S Molday; William W Hauswirth
Journal:  Hum Gene Ther       Date:  2019-09-30       Impact factor: 5.695

6.  A short hepatitis C virus NS5A peptide expression by AAV vector modulates human T cell activation and reduces vector immunogenicity.

Authors:  Winston Colon-Moran; Alan Baer; Gauri Lamture; Jack T Stapleton; Joseph W Fischer; Nirjal Bhattarai
Journal:  Gene Ther       Date:  2021-11-11       Impact factor: 4.184

7.  GPR108 Is a Highly Conserved AAV Entry Factor.

Authors:  Amanda M Dudek; Nerea Zabaleta; Eric Zinn; Sirika Pillay; James Zengel; Caryn Porter; Jennifer Santos Franceschini; Reynette Estelien; Jan E Carette; Guo Ling Zhou; Luk H Vandenberghe
Journal:  Mol Ther       Date:  2019-11-13       Impact factor: 11.454

8.  Successful gene therapy requires targeting the vast majority of cancer cells.

Authors:  Takuya Sagara; Marija Debeljak; Chapman M Wright; Nicole M Anders; Hong Liang; Michelle A Rudek; Marc Ostermeier; James R Eshleman; Yoshihisa Matsushita
Journal:  Cancer Biol Ther       Date:  2020-09-30       Impact factor: 4.742

9.  Generation of a 3D Liver Model Comprising Human Extracellular Matrix in an Alginate/Gelatin-Based Bioink by Extrusion Bioprinting for Infection and Transduction Studies.

Authors:  Thomas Hiller; Johanna Berg; Laura Elomaa; Viola Röhrs; Imran Ullah; Katrin Schaar; Ann-Christin Dietrich; Munir A Al-Zeer; Andreas Kurtz; Andreas C Hocke; Stefan Hippenstiel; Henry Fechner; Marie Weinhart; Jens Kurreck
Journal:  Int J Mol Sci       Date:  2018-10-12       Impact factor: 5.923

10.  Viral vectors as a novel tool for clinical and neuropsychiatric research applications.

Authors:  Yao Wang; Zhiwei Hu; Peijun Ju; Shan Yin; Fujie Wang; Oudong Pan; Jinghong Chen
Journal:  Gen Psychiatr       Date:  2018-10-25
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