Literature DB >> 29515186

Systemic sclerosis: Autologous HSCT is efficacious, but can we make it safer?

Richard K Burt1, Dominique Farge2.   

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Year:  2018        PMID: 29515186     DOI: 10.1038/nrrheum.2018.34

Source DB:  PubMed          Journal:  Nat Rev Rheumatol        ISSN: 1759-4790            Impact factor:   20.543


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  9 in total

1.  Hematopoietic stem cell transplantation for systemic sclerosis: if you are confused, remember: "it is a matter of the heart".

Authors:  Richard K Burt; Sanjiv J Shah; Mihai Gheorghiade; Eric Ruderman; James Schroeder
Journal:  J Rheumatol       Date:  2012-02       Impact factor: 4.666

2.  Cardiac assessment before stem cell transplantation for systemic sclerosis.

Authors:  Richard K Burt; Maria Carolina Oliveira; Sanjiv J Shah
Journal:  JAMA       Date:  2014-11-05       Impact factor: 56.272

3.  Evolution, trends, outcomes, and economics of hematopoietic stem cell transplantation in severe autoimmune diseases.

Authors:  John A Snowden; Manuela Badoglio; Myriam Labopin; Sebastian Giebel; Eoin McGrath; Zora Marjanovic; Joachim Burman; John Moore; Montserrat Rovira; Nico M Wulffraat; Majid Kazmi; Raffaella Greco; Emilian Snarski; Tomas Kozak; Kirill Kirgizov; Tobias Alexander; Peter Bader; Riccardo Saccardi; Dominique Farge
Journal:  Blood Adv       Date:  2017-12-20

4.  Myeloablative Autologous Stem-Cell Transplantation for Severe Scleroderma.

Authors:  Keith M Sullivan; Ellen A Goldmuntz; Lynette Keyes-Elstein; Peter A McSweeney; Ashley Pinckney; Beverly Welch; Maureen D Mayes; Richard A Nash; Leslie J Crofford; Barry Eggleston; Sharon Castina; Linda M Griffith; Julia S Goldstein; Dennis Wallace; Oana Craciunescu; Dinesh Khanna; Rodney J Folz; Jonathan Goldin; E William St Clair; James R Seibold; Kristine Phillips; Shin Mineishi; Robert W Simms; Karen Ballen; Mark H Wener; George E Georges; Shelly Heimfeld; Chitra Hosing; Stephen Forman; Suzanne Kafaja; Richard M Silver; Leroy Griffing; Jan Storek; Sharon LeClercq; Richard Brasington; Mary E Csuka; Christopher Bredeson; Carolyn Keever-Taylor; Robyn T Domsic; M Bashar Kahaleh; Thomas Medsger; Daniel E Furst
Journal:  N Engl J Med       Date:  2018-01-04       Impact factor: 91.245

5.  Autologous non-myeloablative haemopoietic stem-cell transplantation compared with pulse cyclophosphamide once per month for systemic sclerosis (ASSIST): an open-label, randomised phase 2 trial.

Authors:  Richard K Burt; Sanjiv J Shah; Karin Dill; Thomas Grant; Mihai Gheorghiade; James Schroeder; Robert Craig; Ikuo Hirano; Karin Marshall; Eric Ruderman; Borko Jovanovic; Francesca Milanetti; Sandeep Jain; Kristin Boyce; Amy Morgan; James Carr; Walter Barr
Journal:  Lancet       Date:  2011-07-21       Impact factor: 79.321

6.  Autologous hematopoietic stem cell transplantation for autoimmune diseases: an observational study on 12 years' experience from the European Group for Blood and Marrow Transplantation Working Party on Autoimmune Diseases.

Authors:  Dominique Farge; Myriam Labopin; Alan Tyndall; Athanasios Fassas; Gian Luigi Mancardi; Jaap Van Laar; Jian Ouyang; Tomas Kozak; John Moore; Ina Kötter; Virginie Chesnel; Alberto Marmont; Alois Gratwohl; Riccardo Saccardi
Journal:  Haematologica       Date:  2009-09-22       Impact factor: 9.941

7.  Cardiac involvement and treatment-related mortality after non-myeloablative haemopoietic stem-cell transplantation with unselected autologous peripheral blood for patients with systemic sclerosis: a retrospective analysis.

Authors:  Richard K Burt; Maria Carolina Oliveira; Sanjiv J Shah; Daniela A Moraes; Belinda Simoes; Mihai Gheorghiade; James Schroeder; Eric Ruderman; Dominique Farge; Z Jessie Chai; Zora Marjanovic; Sandeep Jain; Amy Morgan; Francesca Milanetti; Xiaoqiang Han; Borko Jovanovic; Irene B Helenowski; Julio Voltarelli
Journal:  Lancet       Date:  2013-01-28       Impact factor: 79.321

Review 8.  Cardiopulmonary assessment of patients with systemic sclerosis for hematopoietic stem cell transplantation: recommendations from the European Society for Blood and Marrow Transplantation Autoimmune Diseases Working Party and collaborating partners.

Authors:  D Farge; R K Burt; M-C Oliveira; E Mousseaux; M Rovira; Z Marjanovic; J de Vries-Bouwstra; N Del Papa; R Saccardi; S J Shah; D C Lee; C Denton; T Alexander; D G Kiely; J A Snowden
Journal:  Bone Marrow Transplant       Date:  2017-05-22       Impact factor: 5.483

9.  Autologous hematopoietic stem cell transplantation vs intravenous pulse cyclophosphamide in diffuse cutaneous systemic sclerosis: a randomized clinical trial.

Authors:  Jacob M van Laar; Dominique Farge; Jacob K Sont; Kamran Naraghi; Zora Marjanovic; Jérôme Larghero; Annemie J Schuerwegh; Erik W A Marijt; Madelon C Vonk; Anton V Schattenberg; Marco Matucci-Cerinic; Alexandre E Voskuyl; Arjan A van de Loosdrecht; Thomas Daikeler; Ina Kötter; Marc Schmalzing; Thierry Martin; Bruno Lioure; Stefan M Weiner; Alexander Kreuter; Christophe Deligny; Jean-Marc Durand; Paul Emery; Klaus P Machold; Francoise Sarrot-Reynauld; Klaus Warnatz; Daniel F P Adoue; Joël Constans; Hans-Peter Tony; Nicoletta Del Papa; Athanasios Fassas; Andrea Himsel; David Launay; Andrea Lo Monaco; Pierre Philippe; Isabelle Quéré; Éric Rich; Rene Westhovens; Bridget Griffiths; Riccardo Saccardi; Frank H van den Hoogen; Willem E Fibbe; Gérard Socié; Alois Gratwohl; Alan Tyndall
Journal:  JAMA       Date:  2014-06-25       Impact factor: 56.272

  9 in total
  5 in total

1.  CD34-selected versus unmanipulated autologous haematopoietic stem cell transplantation in the treatment of severe systemic sclerosis: a post hoc analysis of a phase I/II clinical trial conducted in Japan.

Authors:  Masahiro Ayano; Hiroshi Tsukamoto; Hiroki Mitoma; Yasutaka Kimoto; Mitsuteru Akahoshi; Yojiro Arinobu; Toshihiro Miyamoto; Takahiko Horiuchi; Hiroaki Niiro; Koji Nagafuji; Mine Harada; Koichi Akashi
Journal:  Arthritis Res Ther       Date:  2019-01-22       Impact factor: 5.156

Review 2.  Mesenchymal stem cell as a novel approach to systemic sclerosis; current status and future perspectives.

Authors:  Mina Abedi; Sepideh Alavi-Moghadam; Moloud Payab; Parisa Goodarzi; Fereshteh Mohamadi-Jahani; Forough Azam Sayahpour; Bagher Larijani; Babak Arjmand
Journal:  Cell Regen       Date:  2020-12-01

3.  Case Report: Chemotherapy-Associated Systemic Sclerosis: Is DNA Damage to Blame?

Authors:  Amy X Du; Robert Gniadecki; Jan Storek; Mohamed Osman
Journal:  Front Med (Lausanne)       Date:  2022-02-24

Review 4.  New Era in Systemic Sclerosis Treatment: Recently Approved Therapeutics.

Authors:  Satoshi Ebata; Asako Yoshizaki-Ogawa; Shinichi Sato; Ayumi Yoshizaki
Journal:  J Clin Med       Date:  2022-08-08       Impact factor: 4.964

Review 5.  Mesenchymal Stromal Cells Based Therapy in Systemic Sclerosis: Rational and Challenges.

Authors:  Juliette Peltzer; Marc Aletti; Nadira Frescaline; Elodie Busson; Jean-Jacques Lataillade; Christophe Martinaud
Journal:  Front Immunol       Date:  2018-09-13       Impact factor: 7.561

  5 in total

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