Mark G Weiner1. 1. Department of Clinical Sciences, Lewis Katz School of Medicine at Temple University, Philadelphia, PA. Electronic address: Mark.weiner@tuhs.temple.edu.
Authors: Reka Maria Blazsik; Patrick Emanuel Beeler; Karol Tarcak; Marcus Cheetham; Viktor von Wyl; Holger Dressel Journal: Orphanet J Rare Dis Date: 2021-02-27 Impact factor: 4.123