Literature DB >> 28944740

A novel nonviral gene delivery system for treating Leber's congenital amaurosis.

Da Sun1, Rebecca M Schur1, Zheng-Rong Lu1,2.   

Abstract

Entities:  

Keywords:  ECO; LCA; RPE65; gene therapy; nanoparticle; nonviral; retina

Mesh：

Substances：

Year:  2017        PMID： 28944740     DOI： 10.4155/tde-2017-0072

Source DB:  PubMed          Journal:  Ther Deliv        ISSN： 2041-5990


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  3 in total

1.  Non-viral Gene Therapy for Stargardt Disease with ECO/pRHO-ABCA4 Self-Assembled Nanoparticles.

Authors:  Da Sun; Rebecca M Schur; Avery E Sears; Song-Qi Gao; Amita Vaidya; Wenyu Sun; Akiko Maeda; Timothy Kern; Krzysztof Palczewski; Zheng-Rong Lu
Journal:  Mol Ther       Date:  2019-09-12       Impact factor: 11.454

2.  Synthesis and Evaluation of pH-Sensitive Multifunctional Lipids for Efficient Delivery of CRISPR/Cas9 in Gene Editing.

Authors:  Da Sun; Zhanhu Sun; Hongfa Jiang; Amita M Vaidya; Rui Xin; Nadia R Ayat; Andrew L Schilb; Peter L Qiao; Zheng Han; Amirreza Naderi; Zheng-Rong Lu
Journal:  Bioconjug Chem       Date:  2019-01-18       Impact factor: 4.774

Review 3.  Directing the Way-Receptor and Chemical Targeting Strategies for Nucleic Acid Delivery.

Authors:  Ricarda Carolin Steffens; Ernst Wagner
Journal:  Pharm Res       Date:  2022-09-15       Impact factor: 4.580
  3 in total

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