Literature DB >> 28888564

Everolimus for the Treatment of Tuberous Sclerosis Complex-Related Cardiac Rhabdomyomas in Pediatric Patients.

Nagib Dahdah1.   

Abstract

Entities:  

Keywords:  cardiac tumors; hamartomas; infants; mTOR inhibition

Mesh:

Substances:

Year:  2017        PMID: 28888564     DOI: 10.1016/j.jpeds.2017.06.076

Source DB:  PubMed          Journal:  J Pediatr        ISSN: 0022-3476            Impact factor:   4.406


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  5 in total

Review 1.  Monitoring and Managing Patients with Tuberous Sclerosis Complex: Current State of Knowledge.

Authors:  Inês Gomes; Joana Jesus Ribeiro; Filipe Palavra
Journal:  J Multidiscip Healthc       Date:  2022-07-14

Review 2.  Perfect match: mTOR inhibitors and tuberous sclerosis complex.

Authors:  Cong Luo; Wen-Rui Ye; Wei Shi; Ping Yin; Chen Chen; Yun-Bo He; Min-Feng Chen; Xiong-Bin Zu; Yi Cai
Journal:  Orphanet J Rare Dis       Date:  2022-03-04       Impact factor: 4.123

3.  Use of Everolimus to treat cardiac rhabdomyomas and incessant arrhythmias in a newborn: Benefits and complications.

Authors:  Eyal Sagiv; Sathish Mallenahalli Chikkabyrappa; Jeffrey Conwell; Mark Lewin; Terrence Un Hoong Chun
Journal:  Ann Pediatr Cardiol       Date:  2022-06-14

4.  Incidence of tuberous sclerosis and age at first diagnosis: new data and emerging trends from a national, prospective surveillance study.

Authors:  Daniel Ebrahimi-Fakhari; Lilian Lisa Mann; Martin Poryo; Norbert Graf; Rüdiger von Kries; Beate Heinrich; Darius Ebrahimi-Fakhari; Marina Flotats-Bastardas; Ludwig Gortner; Michael Zemlin; Sascha Meyer
Journal:  Orphanet J Rare Dis       Date:  2018-07-17       Impact factor: 4.123

5.  Efficacy, Retention and Tolerability of Everolimus in Patients with Tuberous Sclerosis Complex: A Survey-Based Study on Patients' Perspectives.

Authors:  Laurent M Willems; Felix Rosenow; Susanne Schubert-Bast; Gerhard Kurlemann; Johann Philipp Zöllner; Thomas Bast; Astrid Bertsche; Ulrich Bettendorf; Daniel Ebrahimi-Fakhari; Janina Grau; Andreas Hahn; Hans Hartmann; Christoph Hertzberg; Frauke Hornemann; Ilka Immisch; Julia Jacobs; Karl Martin Klein; Kerstin A Klotz; Gerhard Kluger; Susanne Knake; Markus Knuf; Klaus Marquard; Thomas Mayer; Sascha Meyer; Hiltrud Muhle; Karen Müller-Schlüter; Felix von Podewils; Susanne Ruf; Matthias Sauter; Hannah Schäfer; Jan-Ulrich Schlump; Steffen Syrbe; Charlotte Thiels; Regina Trollmann; Adelheid Wiemer-Kruel; Bernd Wilken; Bianca Zukunft; Adam Strzelczyk
Journal:  CNS Drugs       Date:  2021-07-17       Impact factor: 5.749

  5 in total

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