Literature DB >> 28303022

To cleave or not to cleave: therapeutic gene editing with and without programmable nucleases.

Tod M Woolf1, Channabasavaiah B Gurumurthy2, Frederick Boyce3, Eric B Kmiec4.   

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Year:  2017        PMID： 28303022     DOI： 10.1038/nrd.2017.42

Source DB:  PubMed          Journal:  Nat Rev Drug Discov        ISSN： 1474-1776            Impact factor:   84.694


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  12 in total

Review 1.  Regulation of targeted gene repair by intrinsic cellular processes.

Authors:  Julia U Engstrom; Takayuki Suzuki; Eric B Kmiec
Journal:  Bioessays       Date:  2009-02       Impact factor: 4.345

Review 2.  Therapeutic repair of mutated nucleic acid sequences.

Authors:  T M Woolf
Journal:  Nat Biotechnol       Date:  1998-04       Impact factor: 54.908

Review 3.  Therapeutic genome editing: prospects and challenges.

Authors:  David Benjamin Turitz Cox; Randall Jeffrey Platt; Feng Zhang
Journal:  Nat Med       Date:  2015-02       Impact factor: 53.440

4.  LNA modification of single-stranded DNA oligonucleotides allows subtle gene modification in mismatch-repair-proficient cells.

Authors:  Thomas W van Ravesteyn; Marleen Dekker; Alexander Fish; Titia K Sixma; Astrid Wolters; Rob J Dekker; Hein P J Te Riele
Journal:  Proc Natl Acad Sci U S A       Date:  2016-03-07       Impact factor: 11.205

5.  Stable gene targeting in human cells using single-strand oligonucleotides with modified bases.

Authors:  Xavier Rios; Adrian W Briggs; Danos Christodoulou; Josh M Gorham; Jonathan G Seidman; George M Church
Journal:  PLoS One       Date:  2012-05-14       Impact factor: 3.240

6.  Promoterless gene targeting without nucleases ameliorates haemophilia B in mice.

Authors:  A Barzel; N K Paulk; Y Shi; Y Huang; K Chu; F Zhang; P N Valdmanis; L P Spector; M H Porteus; K M Gaensler; M A Kay
Journal:  Nature       Date:  2014-10-29       Impact factor: 49.962

7.  Engineering and optimising deaminase fusions for genome editing.

Authors:  Luhan Yang; Adrian W Briggs; Wei Leong Chew; Prashant Mali; Marc Guell; John Aach; Daniel Bryan Goodman; David Cox; Yinan Kan; Emal Lesha; Venkataramanan Soundararajan; Feng Zhang; George Church
Journal:  Nat Commun       Date:  2016-11-02       Impact factor: 14.919

8.  Enhanced gene repair mediated by methyl-CpG-modified single-stranded oligonucleotides.

Authors:  Carmen Bertoni; Arjun Rustagi; Thomas A Rando
Journal:  Nucleic Acids Res       Date:  2009-12       Impact factor: 16.971

9.  Nanoparticles that deliver triplex-forming peptide nucleic acid molecules correct F508del CFTR in airway epithelium.

Authors:  Nicole Ali McNeer; Kavitha Anandalingam; Rachel J Fields; Christina Caputo; Sascha Kopic; Anisha Gupta; Elias Quijano; Lee Polikoff; Yong Kong; Raman Bahal; John P Geibel; Peter M Glazer; W Mark Saltzman; Marie E Egan
Journal:  Nat Commun       Date:  2015-04-27       Impact factor: 14.919

10.  Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage.

Authors:  Alexis C Komor; Yongjoo B Kim; Michael S Packer; John A Zuris; David R Liu
Journal:  Nature       Date:  2016-04-20       Impact factor: 49.962
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  5 in total

1.  Kinetics of Nuclear Uptake and Site-Specific DNA Cleavage during CRISPR-Directed Gene Editing in Solid Tumor Cells.

Authors:  Kelly Banas; Natalia Rivera-Torres; Pawel Bialk; Byung-Chun Yoo; Eric B Kmiec
Journal:  Mol Cancer Res       Date:  2020-03-17       Impact factor: 5.852

2.  Precise and efficient nucleotide substitution near genomic nick via noncanonical homology-directed repair.

Authors:  Kazuhiro Nakajima; Yue Zhou; Akiko Tomita; Yoshihiro Hirade; Channabasavaiah B Gurumurthy; Shinichiro Nakada
Journal:  Genome Res       Date:  2017-12-22       Impact factor: 9.043

3.  Efficient Delivery and Nuclear Uptake Is Not Sufficient to Detect Gene Editing in CD34+ Cells Directed by a Ribonucleoprotein Complex.

Authors:  Shirin R Modarai; Dula Man; Pawel Bialk; Natalia Rivera-Torres; Kevin Bloh; Eric B Kmiec
Journal:  Mol Ther Nucleic Acids       Date:  2018-02-07       Impact factor: 8.886

Review 4.  Generating mouse models for biomedical research: technological advances.

Authors:  Channabasavaiah B Gurumurthy; Kevin C Kent Lloyd
Journal:  Dis Model Mech       Date:  2019-01-08       Impact factor: 5.758

5.  CRISPR-Directed In Vitro Gene Editing of Plasmid DNA Catalyzed by Cpf1 (Cas12a) Nuclease and a Mammalian Cell-Free Extract.

Authors:  Brett M Sansbury; Amanda M Wagner; Erez Nitzan; Gabi Tarcic; Eric B Kmiec
Journal:  CRISPR J       Date:  2018-04-01
  5 in total

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