Literature DB >> 28117345

A non-viral CRISPR/Cas9 delivery system for therapeutically targeting HBV DNA and pcsk9 in vivo.

Chao Jiang1, Miao Mei1, Bin Li2, Xiurui Zhu3, Wenhong Zu1, Yujie Tian1, Qiannan Wang1, Yong Guo3, Yizhou Dong2, Xu Tan1.   

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Year:  2017        PMID: 28117345      PMCID: PMC5339835          DOI: 10.1038/cr.2017.16

Source DB:  PubMed          Journal:  Cell Res        ISSN: 1001-0602            Impact factor:   25.617


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  15 in total

1.  Inhibition of hepatitis B virus by the CRISPR/Cas9 system via targeting the conserved regions of the viral genome.

Authors:  Xing Liu; Ruidong Hao; Shuliang Chen; Deyin Guo; Yu Chen
Journal:  J Gen Virol       Date:  2015-04-22       Impact factor: 3.891

2.  Targeting hepatitis B virus cccDNA by CRISPR/Cas9 nuclease efficiently inhibits viral replication.

Authors:  Chunsheng Dong; Liang Qu; Haoyi Wang; Lin Wei; Yuansu Dong; Sidong Xiong
Journal:  Antiviral Res       Date:  2015-04-03       Impact factor: 5.970

Review 3.  Targeting hepatitis B virus cccDNA using CRISPR/Cas9.

Authors:  Edward M Kennedy; Anand V R Kornepati; Bryan R Cullen
Journal:  Antiviral Res       Date:  2015-10-22       Impact factor: 5.970

4.  Hydrodynamic injection of viral DNA: a mouse model of acute hepatitis B virus infection.

Authors:  Priscilla L Yang; Alana Althage; Josan Chung; Francis V Chisari
Journal:  Proc Natl Acad Sci U S A       Date:  2002-10-08       Impact factor: 11.205

5.  Recombinant covalently closed circular hepatitis B virus DNA induces prolonged viral persistence in immunocompetent mice.

Authors:  Zhihua Qi; Gaiyun Li; Hao Hu; Chunhui Yang; Xiaoming Zhang; Qibin Leng; Youhua Xie; Demin Yu; Xinxin Zhang; Yueqiu Gao; Ke Lan; Qiang Deng
Journal:  J Virol       Date:  2014-05-07       Impact factor: 5.103

6.  An Orthogonal Array Optimization of Lipid-like Nanoparticles for mRNA Delivery in Vivo.

Authors:  Bin Li; Xiao Luo; Binbin Deng; Junfeng Wang; David W McComb; Yimin Shi; Karin M L Gaensler; Xu Tan; Amy L Dunn; Bryce A Kerlin; Yizhou Dong
Journal:  Nano Lett       Date:  2015-11-06       Impact factor: 11.189

7.  The CRISPR/Cas9 System Facilitates Clearance of the Intrahepatic HBV Templates In Vivo.

Authors:  Su-Ru Lin; Hung-Chih Yang; Yi-Ting Kuo; Chun-Jen Liu; Ta-Yu Yang; Ku-Chun Sung; You-Yu Lin; Hurng-Yi Wang; Chih-Chiang Wang; Yueh-Chi Shen; Fang-Yi Wu; Jia-Horng Kao; Ding-Shinn Chen; Pei-Jer Chen
Journal:  Mol Ther Nucleic Acids       Date:  2014-08-19       Impact factor: 10.183

8.  In vivo genome editing using Staphylococcus aureus Cas9.

Authors:  F Ann Ran; Le Cong; Winston X Yan; David A Scott; Jonathan S Gootenberg; Andrea J Kriz; Bernd Zetsche; Ophir Shalem; Xuebing Wu; Kira S Makarova; Eugene V Koonin; Phillip A Sharp; Feng Zhang
Journal:  Nature       Date:  2015-04-01       Impact factor: 49.962

9.  HBVdb: a knowledge database for Hepatitis B Virus.

Authors:  Juliette Hayer; Fanny Jadeau; Gilbert Deléage; Alan Kay; Fabien Zoulim; Christophe Combet
Journal:  Nucleic Acids Res       Date:  2012-11-03       Impact factor: 16.971

10.  Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo.

Authors:  Hao Yin; Chun-Qing Song; Joseph R Dorkin; Lihua J Zhu; Yingxiang Li; Qiongqiong Wu; Angela Park; Junghoon Yang; Sneha Suresh; Aizhan Bizhanova; Ankit Gupta; Mehmet F Bolukbasi; Stephen Walsh; Roman L Bogorad; Guangping Gao; Zhiping Weng; Yizhou Dong; Victor Koteliansky; Scot A Wolfe; Robert Langer; Wen Xue; Daniel G Anderson
Journal:  Nat Biotechnol       Date:  2016-02-01       Impact factor: 54.908

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  84 in total

Review 1.  Non-viral delivery systems for CRISPR/Cas9-based genome editing: Challenges and opportunities.

Authors:  Ling Li; Shuo Hu; Xiaoyuan Chen
Journal:  Biomaterials       Date:  2018-04-18       Impact factor: 12.479

Review 2.  Delivering the Messenger: Advances in Technologies for Therapeutic mRNA Delivery.

Authors:  Piotr S Kowalski; Arnab Rudra; Lei Miao; Daniel G Anderson
Journal:  Mol Ther       Date:  2019-02-19       Impact factor: 11.454

Review 3.  Transfection by cationic gemini lipids and surfactants.

Authors:  M Damen; A J J Groenen; S F M van Dongen; R J M Nolte; B J Scholte; M C Feiters
Journal:  Medchemcomm       Date:  2018-07-17       Impact factor: 3.597

4.  A Potent Branched-Tail Lipid Nanoparticle Enables Multiplexed mRNA Delivery and Gene Editing In Vivo.

Authors:  Khalid A Hajj; Jilian R Melamed; Namit Chaudhary; Nicholas G Lamson; Rebecca L Ball; Saigopalakrishna S Yerneni; Kathryn A Whitehead
Journal:  Nano Lett       Date:  2020-06-09       Impact factor: 11.189

5.  Synthetic mRNA nanoparticle-mediated restoration of p53 tumor suppressor sensitizes p53-deficient cancers to mTOR inhibition.

Authors:  Na Kong; Wei Tao; Xiang Ling; Junqing Wang; Yuling Xiao; Sanjun Shi; Xiaoyuan Ji; Aram Shajii; Silvia Tian Gan; Na Yoon Kim; Dan G Duda; Tian Xie; Omid C Farokhzad; Jinjun Shi
Journal:  Sci Transl Med       Date:  2019-12-18       Impact factor: 17.956

6.  CRISPR-delivery particles targeting nuclear receptor-interacting protein 1 (Nrip1) in adipose cells to enhance energy expenditure.

Authors:  Yuefei Shen; Jessica L Cohen; Sarah M Nicoloro; Mark Kelly; Batuhan Yenilmez; Felipe Henriques; Emmanouela Tsagkaraki; Yvonne J K Edwards; Xiaodi Hu; Randall H Friedline; Jason K Kim; Michael P Czech
Journal:  J Biol Chem       Date:  2018-09-06       Impact factor: 5.157

Review 7.  Engineering the Delivery System for CRISPR-Based Genome Editing.

Authors:  Zachary Glass; Matthew Lee; Yamin Li; Qiaobing Xu
Journal:  Trends Biotechnol       Date:  2018-01-02       Impact factor: 19.536

Review 8.  Nanoscale platforms for messenger RNA delivery.

Authors:  Bin Li; Xinfu Zhang; Yizhou Dong
Journal:  Wiley Interdiscip Rev Nanomed Nanobiotechnol       Date:  2018-05-04

9.  Targeted Delivery of CRISPR/Cas9-Mediated Cancer Gene Therapy via Liposome-Templated Hydrogel Nanoparticles.

Authors:  Zeming Chen; Fuyao Liu; Yanke Chen; Jun Liu; Xiaoying Wang; Ann T Chen; Gang Deng; Hongyi Zhang; Jie Liu; Zhangyong Hong; Jiangbing Zhou
Journal:  Adv Funct Mater       Date:  2017-10-16       Impact factor: 18.808

10.  Engineered materials for in vivo delivery of genome-editing machinery.

Authors:  Sheng Tong; Buhle Moyo; Ciaran M Lee; Kam Leong; Gang Bao
Journal:  Nat Rev Mater       Date:  2019-10-04       Impact factor: 66.308

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