Literature DB >> 28066780

Efficient CRISPR/Cas9-based gene correction in induced pluripotent stem cells established from fibroblasts of patients with sickle cell disease.

Masahiro Sato1, Issei Saitoh2, Emi Inada3.   

Abstract

Entities:  

Year:  2016        PMID： 28066780      PMCID： PMC5182212          DOI： 10.21037/sci.2016.11.05

Source DB:  PubMed          Journal:  Stem Cell Investig        ISSN： 2306-9759


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  18 in total

1.  Generation of isogenic pluripotent stem cells differing exclusively at two early onset Parkinson point mutations.

Authors:  Frank Soldner; Josée Laganière; Albert W Cheng; Dirk Hockemeyer; Qing Gao; Raaji Alagappan; Vikram Khurana; Lawrence I Golbe; Richard H Myers; Susan Lindquist; Lei Zhang; Dmitry Guschin; Lauren K Fong; B Joseph Vu; Xiangdong Meng; Fyodor D Urnov; Edward J Rebar; Philip D Gregory; H Steve Zhang; Rudolf Jaenisch
Journal:  Cell       Date:  2011-07-14       Impact factor: 41.582

2.  Site-specific gene correction of a point mutation in human iPS cells derived from an adult patient with sickle cell disease.

Authors:  Jizhong Zou; Prashant Mali; Xiaosong Huang; Sarah N Dowey; Linzhao Cheng
Journal:  Blood       Date:  2011-08-31       Impact factor: 22.113

3.  In situ genetic correction of the sickle cell anemia mutation in human induced pluripotent stem cells using engineered zinc finger nucleases.

Authors:  Vittorio Sebastiano; Morgan L Maeder; James F Angstman; Bahareh Haddad; Cyd Khayter; Dana T Yeo; Mathew J Goodwin; John S Hawkins; Cherie L Ramirez; Luis F Z Batista; Steven E Artandi; Marius Wernig; J Keith Joung
Journal:  Stem Cells       Date:  2011-11       Impact factor: 6.277

Review 4.  Strategies and new developments in the generation of patient-specific pluripotent stem cells.

Authors:  Shinya Yamanaka
Journal:  Cell Stem Cell       Date:  2007-06-07       Impact factor: 24.633

5.  Naïve Induced Pluripotent Stem Cells Generated From β-Thalassemia Fibroblasts Allow Efficient Gene Correction With CRISPR/Cas9.

Authors:  Yuanyuan Yang; Xiaobai Zhang; Li Yi; Zhenzhen Hou; Jiayu Chen; Xiaochen Kou; Yanhong Zhao; Hong Wang; Xiao-Fang Sun; Cizhong Jiang; Yixuan Wang; Shaorong Gao
Journal:  Stem Cells Transl Med       Date:  2015-12-16       Impact factor: 6.940

6.  Derivation of naive human embryonic stem cells.

Authors:  Carol B Ware; Angelique M Nelson; Brigham Mecham; Jennifer Hesson; Wenyu Zhou; Erica C Jonlin; Antonio J Jimenez-Caliani; Xinxian Deng; Christopher Cavanaugh; Savannah Cook; Paul J Tesar; Jeffrey Okada; Lilyana Margaretha; Henrik Sperber; Michael Choi; C Anthony Blau; Piper M Treuting; R David Hawkins; Vincenzo Cirulli; Hannele Ruohola-Baker
Journal:  Proc Natl Acad Sci U S A       Date:  2014-03-12       Impact factor: 11.205

7.  PDGF-AB and 5-Azacytidine induce conversion of somatic cells into tissue-regenerative multipotent stem cells.

Authors:  Vashe Chandrakanthan; Avani Yeola; Jair C Kwan; Rema A Oliver; Qiao Qiao; Young Chan Kang; Peter Zarzour; Dominik Beck; Lies Boelen; Ashwin Unnikrishnan; Jeanette E Villanueva; Andrea C Nunez; Kathy Knezevic; Cintia Palu; Rabab Nasrallah; Michael Carnell; Alex Macmillan; Renee Whan; Yan Yu; Philip Hardy; Shane T Grey; Amadeus Gladbach; Fabien Delerue; Lars Ittner; Ralph Mobbs; Carl R Walkley; Louise E Purton; Robyn L Ward; Jason W H Wong; Luke B Hesson; William Walsh; John E Pimanda
Journal:  Proc Natl Acad Sci U S A       Date:  2016-04-04       Impact factor: 11.205

8.  Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cells.

Authors:  Kosuke Yusa; S Tamir Rashid; Helene Strick-Marchand; Ignacio Varela; Pei-Qi Liu; David E Paschon; Elena Miranda; Adriana Ordóñez; Nicholas R F Hannan; Foad J Rouhani; Sylvie Darche; Graeme Alexander; Stefan J Marciniak; Noemi Fusaki; Mamoru Hasegawa; Michael C Holmes; James P Di Santo; David A Lomas; Allan Bradley; Ludovic Vallier
Journal:  Nature       Date:  2011-10-12       Impact factor: 49.962

Review 9.  Genome-editing technologies for gene correction of hemophilia.

Authors:  Chul-Yong Park; Dongjin R Lee; Jin Jea Sung; Dong-Wook Kim
Journal:  Hum Genet       Date:  2016-06-29       Impact factor: 4.132

10.  Systematic identification of culture conditions for induction and maintenance of naive human pluripotency.

Authors:  Thorold W Theunissen; Benjamin E Powell; Haoyi Wang; Maya Mitalipova; Dina A Faddah; Jessica Reddy; Zi Peng Fan; Dorothea Maetzel; Kibibi Ganz; Linyu Shi; Tenzin Lungjangwa; Sumeth Imsoonthornruksa; Yonatan Stelzer; Sudharshan Rangarajan; Ana D'Alessio; Jianming Zhang; Qing Gao; Meelad M Dawlaty; Richard A Young; Nathanael S Gray; Rudolf Jaenisch
Journal:  Cell Stem Cell       Date:  2014-07-24       Impact factor: 24.633
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  1 in total

Review 1.  CRISPR-Cas9: A Preclinical and Clinical Perspective for the Treatment of Human Diseases.

Authors:  Garima Sharma; Ashish Ranjan Sharma; Manojit Bhattacharya; Sang-Soo Lee; Chiranjib Chakraborty
Journal:  Mol Ther       Date:  2020-09-20       Impact factor: 11.454
  1 in total

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