Literature DB >> 27983559

Phenotype Characterization of HD Intermediate Alleles in PREDICT-HD.

Nancy R Downing1, Spencer Lourens2, Isabella De Soriano3, Jeffrey D Long3,4, Jane S Paulsen3,5,6.   

Abstract

BACKGROUND: Huntington disease (HD) is a neurodegenerative disease caused by a CAG repeat expansion on chromosome 4. Pathology is associated with CAG repeat length. Prior studies examining people in the intermediate allele (IA) range found subtle differences in motor, cognitive, and behavioral domains compared to controls.
OBJECTIVE: The purpose of this study was to examine baseline and longitudinal differences in motor, cognitive, behavioral, functional, and imaging outcomes between persons with CAG repeats in three ranges: normal (≤26), intermediate (27-35), and reduced penetrance (36-39).
METHODS: We examined longitudinal data from 389 participants in three allele groups: 280 normal controls (NC), 21 intermediate allele [IA], and 88 reduced penetrance [RP]. We used linear mixed models to identify differences in baseline and longitudinal outcomes between groups. Three models were tested: 1) no baseline or longitudinal differences; 2) baseline differences but no longitudinal differences; and 3) baseline and longitudinal differences.
RESULTS: Model 1 was the best fitting model for most outcome variables. Models 2 and 3 were best fitting for some of the variables. We found baseline and longitudinal trends of declining performance across increasing CAG repeat length groups, but no significant differences between the NC and IA groups.
CONCLUSION: We did not find evidence to support differences in the IA group compared to the NC group. These findings are limited by a small IA sample size.

Entities:  

Keywords:  Huntington disease; intermediate alleles

Mesh:

Year:  2016        PMID: 27983559      PMCID: PMC6258187          DOI: 10.3233/JHD-160185

Source DB:  PubMed          Journal:  J Huntingtons Dis        ISSN: 1879-6397


  34 in total

1.  Structural MR image processing using the BRAINS2 toolbox.

Authors:  Vincent A Magnotta; Greg Harris; Nancy C Andreasen; Daniel S O'Leary; William T C Yuh; Dan Heckel
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2.  Large normal and reduced penetrance alleles in Huntington disease: instability in families and frequency at the laboratory, at the clinic and in the population.

Authors:  J Sequeiros; E M Ramos; J Cerqueira; M C Costa; A Sousa; J Pinto-Basto; I Alonso
Journal:  Clin Genet       Date:  2010-10       Impact factor: 4.438

3.  Developing the World Health Organization Disability Assessment Schedule 2.0.

Authors:  T Bedirhan Ustün; Somnath Chatterji; Nenad Kostanjsek; Jürgen Rehm; Cille Kennedy; Joanne Epping-Jordan; Shekhar Saxena; Michael von Korff; Charles Pull
Journal:  Bull World Health Organ       Date:  2010-05-20       Impact factor: 9.408

4.  The CAG repeat at the Huntington disease gene in the Portuguese population: insights into its dynamics and to the origin of the mutation.

Authors:  Maria do Carmo Costa; Paula Magalhães; Laura Guimarães; Patrícia Maciel; Jorge Sequeiros; Alda Sousa
Journal:  J Hum Genet       Date:  2005-12-22       Impact factor: 3.172

5.  The measurement of everyday cognition (ECog): scale development and psychometric properties.

Authors:  Sarah Tomaszewski Farias; Dan Mungas; Bruce R Reed; Deborah Cahn-Weiner; William Jagust; Kathleen Baynes; Charles Decarli
Journal:  Neuropsychology       Date:  2008-07       Impact factor: 3.295

6.  Analysis of the Reasons for Non-Uptake of Predictive Testing for Huntington's Disease in Spain: A Qualitative Study.

Authors:  Jesús Rivera-Navarro; Esther Cubo; Natividad Mariscal
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7.  Random-effects models for longitudinal data.

Authors:  N M Laird; J H Ware
Journal:  Biometrics       Date:  1982-12       Impact factor: 2.571

Review 8.  Huntington's disease: from molecular pathogenesis to clinical treatment.

Authors:  Christopher A Ross; Sarah J Tabrizi
Journal:  Lancet Neurol       Date:  2011-01       Impact factor: 44.182

9.  Huntington's disease as caused by 34 CAG repeats.

Authors:  Jürgen Andrich; Larissa Arning; Stefan Wieczorek; Peter H Kraus; Ralf Gold; Carsten Saft
Journal:  Mov Disord       Date:  2008-04-30       Impact factor: 10.338

10.  WHODAS 2.0 in prodromal Huntington disease: measures of functioning in neuropsychiatric disease.

Authors:  Nancy R Downing; Ji-In Kim; Janet K Williams; Jeffrey D Long; James A Mills; Jane S Paulsen
Journal:  Eur J Hum Genet       Date:  2013-12-11       Impact factor: 4.246

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