Sara Reardon. Show Affiliations »
Abstract
Entities: Disease
Mesh: See more » AnimalsClinical Trials as TopicFactor IX/geneticsFemaleGenetic EngineeringGenetic TherapyHIV Infections/geneticsHIV Infections/therapyHemoglobinopathies/geneticsHemoglobinopathies/therapyHemophilia B/geneticsHemophilia B/therapyHumansInfantLeukemia/geneticsLeukemia/immunologyLeukemia/therapyLondonT-Lymphocytes/immunologyT-Lymphocytes/metabolismT-Lymphocytes/transplantationbeta-Thalassemia/geneticsbeta-Thalassemia/therapy
Substances: See more » Factor IX
Year: 2015 PMID: 26560278 DOI: 10.1038/nature.2015.18737
Source DB: PubMed Journal: Nature ISSN: 0028-0836 Impact factor: 49.962