Literature DB >> 26492578

Novel mutations in genes causing hereditary spastic paraplegia and Charcot-Marie-Tooth neuropathy identified by an optimized protocol for homozygosity mapping based on whole-exome sequencing.

Daliya Kancheva1,2,3, Derek Atkinson1,2, Peter De Rijk4, Magdalena Zimon1,2,5, Teodora Chamova6, Vanyo Mitev3, Ahmet Yaramis7, Gian Maria Fabrizi8, Haluk Topaloglu9, Ivailo Tournev6,10, Yesim Parman, Yesim Parma11, Esra Battaloglu12, Alejandro Estrada-Cuzcano1,2, Albena Jordanova1,2,3.   

Abstract

PURPOSE: Homozygosity mapping is an effective approach for detecting molecular defects in consanguineous families by delineating stretches of genomic DNA that are identical by descent. Constant developments in next-generation sequencing created possibilities to combine whole-exome sequencing (WES) and homozygosity mapping in a single step.
METHODS: Basic optimization of homozygosity mapping parameters was performed in a group of families with autosomal-recessive (AR) mutations for which both single-nucleotide polymorphism (SNP) array and WES data were available. We varied the criteria for SNP extraction and PLINK thresholds to estimate their effect on the accuracy of homozygosity mapping based on WES.
RESULTS: Our protocol showed high specificity and sensitivity for homozygosity detection and facilitated the identification of novel mutations in GAN, GBA2, and ZFYVE26 in four families affected by hereditary spastic paraplegia or Charcot-Marie-Tooth disease. Filtering and mapping with optimized parameters was integrated into the HOMWES (homozygosity mapping based on WES analysis) tool in the GenomeComb package for genomic data analysis.
CONCLUSION: We present recommendations for detection of homozygous regions based on WES data and a bioinformatics tool for their identification, which can be widely applied for studying AR disorders.Genet Med 18 6, 600-607.

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Year:  2015        PMID: 26492578     DOI: 10.1038/gim.2015.139

Source DB:  PubMed          Journal:  Genet Med        ISSN: 1098-3600            Impact factor:   8.822


  32 in total

1.  Optimized filtering reduces the error rate in detecting genomic variants by short-read sequencing.

Authors:  Joke Reumers; Peter De Rijk; Hui Zhao; Anthony Liekens; Dominiek Smeets; John Cleary; Peter Van Loo; Maarten Van Den Bossche; Kirsten Catthoor; Bernard Sabbe; Evelyn Despierre; Ignace Vergote; Brian Hilbush; Diether Lambrechts; Jurgen Del-Favero
Journal:  Nat Biotechnol       Date:  2011-12-18       Impact factor: 54.908

2.  The Genome Analysis Toolkit: a MapReduce framework for analyzing next-generation DNA sequencing data.

Authors:  Aaron McKenna; Matthew Hanna; Eric Banks; Andrey Sivachenko; Kristian Cibulskis; Andrew Kernytsky; Kiran Garimella; David Altshuler; Stacey Gabriel; Mark Daly; Mark A DePristo
Journal:  Genome Res       Date:  2010-07-19       Impact factor: 9.043

3.  HomSI: a homozygous stretch identifier from next-generation sequencing data.

Authors:  Zeliha Görmez; Burcu Bakir-Gungor; Mahmut Samil Sagiroglu
Journal:  Bioinformatics       Date:  2013-12-03       Impact factor: 6.937

4.  Autozygosity mapping with exome sequence data.

Authors:  Ian M Carr; Sanjeev Bhaskar; James O'Sullivan; Mohammed A Aldahmesh; Hanan E Shamseldin; Alexander F Markham; David T Bonthron; Graeme Black; Fowzan S Alkuraya
Journal:  Hum Mutat       Date:  2012-10-22       Impact factor: 4.878

5.  H3M2: detection of runs of homozygosity from whole-exome sequencing data.

Authors:  Alberto Magi; Lorenzo Tattini; Flavia Palombo; Matteo Benelli; Alessandro Gialluisi; Betti Giusti; Rosanna Abbate; Marco Seri; Gian Franco Gensini; Giovanni Romeo; Tommaso Pippucci
Journal:  Bioinformatics       Date:  2014-06-24       Impact factor: 6.937

6.  Quantification of homozygosity in consanguineous individuals with autosomal recessive disease.

Authors:  C Geoffrey Woods; James Cox; Kelly Springell; Daniel J Hampshire; Moin D Mohamed; Martin McKibbin; Rowena Stern; F Lucy Raymond; Richard Sandford; Saghira Malik Sharif; Gulshan Karbani; Mustaq Ahmed; Jacquelyn Bond; David Clayton; Chris F Inglehearn
Journal:  Am J Hum Genet       Date:  2006-03-21       Impact factor: 11.025

7.  Use of isolated inbred human populations for identification of disease genes.

Authors:  V C Sheffield; E M Stone; R Carmi
Journal:  Trends Genet       Date:  1998-10       Impact factor: 11.639

8.  Two novel mutations in the GDAP1 and PRX genes in early onset Charcot-Marie-Tooth syndrome.

Authors:  M Auer-Grumbach; C Fischer; L Papić; E John; B Plecko; R E Bittner; G Bernert; T R Pieber; G Miltenberger; R Schwarz; C Windpassinger; F Grill; V Timmerman; M R Speicher; A R Janecke
Journal:  Neuropediatrics       Date:  2008-02       Impact factor: 1.947

Review 9.  Overlapping molecular pathological themes link Charcot-Marie-Tooth neuropathies and hereditary spastic paraplegias.

Authors:  Vincent Timmerman; Virginia E Clowes; Evan Reid
Journal:  Exp Neurol       Date:  2012-01-18       Impact factor: 5.330

10.  Mutations in GBA2 cause autosomal-recessive cerebellar ataxia with spasticity.

Authors:  Monia B Hammer; Ghada Eleuch-Fayache; Lucia V Schottlaender; Houda Nehdi; J Raphael Gibbs; Sampath K Arepalli; Sean B Chong; Dena G Hernandez; Anna Sailer; Guoxiang Liu; Pramod K Mistry; Huaibin Cai; Ginamarie Shrader; Celeste Sassi; Yosr Bouhlal; Henry Houlden; Fayçal Hentati; Rim Amouri; Andrew B Singleton
Journal:  Am J Hum Genet       Date:  2013-01-17       Impact factor: 11.025

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  19 in total

1.  Evaluation of population stratification adjustment using genome-wide or exonic variants.

Authors:  Yuning Chen; Gina M Peloso; Ching-Ti Liu; Anita L DeStefano; Josée Dupuis
Journal:  Genet Epidemiol       Date:  2020-06-30       Impact factor: 2.135

2.  Sphingosine 1-phosphate lyase deficiency causes Charcot-Marie-Tooth neuropathy.

Authors:  Derek Atkinson; Jelena Nikodinovic Glumac; Bob Asselbergh; Biljana Ermanoska; David Blocquel; Regula Steiner; Alejandro Estrada-Cuzcano; Kristien Peeters; Tinne Ooms; Els De Vriendt; Xiang-Lei Yang; Thorsten Hornemann; Vedrana Milic Rasic; Albena Jordanova
Journal:  Neurology       Date:  2017-01-11       Impact factor: 9.910

3.  Loss-of-function mutations in the ATP13A2/PARK9 gene cause complicated hereditary spastic paraplegia (SPG78).

Authors:  Alejandro Estrada-Cuzcano; Shaun Martin; Teodora Chamova; Matthis Synofzik; Dagmar Timmann; Tine Holemans; Albena Andreeva; Jennifer Reichbauer; Riet De Rycke; Dae-In Chang; Sarah van Veen; Jean Samuel; Ludger Schöls; Thorsten Pöppel; Danny Mollerup Sørensen; Bob Asselbergh; Christine Klein; Stephan Zuchner; Albena Jordanova; Peter Vangheluwe; Ivailo Tournev; Rebecca Schüle
Journal:  Brain       Date:  2017-02       Impact factor: 13.501

4.  Distinguishing the differences in β-glycosylceramidase folds, dynamics, and actions informs therapeutic uses.

Authors:  Fredj Ben Bdira; Marta Artola; Herman S Overkleeft; Marcellus Ubbink; Johannes M F G Aerts
Journal:  J Lipid Res       Date:  2018-10-02       Impact factor: 5.922

5.  Spastic paraplegia type 46: novel and recurrent GBA2 gene variants in a compound heterozygous Italian patient with spastic ataxia phenotype.

Authors:  Marta Gatti; Stefania Magri; Daniela Di Bella; Elisa Sarto; Franco Taroni; Caterina Mariotti; Lorenzo Nanetti
Journal:  Neurol Sci       Date:  2021-07-12       Impact factor: 3.307

Review 6.  Next-generation sequencing in Charcot-Marie-Tooth disease: opportunities and challenges.

Authors:  Menelaos Pipis; Alexander M Rossor; Matilde Laura; Mary M Reilly
Journal:  Nat Rev Neurol       Date:  2019-10-03       Impact factor: 42.937

7.  High diagnostic rate of trio exome sequencing in consanguineous families with neurogenetic diseases.

Authors:  Semra Hiz Kurul; Yavuz Oktay; Ana Töpf; Nóra Zs Szabó; Serdal Güngör; Ahmet Yaramis; Ece Sonmezler; Leslie Matalonga; Uluc Yis; Katherine Schon; Ida Paramonov; İpek Polat Kalafatcilar; Fei Gao; Aliz Rieger; Nur Arslan; Elmasnur Yilmaz; Burcu Ekinci; Pinar Pulat Edem; Mahmut Aslan; Bilge Özgör; Angela Lochmüller; Ashwati Nair; Emily O'Heir; Alysia K Lovgren; Reza Maroofian; Henry Houlden; Kiran Polavarapu; Andreas Roos; Juliane S Müller; Denisa Hathazi; Patrick F Chinnery; Steven Laurie; Sergi Beltran; Hanns Lochmüller; Rita Horvath
Journal:  Brain       Date:  2022-05-24       Impact factor: 15.255

8.  Bi-allelic variants in neuronal cell adhesion molecule cause a neurodevelopmental disorder characterized by developmental delay, hypotonia, neuropathy/spasticity.

Authors:  Alina Kurolap; Florian Kreuder; Claudia Gonzaga-Jauregui; Morasha Plesser Duvdevani; Tamar Harel; Luna Tammer; Baozhong Xin; Somayeh Bakhtiari; James Rice; Clare L van Eyk; Jozef Gecz; Jean K Mah; Derek Atkinson; Heidi Cope; Jennifer A Sullivan; Alon M Douek; Daniel Colquhoun; Jason Henry; Donald Wlodkowic; Yesim Parman; Ayşe Candayan; Elif Kocasoy-Orhan; Anat Ilivitzki; Shiri Soudry; Rina Leibu; Fabian Glaser; Valerie Sency; Gil Ast; Vandana Shashi; Michael C Fahey; Esra Battaloğlu; Albena Jordanova; Vardiella Meiner; A Micheil Innes; Heng Wang; Orly Elpeleg; Michael C Kruer; Jan Kaslin; Hagit Baris Feldman
Journal:  Am J Hum Genet       Date:  2022-02-01       Impact factor: 11.043

9.  Whole exome sequencing as a diagnostic tool for patients with ciliopathy-like phenotypes.

Authors:  Sheila Castro-Sánchez; María Álvarez-Satta; Mohamed A Tohamy; Sergi Beltran; Sophia Derdak; Diana Valverde
Journal:  PLoS One       Date:  2017-08-11       Impact factor: 3.240

10.  Whole-exome sequencing to analyze population structure, parental inbreeding, and familial linkage.

Authors:  Aziz Belkadi; Vincent Pedergnana; Aurélie Cobat; Yuval Itan; Quentin B Vincent; Avinash Abhyankar; Lei Shang; Jamila El Baghdadi; Aziz Bousfiha; Alexandre Alcais; Bertrand Boisson; Jean-Laurent Casanova; Laurent Abel
Journal:  Proc Natl Acad Sci U S A       Date:  2016-05-31       Impact factor: 11.205

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