Literature DB >> 26414176

Development of Preliminary Remission Criteria for Gout Using Delphi and 1000Minds Consensus Exercises.

Hugh de Lautour1, William J Taylor2, Ade Adebajo3, Rieke Alten4, Ruben Burgos-Vargas5, Peter Chapman6, Marco A Cimmino7, Geraldo da Rocha Castelar Pinheiro8, Ric Day9, Leslie R Harrold10, Philip Helliwell11, Matthijs Janssen12, Gail Kerr13, Arthur Kavanaugh14, Dinesh Khanna15, Puja P Khanna16, Chingtsai Lin17, Worawit Louthrenoo18, Geraldine McCarthy19, Janitzia Vazquez-Mellado5, Ted R Mikuls20, Tuhina Neogi21, Alexis Ogdie22, Fernando Perez-Ruiz23, Naomi Schlesinger24, H Ralph Schumacher22, Carlo A Scirè25, Jasvinder A Singh26, Francisca Sivera27, Ole Slot28, Lisa K Stamp29, Anne-Kathrin Tausche30, Robert Terkeltaub31, Till Uhlig32, Mart van de Laar33, Douglas White34, Hisashi Yamanaka35, Xuejun Zeng36, Nicola Dalbeth37.   

Abstract

OBJECTIVE: To establish consensus for potential remission criteria to use in clinical trials of gout.
METHODS: Experts (n = 88) in gout from multiple countries were invited to participate in a web-based questionnaire study. Three rounds of Delphi consensus exercises were conducted using SurveyMonkey, followed by a discrete-choice experiment using 1000Minds software. The exercises focused on identifying domains, definitions for each domain, and the timeframe over which remission should be defined.
RESULTS: There were 49 respondents (56% response) to the initial survey, with subsequent response rates ranging from 57% to 90%. Consensus was reached for the inclusion of serum urate (98% agreement), flares (96%), tophi (92%), pain (83%), and patient global assessment of disease activity (93%) as measurement domains in remission criteria. Consensus was also reached for domain definitions, including serum urate (<0.36 mm), pain (<2 on a 10-point scale), and patient global assessment (<2 on a 10-point scale), all of which should be measured at least twice over a set time interval. Consensus was not achieved in the Delphi exercise for the timeframe for remission, with equal responses for 6 months (51%) and 1 year (49%). In the discrete-choice experiment, there was a preference towards 12 months as a timeframe for remission.
CONCLUSION: These consensus exercises have identified domains and provisional definitions for gout remission criteria. Based on the results of these exercises, preliminary remission criteria are proposed with domains of serum urate, acute flares, tophus, pain, and patient global assessment. These preliminary criteria now require testing in clinical data sets.
© 2016, American College of Rheumatology.

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Year:  2016        PMID: 26414176     DOI: 10.1002/acr.22741

Source DB:  PubMed          Journal:  Arthritis Care Res (Hoboken)        ISSN: 2151-464X            Impact factor:   4.794


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