Literature DB >> 25943494

Genome editing technologies: defining a path to clinic.

Jacqueline Corrigan-Curay1, Marina O'Reilly2, Donald B Kohn3, Paula M Cannon4, Gang Bao5, Frederic D Bushman6, Dana Carroll7, Toni Cathomen8, J Keith Joung9, David Roth6, Michel Sadelain10, Andrew M Scharenberg11, Christof von Kalle12, Feng Zhang13, Robert Jambou2, Eugene Rosenthal2, Morad Hassani2, Aparna Singh2, Matthew H Porteus14.   

Abstract

Mesh:

Year:  2015        PMID: 25943494      PMCID: PMC4427885          DOI: 10.1038/mt.2015.54

Source DB:  PubMed          Journal:  Mol Ther        ISSN: 1525-0016            Impact factor:   11.454


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  44 in total

Review 1.  The RAG proteins in V(D)J recombination: more than just a nuclease.

Authors:  M J Sadofsky
Journal:  Nucleic Acids Res       Date:  2001-04-01       Impact factor: 16.971

2.  A general strategy for selecting high-affinity zinc finger proteins for diverse DNA target sites.

Authors:  H A Greisman; C O Pabo
Journal:  Science       Date:  1997-01-31       Impact factor: 47.728

3.  Engineering customized TALE nucleases (TALENs) and TALE transcription factors by fast ligation-based automatable solid-phase high-throughput (FLASH) assembly.

Authors:  Deepak Reyon; Morgan L Maeder; Cyd Khayter; Shengdar Q Tsai; Jonathan E Foley; Jeffry D Sander; J Keith Joung
Journal:  Curr Protoc Mol Biol       Date:  2013-07

4.  Gene conversion tracts from double-strand break repair in mammalian cells.

Authors:  B Elliott; C Richardson; J Winderbaum; J A Nickoloff; M Jasin
Journal:  Mol Cell Biol       Date:  1998-01       Impact factor: 4.272

5.  A programmable dual-RNA-guided DNA endonuclease in adaptive bacterial immunity.

Authors:  Martin Jinek; Krzysztof Chylinski; Ines Fonfara; Michael Hauer; Jennifer A Doudna; Emmanuelle Charpentier
Journal:  Science       Date:  2012-06-28       Impact factor: 47.728

6.  Efficient clinical scale gene modification via zinc finger nuclease-targeted disruption of the HIV co-receptor CCR5.

Authors:  Dawn A Maier; Andrea L Brennan; Shuguang Jiang; Gwendolyn K Binder-Scholl; Gary Lee; Gabriela Plesa; Zhaohui Zheng; Julio Cotte; Carmine Carpenito; Travis Wood; S Kaye Spratt; Dale Ando; Philip Gregory; Michael C Holmes; Elena E Perez; James L Riley; Richard G Carroll; Carl H June; Bruce L Levine
Journal:  Hum Gene Ther       Date:  2013-03-06       Impact factor: 5.695

Review 7.  ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering.

Authors:  Thomas Gaj; Charles A Gersbach; Carlos F Barbas
Journal:  Trends Biotechnol       Date:  2013-05-09       Impact factor: 19.536

8.  CRISPR-mediated modular RNA-guided regulation of transcription in eukaryotes.

Authors:  Luke A Gilbert; Matthew H Larson; Leonardo Morsut; Zairan Liu; Gloria A Brar; Sandra E Torres; Noam Stern-Ginossar; Onn Brandman; Evan H Whitehead; Jennifer A Doudna; Wendell A Lim; Jonathan S Weissman; Lei S Qi
Journal:  Cell       Date:  2013-07-11       Impact factor: 41.582

9.  Mouse transplant models for evaluating the oncogenic risk of a self-inactivating XSCID lentiviral vector.

Authors:  Sheng Zhou; Zhijun Ma; Taihe Lu; Laura Janke; John T Gray; Brian P Sorrentino
Journal:  PLoS One       Date:  2013-04-23       Impact factor: 3.240

10.  Targeted gene addition to a predetermined site in the human genome using a ZFN-based nicking enzyme.

Authors:  Jianbin Wang; Geoffrey Friedman; Yannick Doyon; Nathaniel S Wang; Carrie Jiaxin Li; Jeffrey C Miller; Kevin L Hua; Jenny Jiacheng Yan; Joshua E Babiarz; Philip D Gregory; Michael C Holmes
Journal:  Genome Res       Date:  2012-03-20       Impact factor: 9.043

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  35 in total

1.  Molecular Therapy Special Issue on Gene Editing Technologies and Applications.

Authors:  Robert Frederickson; Seppo Ylä-Herttuala
Journal:  Mol Ther       Date:  2015-08       Impact factor: 11.454

Review 2.  Salient Features of Endonuclease Platforms for Therapeutic Genome Editing.

Authors:  Michael T Certo; Richard A Morgan
Journal:  Mol Ther       Date:  2016-01-22       Impact factor: 11.454

Review 3.  Genetic treatment of a molecular disorder: gene therapy approaches to sickle cell disease.

Authors:  Megan D Hoban; Stuart H Orkin; Daniel E Bauer
Journal:  Blood       Date:  2016-01-12       Impact factor: 22.113

4.  Development and Characterization of a Modular CRISPR and RNA Aptamer Mediated Base Editing System.

Authors:  Juan Carlos Collantes; Victor M Tan; Huiting Xu; Melany Ruiz-Urigüen; Amer Alasadi; Jingjing Guo; Hanlin Tao; Chi Su; Katarzyna M Tyc; Tommaso Selmi; John J Lambourne; Jennifer A Harbottle; Jesse Stombaugh; Jinchuan Xing; Ceri M Wiggins; Shengkan Jin
Journal:  CRISPR J       Date:  2021-02

5.  Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells.

Authors:  Mark A DeWitt; Wendy Magis; Nicolas L Bray; Tianjiao Wang; Jennifer R Berman; Fabrizia Urbinati; Seok-Jin Heo; Therese Mitros; Denise P Muñoz; Dario Boffelli; Donald B Kohn; Mark C Walters; Dana Carroll; David I K Martin; Jacob E Corn
Journal:  Sci Transl Med       Date:  2016-10-12       Impact factor: 17.956

Review 6.  A genome editing primer for the hematologist.

Authors:  Megan D Hoban; Daniel E Bauer
Journal:  Blood       Date:  2016-04-06       Impact factor: 22.113

Review 7.  The clinical applications of genome editing in HIV.

Authors:  Cathy X Wang; Paula M Cannon
Journal:  Blood       Date:  2016-04-06       Impact factor: 22.113

8.  Deciphering the EU clinical trials regulation.

Authors:  Mohamed Abou-El-Enein; Christian K Schneider
Journal:  Nat Biotechnol       Date:  2016-03       Impact factor: 54.908

9.  Knock-in editing: it functionally corrects!

Authors:  Matthew H Porteus
Journal:  Blood       Date:  2016-05-26       Impact factor: 22.113

10.  A New Induction to the Gene and Cell Therapy Hall Of Fame: Genome Editing.

Authors:  Michel Sadelain
Journal:  Mol Ther       Date:  2016-03       Impact factor: 11.454

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