Literature DB >> 25186559

Rational design for enhanced gene therapy with DNA transposons.

Perry B Hackett1, Elena L Aronovich1.   

Abstract

Year:  2014        PMID： 25186559      PMCID： PMC4435493          DOI： 10.1038/mt.2014.149

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  16 in total

1.  High levels of foreign gene expression in hepatocytes after tail vein injections of naked plasmid DNA.

Authors:  G Zhang; V Budker; J A Wolff
Journal:  Hum Gene Ther       Date:  1999-07-01       Impact factor: 5.695

2.  The expression of three abundance classes of messenger RNA in mouse tissues.

Authors:  N D Hastie; J O Bishop
Journal:  Cell       Date:  1976-12       Impact factor: 41.582

3.  Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA.

Authors:  F Liu; Y Song; D Liu
Journal:  Gene Ther       Date:  1999-07       Impact factor: 5.250

4.  Duration of expression and activity of Sleeping Beauty transposase in mouse liver following hydrodynamic DNA delivery.

Authors:  Jason B Bell; Elena L Aronovich; Jeffrey M Schreifels; Thomas C Beadnell; Perry B Hackett
Journal:  Mol Ther       Date:  2010-07-13       Impact factor: 11.454

5.  An operator at -280 base pairs that is required for repression of araBAD operon promoter: addition of DNA helical turns between the operator and promoter cyclically hinders repression.

Authors:  T M Dunn; S Hahn; S Ogden; R F Schleif
Journal:  Proc Natl Acad Sci U S A       Date:  1984-08       Impact factor: 11.205

6.  Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII.

Authors:  Carole Vogler; Beth Levy; Jeffrey H Grubb; Nancy Galvin; Yun Tan; Emil Kakkis; Nadine Pavloff; William S Sly
Journal:  Proc Natl Acad Sci U S A       Date:  2005-09-14       Impact factor: 11.205

Review 7.  Progress and prospects: immune responses to viral vectors.

Authors:  S Nayak; R W Herzog
Journal:  Gene Ther       Date:  2009-11-12       Impact factor: 5.250

8.  Systemic correction of storage disease in MPS I NOD/SCID mice using the sleeping beauty transposon system.

Authors:  Elena L Aronovich; Jason B Bell; Shaukat A Khan; Lalitha R Belur; Roland Gunther; Brenda Koniar; Patricia A Schachern; Josh B Parker; Cathy S Carlson; Chester B Whitley; R Scott McIvor; Pankaj Gupta; Perry B Hackett
Journal:  Mol Ther       Date:  2009-04-21       Impact factor: 11.454

9.  Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients.

Authors:  Steven J Howe; Marc R Mansour; Kerstin Schwarzwaelder; Cynthia Bartholomae; Michael Hubank; Helena Kempski; Martijn H Brugman; Karin Pike-Overzet; Stephen J Chatters; Dick de Ridder; Kimberly C Gilmour; Stuart Adams; Susannah I Thornhill; Kathryn L Parsley; Frank J T Staal; Rosemary E Gale; David C Linch; Jinhua Bayford; Lucie Brown; Michelle Quaye; Christine Kinnon; Philip Ancliff; David K Webb; Manfred Schmidt; Christof von Kalle; H Bobby Gaspar; Adrian J Thrasher
Journal:  J Clin Invest       Date:  2008-09       Impact factor: 14.808

10.  Hyperactive piggyBac transposons for sustained and robust liver-targeted gene therapy.

Authors:  Mario Di Matteo; Emira Samara-Kuko; Natalie J Ward; Simon N Waddington; Simon N Waddingon; John H McVey; Marinee K L Chuah; Thierry VandenDriessche
Journal:  Mol Ther       Date:  2014-07-18       Impact factor: 11.454
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